JP2021517168A5 - - Google Patents
Info
- Publication number
- JP2021517168A5 JP2021517168A5 JP2020571336A JP2020571336A JP2021517168A5 JP 2021517168 A5 JP2021517168 A5 JP 2021517168A5 JP 2020571336 A JP2020571336 A JP 2020571336A JP 2020571336 A JP2020571336 A JP 2020571336A JP 2021517168 A5 JP2021517168 A5 JP 2021517168A5
- Authority
- JP
- Japan
- Prior art keywords
- acid sequence
- composition according
- gba
- amino acid
- sequence
- Prior art date
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024075599A JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862641012P | 2018-03-09 | 2018-03-09 | |
| US62/641,012 | 2018-03-09 | ||
| PCT/US2019/021422 WO2019173756A1 (en) | 2018-03-09 | 2019-03-08 | Compositions and methods for treating parkinson's disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024075599A Division JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2021517168A JP2021517168A (ja) | 2021-07-15 |
| JPWO2019173756A5 JPWO2019173756A5 (https=) | 2022-03-15 |
| JP2021517168A5 true JP2021517168A5 (https=) | 2022-03-15 |
Family
ID=67847471
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020571336A Pending JP2021517168A (ja) | 2018-03-09 | 2019-03-08 | パーキンソン病を処置するための組成物及び方法 |
| JP2024075599A Pending JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024075599A Pending JP2024102250A (ja) | 2018-03-09 | 2024-05-08 | パーキンソン病を処置するための組成物及び方法 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20210000929A1 (https=) |
| EP (1) | EP3762505A4 (https=) |
| JP (2) | JP2021517168A (https=) |
| AU (2) | AU2019231889A1 (https=) |
| CA (1) | CA3092961A1 (https=) |
| IL (1) | IL277182A (https=) |
| MA (1) | MA54792A (https=) |
| WO (1) | WO2019173756A1 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2021097131A1 (en) * | 2019-11-12 | 2021-05-20 | Orchard Therapeutics (Europe) Limited | Compositions and methods for treating or preventing crohn's disease |
| KR20230003492A (ko) * | 2020-03-29 | 2023-01-06 | 예다 리서치 앤드 디벨럽먼트 캄파니 리미티드 | 고셔병 치료용 베타-글루코세레브로시다아제 변이체 |
| EP4146797A1 (en) * | 2020-05-06 | 2023-03-15 | Orchard Therapeutics (Europe) Limited | Treatment for neurodegenerative diseases |
| WO2021239308A1 (en) * | 2020-05-27 | 2021-12-02 | Universität Zürich | Viral vectors expressing therapeutic proteins specifically in myeloid cells and microglia |
| BR112023001456A2 (pt) * | 2020-07-27 | 2023-04-11 | Voyager Therapeutics Inc | Composições e métodos para o tratamento de distúrbios neurológicos relacionados à deficiência de beta glicosilceramidase |
| WO2023004366A1 (en) * | 2021-07-21 | 2023-01-26 | Aspen Neuroscience, Inc. | Transposon-based modulation of gba1 and related compositions and uses thereof |
| AU2024213347A1 (en) * | 2023-02-02 | 2025-08-14 | Embold Therapeutics, Inc. | Engineered glucocerebrosidase variants |
| WO2024238448A2 (en) * | 2023-05-12 | 2024-11-21 | Temple University - Of The Commonwealth System Of Higher Education | Chimeric capsid recombinant adeno-associated virus with bbb penetration and microglia targeting (aav-bm) |
| GB202307366D0 (en) * | 2023-05-17 | 2023-06-28 | Ospedale San Raffaele Srl | Vector |
| EP4728055A2 (en) | 2023-06-13 | 2026-04-22 | Aspen Neuroscience, Inc. | Methods for differentiating dopaminergic neurons from stem cells |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE69727492T2 (de) * | 1996-12-05 | 2004-12-16 | Crucell Holland B.V. | Genetische modifikation der hämatopoietischen repopulation von stammzellen in primaten |
| CN101541172A (zh) * | 2005-06-08 | 2009-09-23 | 阿米库斯治疗学公司 | 溶酶体酶编码基因突变相关的cns紊乱的治疗 |
| WO2012094321A1 (en) * | 2011-01-03 | 2012-07-12 | Avm Biotechnology, Llc | Personalized production of biologics and method for reprogramming somatic cells |
| DK3444342T3 (da) * | 2012-07-11 | 2020-08-24 | Sangamo Therapeutics Inc | Fremgangsmåder og sammensætninger til behandlingen af lysosomale aflejringssygdomme |
| HUE039334T2 (hu) * | 2012-11-27 | 2018-12-28 | Biomarin Pharm Inc | Célzott terápiás lizoszómális enzim fúziós fehérjék és azok alkalmazásai |
| EP3292206B8 (en) * | 2015-05-07 | 2022-02-09 | Takeda Pharmaceutical Company Limited | Glucocerebrosidase gene therapy for parkinson's disease |
| WO2017106363A1 (en) * | 2015-12-14 | 2017-06-22 | Parkinson's Institute | Refining diagnosis and treatment of complex multi-symptom neurological disorders |
| GB201522243D0 (en) * | 2015-12-16 | 2016-01-27 | Ucl Business Plc | Treatment |
| AU2018354195A1 (en) * | 2017-10-23 | 2020-06-04 | Prevail Therapeutics, Inc. | Gene therapies for neurodegenerative disease |
-
2019
- 2019-03-08 MA MA054792A patent/MA54792A/fr unknown
- 2019-03-08 EP EP19764359.6A patent/EP3762505A4/en active Pending
- 2019-03-08 AU AU2019231889A patent/AU2019231889A1/en not_active Abandoned
- 2019-03-08 WO PCT/US2019/021422 patent/WO2019173756A1/en not_active Ceased
- 2019-03-08 JP JP2020571336A patent/JP2021517168A/ja active Pending
- 2019-03-08 CA CA3092961A patent/CA3092961A1/en active Pending
- 2019-03-08 US US16/979,378 patent/US20210000929A1/en active Pending
-
2020
- 2020-09-07 IL IL277182A patent/IL277182A/en unknown
-
2024
- 2024-05-08 JP JP2024075599A patent/JP2024102250A/ja active Pending
-
2025
- 2025-08-14 AU AU2025217319A patent/AU2025217319A1/en active Pending
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