JP2022523913A - 神経認知障害を処置するための組成物及び方法 - Google Patents

神経認知障害を処置するための組成物及び方法 Download PDF

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JP2022523913A
JP2022523913A JP2021544547A JP2021544547A JP2022523913A JP 2022523913 A JP2022523913 A JP 2022523913A JP 2021544547 A JP2021544547 A JP 2021544547A JP 2021544547 A JP2021544547 A JP 2021544547A JP 2022523913 A JP2022523913 A JP 2022523913A
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acid sequence
amino acid
seq
grn
optionally
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JPWO2020160458A5 (https=
JP2022523913A5 (https=
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メイソン，クリス
クーパー，オリバー
プラスチャート，ロバート
ディーンドレイド，マーク
ティル，ニコ，ペーター ヴァン
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アブロバイオ，インコーポレーテッド
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JP2021544547A 2019-02-01 2020-01-31 神経認知障害を処置するための組成物及び方法 Pending JP2022523913A (ja)

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US201962800096P 2019-02-01 2019-02-01
US62/800,096 2019-02-01
PCT/US2020/016192 WO2020160458A1 (en) 2019-02-01 2020-01-31 Compositions and methods for treating neurocognitive disorders

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US (1) US20220111005A1 (https=)
EP (1) EP3917539A4 (https=)
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JP7013753B2 (ja) * 2017-09-15 2022-02-01 株式会社三洋物産 遊技機
JP7013754B2 (ja) * 2017-09-15 2022-02-01 株式会社三洋物産 遊技機
BR112021015817A2 (pt) 2019-02-22 2021-10-13 The Trustees Of The University Of Pennsylvania Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn
IL292382A (en) * 2019-10-22 2022-06-01 Applied Genetic Tech Corporation Adeno-associated virus (aav) systems for treatment of progranulin associated neurodegenerative diseases or disorders
EP4146797A1 (en) * 2020-05-06 2023-03-15 Orchard Therapeutics (Europe) Limited Treatment for neurodegenerative diseases
WO2021239308A1 (en) * 2020-05-27 2021-12-02 Universität Zürich Viral vectors expressing therapeutic proteins specifically in myeloid cells and microglia
JP6879413B2 (ja) * 2020-06-24 2021-06-02 株式会社三洋物産 遊技機
US20240033332A1 (en) * 2020-12-17 2024-02-01 Kyoto University Agent for activating a neuron
JP2021079226A (ja) * 2021-03-01 2021-05-27 株式会社三洋物産 遊技機
JP2021087833A (ja) * 2021-03-01 2021-06-10 株式会社三洋物産 遊技機
JP2021079225A (ja) * 2021-03-01 2021-05-27 株式会社三洋物産 遊技機
JP2021087836A (ja) * 2021-03-01 2021-06-10 株式会社三洋物産 遊技機
US20240342207A1 (en) * 2021-08-02 2024-10-17 Board Of Regents, The University Of Texas System Modified nucleic acid compositions and associated methods for treatment of phenylketonuria
EP4504762A1 (en) * 2022-04-08 2025-02-12 Shape Therapeutics Inc. Promoter switches for tissue-specific expression
JP7556433B2 (ja) * 2022-08-22 2024-09-26 株式会社三洋物産 遊技機
JP7556434B2 (ja) * 2022-08-22 2024-09-26 株式会社三洋物産 遊技機
JP7556432B2 (ja) * 2022-08-22 2024-09-26 株式会社三洋物産 遊技機
EP4680752A1 (en) * 2023-03-14 2026-01-21 UCB Biopharma SRL Gene therapy
WO2024205404A1 (en) * 2023-03-27 2024-10-03 Sanquin IP B.V. Novel capsid engineered aav vectors for liver-directed gene therapy
CN121313796A (zh) * 2025-11-24 2026-01-13 北京大学 多肽grn-e及其在制备围绝经期情绪障碍的药物或制剂中的应用

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