JP2023516676A5 - - Google Patents

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Publication number
JP2023516676A5
JP2023516676A5 JP2022552798A JP2022552798A JP2023516676A5 JP 2023516676 A5 JP2023516676 A5 JP 2023516676A5 JP 2022552798 A JP2022552798 A JP 2022552798A JP 2022552798 A JP2022552798 A JP 2022552798A JP 2023516676 A5 JP2023516676 A5 JP 2023516676A5
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JP
Japan
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mrna
sequence
mol
lipid
composition according
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JP2022552798A
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Japanese (ja)
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JP7832114B2 (ja
JP2023516676A (ja
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Priority claimed from PCT/US2021/020634 external-priority patent/WO2021178510A1/en
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Publication of JP2023516676A5 publication Critical patent/JP2023516676A5/ja
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JP2022552798A 2020-03-03 2021-03-03 オルニチントランスカルバミラーゼ欠損症の治療のための組成物及び方法 Active JP7832114B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202062984764P 2020-03-03 2020-03-03
US62/984,764 2020-03-03
PCT/US2021/020634 WO2021178510A1 (en) 2020-03-03 2021-03-03 Compositions and methods for the treatment of ornithine transcarbamylase deficiency

Publications (3)

Publication Number Publication Date
JP2023516676A JP2023516676A (ja) 2023-04-20
JP2023516676A5 true JP2023516676A5 (https=) 2024-03-12
JP7832114B2 JP7832114B2 (ja) 2026-03-17

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JP2022552798A Active JP7832114B2 (ja) 2020-03-03 2021-03-03 オルニチントランスカルバミラーゼ欠損症の治療のための組成物及び方法

Country Status (6)

Country Link
US (2) US12351834B2 (https=)
EP (1) EP4114470A4 (https=)
JP (1) JP7832114B2 (https=)
AU (1) AU2021231795A1 (https=)
CA (1) CA3169889A1 (https=)
WO (1) WO2021178510A1 (https=)

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