JP2024515827A5 - - Google Patents

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Publication number
JP2024515827A5
JP2024515827A5 JP2023566512A JP2023566512A JP2024515827A5 JP 2024515827 A5 JP2024515827 A5 JP 2024515827A5 JP 2023566512 A JP2023566512 A JP 2023566512A JP 2023566512 A JP2023566512 A JP 2023566512A JP 2024515827 A5 JP2024515827 A5 JP 2024515827A5
Authority
JP
Japan
Prior art keywords
nucleic acid
sequence
modified
acid according
acid molecule
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023566512A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024515827A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/026805 external-priority patent/WO2022232442A2/en
Publication of JP2024515827A publication Critical patent/JP2024515827A/ja
Publication of JP2024515827A5 publication Critical patent/JP2024515827A5/ja
Pending legal-status Critical Current

Links

JP2023566512A 2021-04-28 2022-04-28 多重CRISPR/Cas9媒介標的遺伝子活性化システム Pending JP2024515827A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163181059P 2021-04-28 2021-04-28
US63/181,059 2021-04-28
PCT/US2022/026805 WO2022232442A2 (en) 2021-04-28 2022-04-28 Multiplex crispr/cas9-mediated target gene activation system

Publications (2)

Publication Number Publication Date
JP2024515827A JP2024515827A (ja) 2024-04-10
JP2024515827A5 true JP2024515827A5 (https=) 2025-05-20

Family

ID=83848892

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023566512A Pending JP2024515827A (ja) 2021-04-28 2022-04-28 多重CRISPR/Cas9媒介標的遺伝子活性化システム

Country Status (7)

Country Link
US (1) US20240209354A1 (https=)
EP (1) EP4330375A4 (https=)
JP (1) JP2024515827A (https=)
CN (1) CN117580941A (https=)
AU (1) AU2022267320A1 (https=)
CA (1) CA3218209A1 (https=)
WO (1) WO2022232442A2 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025111340A1 (en) * 2023-11-20 2025-05-30 William Marsh Rice University Engineered extrachromosomal nucleic acids and methods of use thereof
WO2025227064A1 (en) * 2024-04-26 2025-10-30 Renasci Biotechnologies, Inc. Genomic editing methods to treat cardiovascular disease, and compositions for use in practicing the same
CN119020323A (zh) * 2024-09-29 2024-11-26 中国农业科学院作物科学研究所 一种融合外切酶的CRIPSR/Cas12i3小麦基因编辑体系

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP6793547B2 (ja) * 2013-12-12 2020-12-02 ザ・ブロード・インスティテュート・インコーポレイテッド 最適化機能CRISPR−Cas系による配列操作のための系、方法および組成物
AU2017219605B2 (en) * 2016-02-15 2023-04-13 Temple University - Of The Commonwealth System Of Higher Education Excision of retroviral nucleic acid sequences
AU2018393050A1 (en) * 2017-12-21 2020-06-18 Bayer Healthcare Llc Materials and methods for treatment of Usher Syndrome Type 2A
WO2019236081A1 (en) * 2018-06-06 2019-12-12 Salk Institute For Biological Studies Targeted gene activation using modified guide rna
EP4028063A1 (en) * 2019-09-13 2022-07-20 Regeneron Pharmaceuticals, Inc. Transcription modulation in animals using crispr/cas systems delivered by lipid nanoparticles

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