JP2024521052A5 - - Google Patents
Info
- Publication number
- JP2024521052A5 JP2024521052A5 JP2023569975A JP2023569975A JP2024521052A5 JP 2024521052 A5 JP2024521052 A5 JP 2024521052A5 JP 2023569975 A JP2023569975 A JP 2023569975A JP 2023569975 A JP2023569975 A JP 2023569975A JP 2024521052 A5 JP2024521052 A5 JP 2024521052A5
- Authority
- JP
- Japan
- Prior art keywords
- cells
- viral vector
- polynucleotide
- construct
- promoter
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163188450P | 2021-05-13 | 2021-05-13 | |
| US63/188,450 | 2021-05-13 | ||
| US202163251025P | 2021-09-30 | 2021-09-30 | |
| US63/251,025 | 2021-09-30 | ||
| US202163277549P | 2021-11-09 | 2021-11-09 | |
| US63/277,549 | 2021-11-09 | ||
| PCT/US2022/028396 WO2022240778A1 (en) | 2021-05-13 | 2022-05-09 | Gene therapy delivery compositions and methods for treating hearing loss |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024521052A JP2024521052A (ja) | 2024-05-28 |
| JP2024521052A5 true JP2024521052A5 (https=) | 2025-05-16 |
Family
ID=84028799
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023569975A Pending JP2024521052A (ja) | 2021-05-13 | 2022-05-09 | 遺伝子治療送達組成物及び難聴を処置するための方法 |
Country Status (16)
| Country | Link |
|---|---|
| US (1) | US20250339560A1 (https=) |
| EP (1) | EP4337226A4 (https=) |
| JP (1) | JP2024521052A (https=) |
| KR (1) | KR20240021799A (https=) |
| AU (1) | AU2022271727A1 (https=) |
| CA (1) | CA3218877A1 (https=) |
| CL (1) | CL2023003364A1 (https=) |
| CO (1) | CO2023017148A2 (https=) |
| CR (1) | CR20230577A (https=) |
| DO (1) | DOP2023000248A (https=) |
| EC (1) | ECSP23093588A (https=) |
| IL (1) | IL308396A (https=) |
| JO (1) | JOP20230289A1 (https=) |
| MX (1) | MX2023013394A (https=) |
| PE (1) | PE20240240A1 (https=) |
| WO (1) | WO2022240778A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3727468A4 (en) | 2017-12-19 | 2021-09-22 | Akouos, Inc. | AAV-MEDIATED THERAPEUTIC ANTIBODIES DELIVERY TO THE INTERNAL EAR |
| TW202227476A (zh) * | 2020-09-14 | 2022-07-16 | 哈佛大學校長及研究員協會 | 編碼GJB2之重組腺相關病毒(rAAV)及其用途 |
| IL303317A (en) | 2020-12-01 | 2023-07-01 | Akouos Inc | ANTI-NATURAL ANTIBODY STRUCTURES AND RELATED METHODS FOR THE TREATMENT OF SYMPTOMS ASSOCIATED WITH VESTIBULAR SWANNOMA |
| KR20250175321A (ko) * | 2023-03-28 | 2025-12-16 | 센소리온 | 커넥신 26을 암호화하는 아데노-연관 바이러스 벡터 및 이의 용도 |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO1999007843A1 (en) * | 1997-08-05 | 1999-02-18 | F. Hoffman-La Roche Ag | Human glial cell line-derived neurotrophic factor promoters, vectors containing same, and methods of screening compounds therewith |
| JP2005538697A (ja) * | 2002-04-19 | 2005-12-22 | シエーリング アクチエンゲゼルシャフト | 新規前立腺腫瘍特異的プロモーター |
| CA2609142C (en) * | 2005-05-27 | 2016-02-09 | Fondazione Centro San Raffaele Del Monte Tabor | Therapeutic gene vectors comprising mirna target sequences |
| US20070161031A1 (en) * | 2005-12-16 | 2007-07-12 | The Board Of Trustees Of The Leland Stanford Junior University | Functional arrays for high throughput characterization of gene expression regulatory elements |
| US20150051267A1 (en) * | 2013-08-16 | 2015-02-19 | Purdue Research Foundation | BICISTRONIC GENE TRANSFER TOOLS FOR DELIVERY OF miRNAS AND PROTEIN CODING SEQUENCES |
| WO2017093566A1 (en) * | 2015-12-04 | 2017-06-08 | Universite Pierre Et Marie Curie (Paris 6) | Promoters and uses thereof |
| AU2018344883B2 (en) * | 2017-10-02 | 2024-03-07 | Scientist Of Fortune S.A. | Cellular transport system for transferring a sulfonic acid construct carrying a cargo into the cytoplasm of a cell |
| WO2019200016A1 (en) * | 2018-04-10 | 2019-10-17 | President And Fellows Of Harvard College | Aav vectors encoding clarin-1 or gjb2 and uses thereof |
| WO2020077295A1 (en) * | 2018-10-11 | 2020-04-16 | Decibel Therapeutics, Inc. | Aav1 vectors and uses thereof for treatment of otic indications |
| EP4007814A1 (en) * | 2019-07-26 | 2022-06-08 | Akouos, Inc. | Methods of treating hearing loss using a secreted target protein |
| WO2021067448A1 (en) * | 2019-09-30 | 2021-04-08 | Applied Genetic Technologies Corporation | Adeno-associated virus (aav) systems for treatment of genetic hearing loss |
| WO2021231808A2 (en) * | 2020-05-13 | 2021-11-18 | Akouos, Inc. | Compositions and methods for treating gjb2-associated hearing loss |
-
2022
- 2022-05-09 MX MX2023013394A patent/MX2023013394A/es unknown
- 2022-05-09 CA CA3218877A patent/CA3218877A1/en active Pending
- 2022-05-09 EP EP22808141.0A patent/EP4337226A4/en active Pending
- 2022-05-09 JP JP2023569975A patent/JP2024521052A/ja active Pending
- 2022-05-09 AU AU2022271727A patent/AU2022271727A1/en not_active Abandoned
- 2022-05-09 PE PE2023003052A patent/PE20240240A1/es unknown
- 2022-05-09 US US18/560,064 patent/US20250339560A1/en active Pending
- 2022-05-09 WO PCT/US2022/028396 patent/WO2022240778A1/en not_active Ceased
- 2022-05-09 CR CR20230577A patent/CR20230577A/es unknown
- 2022-05-09 KR KR1020237042840A patent/KR20240021799A/ko active Pending
- 2022-05-09 IL IL308396A patent/IL308396A/en unknown
-
2023
- 2023-11-10 DO DO2023000248A patent/DOP2023000248A/es unknown
- 2023-11-10 CL CL2023003364A patent/CL2023003364A1/es unknown
- 2023-11-12 JO JOJO/P/2023/0289A patent/JOP20230289A1/ar unknown
- 2023-12-11 CO CONC2023/0017148A patent/CO2023017148A2/es unknown
- 2023-12-13 EC ECSENADI202393588A patent/ECSP23093588A/es unknown
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