JP2024525721A5 - - Google Patents

Info

Publication number
JP2024525721A5
JP2024525721A5 JP2024501712A JP2024501712A JP2024525721A5 JP 2024525721 A5 JP2024525721 A5 JP 2024525721A5 JP 2024501712 A JP2024501712 A JP 2024501712A JP 2024501712 A JP2024501712 A JP 2024501712A JP 2024525721 A5 JP2024525721 A5 JP 2024525721A5
Authority
JP
Japan
Prior art keywords
expression construct
vector
construct according
sequence number
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024501712A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024525721A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/IB2022/056458 external-priority patent/WO2023285987A1/en
Publication of JP2024525721A publication Critical patent/JP2024525721A/ja
Publication of JP2024525721A5 publication Critical patent/JP2024525721A5/ja
Pending legal-status Critical Current

Links

JP2024501712A 2021-07-14 2022-07-13 Ｒｅｔｇｃ遺伝子治療 Pending JP2024525721A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163221883P 2021-07-14 2021-07-14
US63/221,883 2021-07-14
PCT/IB2022/056458 WO2023285987A1 (en) 2021-07-14 2022-07-13 Retgc gene therapy

Publications (2)

Publication Number Publication Date
JP2024525721A JP2024525721A (ja) 2024-07-12
JP2024525721A5 true JP2024525721A5 (https=) 2025-07-22

Family

ID=82932504

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024501712A Pending JP2024525721A (ja) 2021-07-14 2022-07-13 Ｒｅｔｇｃ遺伝子治療

Country Status (10)

Country Link
US (1) US20250002936A1 (https=)
EP (1) EP4370695A1 (https=)
JP (1) JP2024525721A (https=)
KR (1) KR20240055728A (https=)
CN (1) CN117980489A (https=)
AU (1) AU2022310166A1 (https=)
CA (1) CA3225084A1 (https=)
IL (1) IL310017A (https=)
MX (1) MX2024000747A (https=)
WO (1) WO2023285987A1 (https=)

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE4345297A1 (de) 1993-11-11 1995-09-28 Nsm Ag Geldspielgerät
US5856152A (en) 1994-10-28 1999-01-05 The Trustees Of The University Of Pennsylvania Hybrid adenovirus-AAV vector and methods of use therefor
CA2346262A1 (en) 1998-09-17 2000-03-23 University Of Florida Methods for treatment of degenerative retinal diseases
SG10201800541SA (en) * 2010-04-23 2018-03-28 Univ Florida Raav-guanylate cyclase compositions and methods for treating leber's congenital amaurosis-1 (lca1)
MA44546B1 (fr) 2016-06-15 2021-03-31 Univ California Virus adéno-associés variants et procédés d'utilisation

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