JP2024537796A5 - - Google Patents

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Publication number
JP2024537796A5
JP2024537796A5 JP2024519540A JP2024519540A JP2024537796A5 JP 2024537796 A5 JP2024537796 A5 JP 2024537796A5 JP 2024519540 A JP2024519540 A JP 2024519540A JP 2024519540 A JP2024519540 A JP 2024519540A JP 2024537796 A5 JP2024537796 A5 JP 2024537796A5
Authority
JP
Japan
Prior art keywords
seq
aav
construct
promoter
vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024519540A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024537796A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/077397 external-priority patent/WO2023056452A1/en
Publication of JP2024537796A publication Critical patent/JP2024537796A/ja
Publication of JP2024537796A5 publication Critical patent/JP2024537796A5/ja
Pending legal-status Critical Current

Links

JP2024519540A 2021-09-30 2022-09-30 難聴を治療するための遺伝子療法送達組成物及び方法 Pending JP2024537796A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163251017P 2021-09-30 2021-09-30
US63/251,017 2021-09-30
PCT/US2022/077397 WO2023056452A1 (en) 2021-09-30 2022-09-30 Gene therapy delivery compositions and methods for treating hearing loss

Publications (2)

Publication Number Publication Date
JP2024537796A JP2024537796A (ja) 2024-10-16
JP2024537796A5 true JP2024537796A5 (https=) 2025-12-09

Family

ID=85783683

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024519540A Pending JP2024537796A (ja) 2021-09-30 2022-09-30 難聴を治療するための遺伝子療法送達組成物及び方法

Country Status (9)

Country Link
US (1) US20250222137A1 (https=)
EP (1) EP4409009A4 (https=)
JP (1) JP2024537796A (https=)
KR (1) KR20240099153A (https=)
CN (1) CN118339302A (https=)
AU (1) AU2022358579A1 (https=)
CA (1) CA3233522A1 (https=)
MX (1) MX2024003910A (https=)
WO (1) WO2023056452A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20240382461A1 (en) * 2023-05-15 2024-11-21 Pharmazz, Inc. Pharmaceutical composition and method for prevention and treatment of hearing loss
CN119859633A (zh) * 2024-12-31 2025-04-22 中国水产科学研究院东海水产研究所 一种拟穴青蟹eyes absent-2基因编辑的方法及应用

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SG10201913266UA (en) * 2015-12-11 2020-02-27 Massachusetts Eye & Ear Infirmary Materials and methods for delivering nucleic acids to cochlear and vestibular cells
EP3762040A4 (en) * 2018-03-05 2022-01-05 Children's Medical Center Corporation COMPOSITIONS AND METHODS OF ADMINISTRATION OF NUCLEIC ACIDS TO COCHLEAR AND VESTIBULAR CELLS
US20210277417A1 (en) * 2018-06-25 2021-09-09 Akouos, Inc. Methods of treating clrn1-associated hearing loss and/or vision loss
WO2021091938A1 (en) * 2019-11-04 2021-05-14 Decibel Therapeutics, Inc. Cochlear outer hair cell promoters and uses thereof
CN111349148A (zh) * 2020-03-13 2020-06-30 辉大(上海)生物科技有限公司 一种腺相关病毒载体及其用途

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