JP2023115348A5 - - Google Patents

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JP2023115348A5
JP2023115348A5 JP2023108132A JP2023108132A JP2023115348A5 JP 2023115348 A5 JP2023115348 A5 JP 2023115348A5 JP 2023108132 A JP2023108132 A JP 2023108132A JP 2023108132 A JP2023108132 A JP 2023108132A JP 2023115348 A5 JP2023115348 A5 JP 2023115348A5
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polynucleotide
seq
identity
nucleotide sequence
polynucleotide according
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JP2023108132A
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JP2023115348A (ja
JP7631425B2 (ja
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JP2023108132A 2015-11-13 2023-06-30 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター Active JP7631425B2 (ja)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201562255317P 2015-11-13 2015-11-13
US62/255,317 2015-11-13
JP2020132079A JP7069258B2 (ja) 2015-11-13 2020-08-04 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター
JP2022075864A JP7307836B2 (ja) 2015-11-13 2022-05-02 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター

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JP2022075864A Division JP7307836B2 (ja) 2015-11-13 2022-05-02 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター

Publications (3)

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JP2023115348A JP2023115348A (ja) 2023-08-18
JP2023115348A5 true JP2023115348A5 (https=) 2023-11-17
JP7631425B2 JP7631425B2 (ja) 2025-02-18

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JP2018524747A Active JP6768798B2 (ja) 2015-11-13 2016-11-11 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター
JP2020132079A Active JP7069258B2 (ja) 2015-11-13 2020-08-04 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター
JP2022075864A Active JP7307836B2 (ja) 2015-11-13 2022-05-02 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター
JP2023108132A Active JP7631425B2 (ja) 2015-11-13 2023-06-30 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター

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JP2018524747A Active JP6768798B2 (ja) 2015-11-13 2016-11-11 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター
JP2020132079A Active JP7069258B2 (ja) 2015-11-13 2020-08-04 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター
JP2022075864A Active JP7307836B2 (ja) 2015-11-13 2022-05-02 組換えfviii変異型をコードする血友病a遺伝子治療用高発現ウイルスベクター

Country Status (18)

Country Link
US (4) US10189888B2 (https=)
EP (1) EP3374387A1 (https=)
JP (4) JP6768798B2 (https=)
KR (2) KR102484553B1 (https=)
CN (3) CN116479001A (https=)
AU (4) AU2016353353B2 (https=)
BR (1) BR112018009717B1 (https=)
CA (1) CA3005334A1 (https=)
CL (1) CL2018001299A1 (https=)
CO (1) CO2018005377A2 (https=)
EA (2) EA202190827A1 (https=)
IL (3) IL281038B2 (https=)
MX (1) MX2018005982A (https=)
MY (2) MY190067A (https=)
SG (2) SG11201804070XA (https=)
TW (3) TWI695069B (https=)
WO (1) WO2017083762A1 (https=)
ZA (3) ZA201803443B (https=)

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KR102817222B1 (ko) * 2021-04-02 2025-06-11 연세대학교 산학협력단 Fe-fviii 변이 유전자로 교정된 줄기세포, 이로부터 분화된 내피 세포 및 이를 포함하는 혈우병 예방 또는 치료용 약제학적 조성물
KR102421131B1 (ko) * 2021-05-28 2022-07-15 알엔에이진(주) 세포내에서 장시간동안 존재할 수 있는 외부 도입 mRNA를 선별하는 방법
EP4211153A4 (en) * 2021-11-25 2023-11-01 Sichuan Real&Best Biotech Co., Ltd. ENGINEERED HUMAN FVII1 WITH INCREASED SECRETION ABILITY AND COAGULATION ACTIVITY
KR20250007615A (ko) * 2022-04-28 2025-01-14 조인트 스탁 컴퍼니 "바이오케드" Fviii-bdd를 인코딩하는 코돈 최적화된 핵산
CN115948408A (zh) * 2022-09-23 2023-04-11 上海信致医药科技有限公司 改进的人凝血因子viii基因表达盒及其应用
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