JP2023535232A5 - - Google Patents

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Publication number
JP2023535232A5
JP2023535232A5 JP2023512465A JP2023512465A JP2023535232A5 JP 2023535232 A5 JP2023535232 A5 JP 2023535232A5 JP 2023512465 A JP2023512465 A JP 2023512465A JP 2023512465 A JP2023512465 A JP 2023512465A JP 2023535232 A5 JP2023535232 A5 JP 2023535232A5
Authority
JP
Japan
Prior art keywords
seq
promoter
sequence
nos
rpe65
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Withdrawn
Application number
JP2023512465A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023535232A (ja
Filing date
Publication date
Priority claimed from CN202010704946.1A external-priority patent/CN113952471A/zh
Application filed filed Critical
Priority claimed from PCT/CN2021/107284 external-priority patent/WO2022017363A1/en
Publication of JP2023535232A publication Critical patent/JP2023535232A/ja
Publication of JP2023535232A5 publication Critical patent/JP2023535232A5/ja
Withdrawn legal-status Critical Current

Links

JP2023512465A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Withdrawn JP2023535232A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
CN202010704946.1 2020-07-21
CN202010704946.1A CN113952471A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
CN202110378979 2021-04-08
CN202110378979.6 2021-04-08
PCT/CN2021/107284 WO2022017363A1 (en) 2020-07-21 2021-07-20 Compositions and methods for the treatment of ocular diseases

Publications (2)

Publication Number Publication Date
JP2023535232A JP2023535232A (ja) 2023-08-16
JP2023535232A5 true JP2023535232A5 (https=) 2024-07-26

Family

ID=79728991

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512465A Withdrawn JP2023535232A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

Country Link
US (1) US20230321280A1 (https=)
EP (1) EP4185335A1 (https=)
JP (1) JP2023535232A (https=)
CN (1) CN116368228A (https=)
AU (1) AU2021314400A1 (https=)
CA (1) CA3186818A1 (https=)
WO (1) WO2022017363A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20250295808A1 (en) * 2022-03-28 2025-09-25 Indian Institute Of Technology Kanpur A system for an ocular gene therapy and a process for preparing thereof
WO2024077089A2 (en) * 2022-10-04 2024-04-11 Siren Biotechnology, Inc. Modified cpg dinucleotides for recombinant viral vector production

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
GB201502137D0 (en) * 2015-02-09 2015-03-25 Ucl Business Plc Treatment
HK1253299A1 (zh) * 2015-06-04 2019-06-14 INSERM (Institut National de la Santé et de la Recherche Médicale) 一种通过基因治疗治疗眼疾病的改进方法
SG11202000840YA (en) * 2017-07-31 2020-02-27 Reflection Biotechnologies Ltd Cellular models of and therapies for ocular diseases
CN111118017B (zh) * 2018-11-01 2023-10-03 上海朗昇生物科技有限公司 治疗Leber先天性黑蒙症的载体及其应用

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