JP2024526234A5 - - Google Patents

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Publication number
JP2024526234A5
JP2024526234A5 JP2023580406A JP2023580406A JP2024526234A5 JP 2024526234 A5 JP2024526234 A5 JP 2024526234A5 JP 2023580406 A JP2023580406 A JP 2023580406A JP 2023580406 A JP2023580406 A JP 2023580406A JP 2024526234 A5 JP2024526234 A5 JP 2024526234A5
Authority
JP
Japan
Prior art keywords
nucleotides
dsrna agent
agent according
myoc
nucleotide sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023580406A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024526234A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/035266 external-priority patent/WO2023278406A1/en
Publication of JP2024526234A publication Critical patent/JP2024526234A/ja
Publication of JP2024526234A5 publication Critical patent/JP2024526234A5/ja
Pending legal-status Critical Current

Links

JP2023580406A 2021-06-28 2022-06-28 Myoc発現をサイレンシングするための組成物および方法 Pending JP2024526234A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202163215804P 2021-06-28 2021-06-28
US63/215,804 2021-06-28
US202163287404P 2021-12-08 2021-12-08
US63/287,404 2021-12-08
US202263351033P 2022-06-10 2022-06-10
US63/351,033 2022-06-10
PCT/US2022/035266 WO2023278406A1 (en) 2021-06-28 2022-06-28 Compositions and methods for silencing myoc expression

Publications (2)

Publication Number Publication Date
JP2024526234A JP2024526234A (ja) 2024-07-17
JP2024526234A5 true JP2024526234A5 (https=) 2025-07-09

Family

ID=84692959

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023580406A Pending JP2024526234A (ja) 2021-06-28 2022-06-28 Myoc発現をサイレンシングするための組成物および方法

Country Status (10)

Country Link
US (1) US20240318175A1 (https=)
EP (1) EP4363587A4 (https=)
JP (1) JP2024526234A (https=)
KR (1) KR20240026216A (https=)
AU (1) AU2022301058A1 (https=)
CA (1) CA3224868A1 (https=)
IL (1) IL309230A (https=)
MX (1) MX2023014976A (https=)
TW (1) TW202317148A (https=)
WO (1) WO2023278406A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR20240117571A (ko) * 2021-12-08 2024-08-01 리제너론 파마슈티칼스 인코포레이티드 돌연변이 마이오실린 질환 모델 및 이의 용도

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2005117938A2 (en) * 2004-04-13 2005-12-15 Regents Of The University Of Minnesota Methods of treating ocular conditions
EP2313505A2 (en) * 2008-07-15 2011-04-27 F. Hoffmann-La Roche AG Compositions and methods for inhibiting expression of tgf-beta receptor genes
EP3540061A1 (en) * 2014-04-02 2019-09-18 Editas Medicine, Inc. Crispr/cas-related methods and compositions for treating primary open angle glaucoma
SG11201702055PA (en) * 2014-09-16 2017-04-27 Genzyme Corp Adeno-associated viral vectors for treating myocilin (myoc) glaucoma
PL4012035T3 (pl) * 2014-09-16 2025-03-24 Genzyme Corporation Wektory wirusowe związane z adenowirusami do leczenia jaskry miocylinowej (myoc)
KR20230008729A (ko) * 2020-04-06 2023-01-16 알닐람 파마슈티칼스 인코포레이티드 Myoc 발현을 사일런싱하기 위한 조성물 및 방법

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