JP2024521052A5 - - Google Patents

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Publication number
JP2024521052A5
JP2024521052A5 JP2023569975A JP2023569975A JP2024521052A5 JP 2024521052 A5 JP2024521052 A5 JP 2024521052A5 JP 2023569975 A JP2023569975 A JP 2023569975A JP 2023569975 A JP2023569975 A JP 2023569975A JP 2024521052 A5 JP2024521052 A5 JP 2024521052A5
Authority
JP
Japan
Prior art keywords
cells
viral vector
polynucleotide
construct
promoter
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023569975A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024521052A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/028396 external-priority patent/WO2022240778A1/en
Publication of JP2024521052A publication Critical patent/JP2024521052A/ja
Publication of JP2024521052A5 publication Critical patent/JP2024521052A5/ja
Pending legal-status Critical Current

Links

JP2023569975A 2021-05-13 2022-05-09 遺伝子治療送達組成物及び難聴を処置するための方法 Pending JP2024521052A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202163188450P 2021-05-13 2021-05-13
US63/188,450 2021-05-13
US202163251025P 2021-09-30 2021-09-30
US63/251,025 2021-09-30
US202163277549P 2021-11-09 2021-11-09
US63/277,549 2021-11-09
PCT/US2022/028396 WO2022240778A1 (en) 2021-05-13 2022-05-09 Gene therapy delivery compositions and methods for treating hearing loss

Publications (2)

Publication Number Publication Date
JP2024521052A JP2024521052A (ja) 2024-05-28
JP2024521052A5 true JP2024521052A5 (https=) 2025-05-16

Family

ID=84028799

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023569975A Pending JP2024521052A (ja) 2021-05-13 2022-05-09 遺伝子治療送達組成物及び難聴を処置するための方法

Country Status (16)

Country Link
US (1) US20250339560A1 (https=)
EP (1) EP4337226A4 (https=)
JP (1) JP2024521052A (https=)
KR (1) KR20240021799A (https=)
AU (1) AU2022271727A1 (https=)
CA (1) CA3218877A1 (https=)
CL (1) CL2023003364A1 (https=)
CO (1) CO2023017148A2 (https=)
CR (1) CR20230577A (https=)
DO (1) DOP2023000248A (https=)
EC (1) ECSP23093588A (https=)
IL (1) IL308396A (https=)
JO (1) JOP20230289A1 (https=)
MX (1) MX2023013394A (https=)
PE (1) PE20240240A1 (https=)
WO (1) WO2022240778A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3727468A4 (en) 2017-12-19 2021-09-22 Akouos, Inc. AAV-MEDIATED THERAPEUTIC ANTIBODIES DELIVERY TO THE INTERNAL EAR
TW202227476A (zh) * 2020-09-14 2022-07-16 哈佛大學校長及研究員協會 編碼GJB2之重組腺相關病毒(rAAV)及其用途
IL303317A (en) 2020-12-01 2023-07-01 Akouos Inc ANTI-NATURAL ANTIBODY STRUCTURES AND RELATED METHODS FOR THE TREATMENT OF SYMPTOMS ASSOCIATED WITH VESTIBULAR SWANNOMA
KR20250175321A (ko) * 2023-03-28 2025-12-16 센소리온 커넥신 26을 암호화하는 아데노-연관 바이러스 벡터 및 이의 용도

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO1999007843A1 (en) * 1997-08-05 1999-02-18 F. Hoffman-La Roche Ag Human glial cell line-derived neurotrophic factor promoters, vectors containing same, and methods of screening compounds therewith
JP2005538697A (ja) * 2002-04-19 2005-12-22 シエーリング アクチエンゲゼルシャフト 新規前立腺腫瘍特異的プロモーター
CA2609142C (en) * 2005-05-27 2016-02-09 Fondazione Centro San Raffaele Del Monte Tabor Therapeutic gene vectors comprising mirna target sequences
US20070161031A1 (en) * 2005-12-16 2007-07-12 The Board Of Trustees Of The Leland Stanford Junior University Functional arrays for high throughput characterization of gene expression regulatory elements
US20150051267A1 (en) * 2013-08-16 2015-02-19 Purdue Research Foundation BICISTRONIC GENE TRANSFER TOOLS FOR DELIVERY OF miRNAS AND PROTEIN CODING SEQUENCES
WO2017093566A1 (en) * 2015-12-04 2017-06-08 Universite Pierre Et Marie Curie (Paris 6) Promoters and uses thereof
AU2018344883B2 (en) * 2017-10-02 2024-03-07 Scientist Of Fortune S.A. Cellular transport system for transferring a sulfonic acid construct carrying a cargo into the cytoplasm of a cell
WO2019200016A1 (en) * 2018-04-10 2019-10-17 President And Fellows Of Harvard College Aav vectors encoding clarin-1 or gjb2 and uses thereof
WO2020077295A1 (en) * 2018-10-11 2020-04-16 Decibel Therapeutics, Inc. Aav1 vectors and uses thereof for treatment of otic indications
EP4007814A1 (en) * 2019-07-26 2022-06-08 Akouos, Inc. Methods of treating hearing loss using a secreted target protein
WO2021067448A1 (en) * 2019-09-30 2021-04-08 Applied Genetic Technologies Corporation Adeno-associated virus (aav) systems for treatment of genetic hearing loss
WO2021231808A2 (en) * 2020-05-13 2021-11-18 Akouos, Inc. Compositions and methods for treating gjb2-associated hearing loss

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