JP2023524065A5 - - Google Patents

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JP2023524065A5
JP2023524065A5 JP2022566328A JP2022566328A JP2023524065A5 JP 2023524065 A5 JP2023524065 A5 JP 2023524065A5 JP 2022566328 A JP2022566328 A JP 2022566328A JP 2022566328 A JP2022566328 A JP 2022566328A JP 2023524065 A5 JP2023524065 A5 JP 2023524065A5
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pharmaceutical composition
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modified oligonucleotides
tds
ceo
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JP2022566328A
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JP2023524065A (ja
JP7738573B2 (ja
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Priority claimed from PCT/US2021/030203 external-priority patent/WO2021222768A2/en
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JP2022566328A 2020-05-01 2021-04-30 Ａｔｘｎ１を調節するための化合物及び方法 Active JP7738573B2 (ja)

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JP2025145172A JP2026012176A (ja) 2020-05-01 2025-09-02 Ａｔｘｎ１を調節するための化合物及び方法

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US202063019089P 2020-05-01 2020-05-01
US63/019,089 2020-05-01
PCT/US2021/030203 WO2021222768A2 (en) 2020-05-01 2021-04-30 Compounds and methods for modulating atxn1

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JP2023524065A JP2023524065A (ja) 2023-06-08
JP2023524065A5 true JP2023524065A5 (https=) 2024-05-13
JP7738573B2 JP7738573B2 (ja) 2025-09-12

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JP2025145172A Pending JP2026012176A (ja) 2020-05-01 2025-09-02 Ａｔｘｎ１を調節するための化合物及び方法

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US (3) US11542504B2 (https=)
EP (1) EP4143321A4 (https=)
JP (2) JP7738573B2 (https=)
KR (1) KR20230005933A (https=)
AU (1) AU2021264010A1 (https=)
BR (1) BR112022021333A2 (https=)
CA (1) CA3181546A1 (https=)
IL (1) IL297435A (https=)
MX (1) MX2022013707A (https=)
TW (1) TWI901676B (https=)
WO (1) WO2021222768A2 (https=)

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TWI901676B (zh) 2020-05-01 2025-10-21 美商Ionis製藥公司 調節ａｔｘｎ１之化合物及方法
CN119410579B (zh) * 2024-12-02 2026-03-17 中国医学科学院输血研究所 一种培养nk细胞的方法及应用

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