JP2021517168A5 - - Google Patents
Info
- Publication number
- JP2021517168A5 JP2021517168A5 JP2020571336A JP2020571336A JP2021517168A5 JP 2021517168 A5 JP2021517168 A5 JP 2021517168A5 JP 2020571336 A JP2020571336 A JP 2020571336A JP 2020571336 A JP2020571336 A JP 2020571336A JP 2021517168 A5 JP2021517168 A5 JP 2021517168A5
- Authority
- JP
- Japan
- Prior art keywords
- acid sequence
- composition according
- gba
- amino acid
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024075599A JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862641012P | 2018-03-09 | 2018-03-09 | |
| US62/641,012 | 2018-03-09 | ||
| PCT/US2019/021422 WO2019173756A1 (en) | 2018-03-09 | 2019-03-08 | Compositions and methods for treating parkinson's disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024075599A Division JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2021517168A JP2021517168A (ja) | 2021-07-15 |
| JP2021517168A5 true JP2021517168A5 (https=) | 2022-03-15 |
Family
ID=67847471
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020571336A Pending JP2021517168A (ja) | 2018-03-09 | 2019-03-08 | パーキンソン病を処置するための組成物及び方法 |
| JP2024075599A Pending JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024075599A Pending JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20210000929A1 (https=) |
| EP (1) | EP3762505A4 (https=) |
| JP (2) | JP2021517168A (https=) |
| AU (2) | AU2019231889A1 (https=) |
| CA (1) | CA3092961A1 (https=) |
| IL (1) | IL277182A (https=) |
| MA (1) | MA54792A (https=) |
| WO (1) | WO2019173756A1 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN115087455A (zh) * | 2019-11-12 | 2022-09-20 | 奥查德疗法(欧洲)有限公司 | 用于治疗或预防克罗恩病的组合物和方法 |
| CN115348884B (zh) * | 2020-03-29 | 2024-07-30 | 耶达研究及发展有限公司 | 用于治疗戈谢病的β-葡糖脑苷脂酶变体 |
| EP4146797A1 (en) * | 2020-05-06 | 2023-03-15 | Orchard Therapeutics (Europe) Limited | Treatment for neurodegenerative diseases |
| US20230227847A1 (en) * | 2020-05-27 | 2023-07-20 | Universität Zürich | Viral vectors expressing therapeutic proteins specifically in myeloid cells and microglia |
| BR112023001456A2 (pt) * | 2020-07-27 | 2023-04-11 | Voyager Therapeutics Inc | Composições e métodos para o tratamento de distúrbios neurológicos relacionados à deficiência de beta glicosilceramidase |
| WO2023004366A1 (en) * | 2021-07-21 | 2023-01-26 | Aspen Neuroscience, Inc. | Transposon-based modulation of gba1 and related compositions and uses thereof |
| JP2026506873A (ja) * | 2023-02-02 | 2026-02-27 | エンボールド セラピューティクス， インコーポレイテッド | 操作されたグルコセレブロシダーゼバリアント |
| WO2024238448A2 (en) * | 2023-05-12 | 2024-11-21 | Temple University - Of The Commonwealth System Of Higher Education | Chimeric capsid recombinant adeno-associated virus with bbb penetration and microglia targeting (aav-bm) |
| GB202307366D0 (en) * | 2023-05-17 | 2023-06-28 | Ospedale San Raffaele Srl | Vector |
| US12565639B2 (en) | 2023-06-13 | 2026-03-03 | Aspen Neuroscience, Inc. | Methods for differentiating dopaminergic neurons from stem cells |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2215222T3 (es) * | 1996-12-05 | 2004-10-01 | Crucell Holland B.V. | Modificacion genetica de celulas cepa de repoblacion hematopoyeticas de primates. |
| AU2006254796B2 (en) * | 2005-06-08 | 2012-08-16 | Amicus Therapeutics, Inc. | Treatment of CNS disorders associated with mutations in genes encoding lysosomal enzymes |
| MY161859A (en) * | 2011-01-03 | 2017-05-15 | Avm Biotechnology Llc | Personalized production of biologics and method for reprogramming somatic cells |
| EP3196301B1 (en) * | 2012-07-11 | 2018-10-17 | Sangamo Therapeutics, Inc. | Methods and compositions for the treatment of monogenic diseases |
| ES2729997T3 (es) * | 2012-11-27 | 2019-11-07 | Biomarin Pharm Inc | Proteínas de fusión terapéuticas dirigidas de enzima lisosómica y usos de las mismas |
| CA2985235A1 (en) * | 2015-05-07 | 2016-11-10 | Shire Human Genetic Therapies, Inc. | Glucocerebrosidase gene therapy for parkinson's disease |
| US20190085394A1 (en) * | 2015-12-14 | 2019-03-21 | Parkinson's Institute | Refining diagnosis and treatment of complex multi-symptom neurological disorders |
| GB201522243D0 (en) * | 2015-12-16 | 2016-01-27 | Ucl Business Plc | Treatment |
| BR112020008033A2 (pt) * | 2017-10-23 | 2020-10-27 | Prevail Therapeutics, Inc. | terapias gênicas para doença neurodegenerativa |
-
2019
- 2019-03-08 JP JP2020571336A patent/JP2021517168A/ja active Pending
- 2019-03-08 EP EP19764359.6A patent/EP3762505A4/en active Pending
- 2019-03-08 CA CA3092961A patent/CA3092961A1/en active Pending
- 2019-03-08 US US16/979,378 patent/US20210000929A1/en active Pending
- 2019-03-08 AU AU2019231889A patent/AU2019231889A1/en not_active Abandoned
- 2019-03-08 MA MA054792A patent/MA54792A/fr unknown
- 2019-03-08 WO PCT/US2019/021422 patent/WO2019173756A1/en not_active Ceased
-
2020
- 2020-09-07 IL IL277182A patent/IL277182A/en unknown
-
2024
- 2024-05-08 JP JP2024075599A patent/JP2024102250A/ja active Pending
-
2025
- 2025-08-14 AU AU2025217319A patent/AU2025217319A1/en active Pending
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