JP2022523913A5 - - Google Patents
Info
- Publication number
- JP2022523913A5 JP2022523913A5 JP2021544547A JP2021544547A JP2022523913A5 JP 2022523913 A5 JP2022523913 A5 JP 2022523913A5 JP 2021544547 A JP2021544547 A JP 2021544547A JP 2021544547 A JP2021544547 A JP 2021544547A JP 2022523913 A5 JP2022523913 A5 JP 2022523913A5
- Authority
- JP
- Japan
- Prior art keywords
- acid sequence
- amino acid
- grn
- optionally
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024231791A JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962800096P | 2019-02-01 | 2019-02-01 | |
| US62/800,096 | 2019-02-01 | ||
| PCT/US2020/016192 WO2020160458A1 (en) | 2019-02-01 | 2020-01-31 | Compositions and methods for treating neurocognitive disorders |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024231791A Division JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022523913A JP2022523913A (ja) | 2022-04-27 |
| JP2022523913A5 true JP2022523913A5 (https=) | 2023-04-25 |
Family
ID=71841663
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021544547A Pending JP2022523913A (ja) | 2019-02-01 | 2020-01-31 | 神経認知障害を処置するための組成物及び方法 |
| JP2024231791A Pending JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024231791A Pending JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20220111005A1 (https=) |
| EP (1) | EP3917539A4 (https=) |
| JP (2) | JP2022523913A (https=) |
| CA (1) | CA3128003A1 (https=) |
| IL (1) | IL285269A (https=) |
| MA (1) | MA54874A (https=) |
| WO (1) | WO2020160458A1 (https=) |
Families Citing this family (20)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP7013753B2 (ja) * | 2017-09-15 | 2022-02-01 | 株式会社三洋物産 | 遊技機 |
| JP7013754B2 (ja) * | 2017-09-15 | 2022-02-01 | 株式会社三洋物産 | 遊技機 |
| BR112021015817A2 (pt) | 2019-02-22 | 2021-10-13 | The Trustees Of The University Of Pennsylvania | Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn |
| MX2022004812A (es) * | 2019-10-22 | 2023-02-23 | Applied Genetic Tech Corporation | Sistemas de virus adeno-asociados (aav) para el tratamiento de enfermedades o trastornos neurodegenerativos asociados a la progranulina. |
| EP4146797A1 (en) * | 2020-05-06 | 2023-03-15 | Orchard Therapeutics (Europe) Limited | Treatment for neurodegenerative diseases |
| US20230227847A1 (en) * | 2020-05-27 | 2023-07-20 | Universität Zürich | Viral vectors expressing therapeutic proteins specifically in myeloid cells and microglia |
| JP6879413B2 (ja) * | 2020-06-24 | 2021-06-02 | 株式会社三洋物産 | 遊技機 |
| US20240033332A1 (en) * | 2020-12-17 | 2024-02-01 | Kyoto University | Agent for activating a neuron |
| JP2021079225A (ja) * | 2021-03-01 | 2021-05-27 | 株式会社三洋物産 | 遊技機 |
| JP2021079226A (ja) * | 2021-03-01 | 2021-05-27 | 株式会社三洋物産 | 遊技機 |
| JP2021087833A (ja) * | 2021-03-01 | 2021-06-10 | 株式会社三洋物産 | 遊技機 |
| JP2021087836A (ja) * | 2021-03-01 | 2021-06-10 | 株式会社三洋物産 | 遊技機 |
| US20240342207A1 (en) * | 2021-08-02 | 2024-10-17 | Board Of Regents, The University Of Texas System | Modified nucleic acid compositions and associated methods for treatment of phenylketonuria |
| WO2023196619A1 (en) * | 2022-04-08 | 2023-10-12 | Shape Therapeutics Inc. | Promoter switches for tissue-specific expression |
| JP7556432B2 (ja) * | 2022-08-22 | 2024-09-26 | 株式会社三洋物産 | 遊技機 |
| JP7556433B2 (ja) * | 2022-08-22 | 2024-09-26 | 株式会社三洋物産 | 遊技機 |
| JP7556434B2 (ja) * | 2022-08-22 | 2024-09-26 | 株式会社三洋物産 | 遊技機 |
| JP2026509301A (ja) * | 2023-03-14 | 2026-03-17 | ユーシービー バイオファルマ エスアールエル | 遺伝子治療 |
| WO2024205404A1 (en) * | 2023-03-27 | 2024-10-03 | Sanquin IP B.V. | Novel capsid engineered aav vectors for liver-directed gene therapy |
| CN121313796A (zh) * | 2025-11-24 | 2026-01-13 | 北京大学 | 多肽grn-e及其在制备围绝经期情绪障碍的药物或制剂中的应用 |
Family Cites Families (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP0495831B1 (en) * | 1989-10-16 | 1997-01-15 | Hem Pharmaceuticals Corp. | Diagnosis and treatment of neuro-cognitive disorders associated with systemic immunological malfunction |
| DK0752248T3 (da) | 1992-11-13 | 2000-11-13 | Idec Pharma Corp | Terapeutisk anvendelse af kimæriske og radioaktivt mærkede antistoffer mod humant B-lymfocytbegrænset differentieringsantig |
| EP1461087A1 (en) * | 2001-12-06 | 2004-09-29 | Institut National De La Sante Et De La Recherche Medicale (Inserm) | Use of cd34+ hematopoietic progenitor cells for the treatment of cns disorders |
| US8486635B2 (en) * | 2006-05-30 | 2013-07-16 | Mayo Foundation For Medical Education And Research | Detecting and treating dementia |
| HUE031156T2 (en) * | 2006-06-07 | 2017-06-28 | Genzyme Corp | Gene therapy for amyotrophic lateral sclerosis and other spinal cord disorders |
| WO2009089635A1 (en) * | 2008-01-16 | 2009-07-23 | Neurodyn, Inc. | Treating neurodegenerative diseases with progranulin (pgrn) |
| US20120039865A1 (en) * | 2008-08-19 | 2012-02-16 | Yale University | Identification of sortilin as a neuronal receptor for the frontotemporal dementia protein, progranulin |
| HRP20250897T1 (hr) * | 2009-05-02 | 2025-09-26 | Genzyme Corporation | Genska terapija za neurodegenerativne poremećaje |
| US20110203007A1 (en) * | 2010-02-16 | 2011-08-18 | Board Of Supervisors Of Louisiana State University And Agricultural And Mechanical College | Assays of neurodegenerative disorders, including frontotemporal dementia and amyotrophic lateral sclerosis |
| JP6312436B2 (ja) * | 2010-11-16 | 2018-04-18 | ニューロダイン ライフ サイエンシズ インコーポレイテッドＮｅｕｒｏｄｙｎ Ｌｉｆｅ Ｓｃｉｅｎｃｅｓ Ｉｎｃ． | ネプリライシンの発現および活性を増大させるための方法および医薬組成物 |
| US20190328906A1 (en) * | 2016-03-02 | 2019-10-31 | The Children's Hospital Of Philadelphia | Therapy for frontotemporal dementia |
| US20210284701A1 (en) * | 2016-07-14 | 2021-09-16 | Emory University | Granulin Compositions and Uses Related Thereto |
| CA3056617A1 (en) | 2017-03-15 | 2018-09-20 | The Regents Of The University Of California | Methods of treating lysosomal disorders |
| BR112021015817A2 (pt) * | 2019-02-22 | 2021-10-13 | The Trustees Of The University Of Pennsylvania | Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn |
-
2020
- 2020-01-31 WO PCT/US2020/016192 patent/WO2020160458A1/en not_active Ceased
- 2020-01-31 MA MA054874A patent/MA54874A/fr unknown
- 2020-01-31 US US17/427,298 patent/US20220111005A1/en active Pending
- 2020-01-31 CA CA3128003A patent/CA3128003A1/en active Pending
- 2020-01-31 EP EP20748326.4A patent/EP3917539A4/en active Pending
- 2020-01-31 JP JP2021544547A patent/JP2022523913A/ja active Pending
-
2021
- 2021-08-01 IL IL285269A patent/IL285269A/en unknown
-
2024
- 2024-12-27 JP JP2024231791A patent/JP2025060943A/ja active Pending
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