JP2024543001A5 - - Google Patents

Info

Publication number
JP2024543001A5
JP2024543001A5 JP2024525372A JP2024525372A JP2024543001A5 JP 2024543001 A5 JP2024543001 A5 JP 2024543001A5 JP 2024525372 A JP2024525372 A JP 2024525372A JP 2024525372 A JP2024525372 A JP 2024525372A JP 2024543001 A5 JP2024543001 A5 JP 2024543001A5
Authority
JP
Japan
Prior art keywords
nucleic acid
acid construct
sequence
viral vector
stxbp1
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024525372A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024543001A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2022/080020 external-priority patent/WO2023073071A1/en
Publication of JP2024543001A publication Critical patent/JP2024543001A/ja
Publication of JP2024543001A5 publication Critical patent/JP2024543001A5/ja
Pending legal-status Critical Current

Links

JP2024525372A 2021-10-28 2022-10-26 核酸構築物、ウイルスベクターおよびウイルス粒子 Pending JP2024543001A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163263175P 2021-10-28 2021-10-28
US63/263,175 2021-10-28
PCT/EP2022/080020 WO2023073071A1 (en) 2021-10-28 2022-10-26 Nucleic acid constructs, viral vectors and viral particles

Publications (2)

Publication Number Publication Date
JP2024543001A JP2024543001A (ja) 2024-11-19
JP2024543001A5 true JP2024543001A5 (https=) 2025-10-31

Family

ID=84362196

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024525372A Pending JP2024543001A (ja) 2021-10-28 2022-10-26 核酸構築物、ウイルスベクターおよびウイルス粒子

Country Status (14)

Country Link
US (1) US20240417434A1 (https=)
EP (1) EP4423286A1 (https=)
JP (1) JP2024543001A (https=)
KR (1) KR20240099360A (https=)
CN (1) CN118434876A (https=)
AR (1) AR127455A1 (https=)
AU (1) AU2022378524A1 (https=)
CA (1) CA3234666A1 (https=)
CL (1) CL2024001100A1 (https=)
CO (1) CO2024005920A2 (https=)
IL (1) IL312340A (https=)
MX (1) MX2024005171A (https=)
TW (1) TW202325849A (https=)
WO (1) WO2023073071A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025122543A1 (en) * 2023-12-05 2025-06-12 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to syntaxin-binding protein 1 deficiency
WO2025213064A1 (en) * 2024-04-05 2025-10-09 Capsida Biotherapeutics, Inc. Gene therapy for stxbp1 encephalopathy

Family Cites Families (18)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5139941A (en) 1985-10-31 1992-08-18 University Of Florida Research Foundation, Inc. AAV transduction vectors
AU8200191A (en) 1990-07-09 1992-02-04 United States of America, as represented by the Secretary, U.S. Department of Commerce, The High efficiency packaging of mutant adeno-associated virus using amber suppressions
US5173414A (en) 1990-10-30 1992-12-22 Applied Immune Sciences, Inc. Production of recombinant adeno-associated virus vectors
DE69233013T2 (de) 1991-08-20 2004-03-04 The Government Of The United States Of America As Represented By The Secretary Of National Institute Of Health, Office Of Technology Transfer Adenovirus vermittelter gentransfer in den gastrointestinaltrakt
EP1103610A1 (en) 1999-11-26 2001-05-30 Introgene B.V. Production of vaccines from immortalised mammalian cell lines
FR2808803B1 (fr) 2000-05-11 2004-12-10 Agronomique Inst Nat Rech Cellules es modifiees et gene specifique de cellules es
FR2836924B1 (fr) 2002-03-08 2005-01-14 Vivalis Lignees de cellules aviaires utiles pour la production de substances d'interet
EP1528101A1 (en) 2003-11-03 2005-05-04 ProBioGen AG Immortalized avian cell lines for virus production
FR2884255B1 (fr) 2005-04-11 2010-11-05 Vivalis Utilisation de lignees de cellules souches aviaires ebx pour la production de vaccin contre la grippe
EP1985305A1 (en) 2007-04-24 2008-10-29 Vivalis Duck embryonic derived stem cell lines for the production of viral vaccines
EP1995309A1 (en) 2007-05-21 2008-11-26 Vivalis Recombinant protein production in avian EBx® cells
JP5608863B2 (ja) * 2007-12-28 2014-10-15 公立大学法人横浜市立大学 新生児期〜乳児期発症の難治性てんかんの検出方法
EP2321417B1 (en) * 2008-08-20 2015-07-15 Brainco Biopharma, S.L. Stxbp1 as psychiatric biomarker in murine model system and its uses
GB201403684D0 (en) 2014-03-03 2014-04-16 King S College London Vector
MX2019011772A (es) * 2017-04-03 2020-01-09 Encoded Therapeutics Inc Expresion transgenica selectiva de tejidos.
KR20220094216A (ko) * 2019-11-08 2022-07-05 코브 테라퓨틱스 변형된 아데노-관련 바이러스 벡터 및 이의 중추신경계로의 전달
US20230265453A1 (en) * 2020-07-08 2023-08-24 Baylor College Of Medicine Gene therapy for stxbp1 encephalopathy
WO2022214635A1 (en) * 2021-04-08 2022-10-13 Stichting Vu Nucleic acid molecules for compensation of stxbp1 haploinsufficiency and their use in the treatment of stxbp1-related disorders

Similar Documents

Publication Publication Date Title
JP2021106619A5 (https=)
JP2024009857A5 (https=)
JP2022068181A5 (https=)
JP2020533959A5 (https=)
JP2020522269A5 (https=)
JP2022549380A5 (https=)
JP2022529631A5 (https=)
JP2022531809A5 (https=)
JP2022535749A5 (https=)
JP2024543001A5 (https=)
JP2018522529A5 (https=)
JP2022524434A5 (https=)
US20250297285A1 (en) Transgene cassettes designed to express a human mecp2 gene
JP2022551744A5 (https=)
JP2021534814A5 (https=)
JP2021533805A5 (https=)
JP2022525302A5 (https=)
JP2023520488A5 (https=)
JP2017529395A5 (https=)
JP2022541070A5 (https=)
JP2024506266A5 (https=)
JP2024504611A5 (https=)
JP2023501897A5 (https=)
JP2024543918A5 (https=)
JP2023537980A5 (https=)