JP2022553375A5 - - Google Patents
Info
- Publication number
- JP2022553375A5 JP2022553375A5 JP2022523854A JP2022523854A JP2022553375A5 JP 2022553375 A5 JP2022553375 A5 JP 2022553375A5 JP 2022523854 A JP2022523854 A JP 2022523854A JP 2022523854 A JP2022523854 A JP 2022523854A JP 2022553375 A5 JP2022553375 A5 JP 2022553375A5
- Authority
- JP
- Japan
- Prior art keywords
- polynucleotide construct
- sequence
- seq
- composition
- expression cassette
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962924567P | 2019-10-22 | 2019-10-22 | |
| US62/924,567 | 2019-10-22 | ||
| PCT/US2020/056890 WO2021081225A1 (en) | 2019-10-22 | 2020-10-22 | Ornithine transcarbamylase (otc) constructs and methods of using the same |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022553375A JP2022553375A (ja) | 2022-12-22 |
| JP2022553375A5 true JP2022553375A5 (OSRAM) | 2023-10-26 |
| JP7826197B2 JP7826197B2 (ja) | 2026-03-09 |
Family
ID=75620841
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022523854A Active JP7826197B2 (ja) | 2019-10-22 | 2020-10-22 | オルニチントランスカルバミラーゼ（ｏｔｃ）構築物およびそれを使用する方法 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20230001021A1 (OSRAM) |
| EP (1) | EP4048317A4 (OSRAM) |
| JP (1) | JP7826197B2 (OSRAM) |
| KR (1) | KR20240130161A (OSRAM) |
| CN (1) | CN116096428A (OSRAM) |
| AU (1) | AU2020371697A1 (OSRAM) |
| CA (1) | CA3158626A1 (OSRAM) |
| IL (1) | IL292420A (OSRAM) |
| WO (1) | WO2021081225A1 (OSRAM) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN113166783B (zh) | 2018-10-09 | 2024-10-11 | 不列颠哥伦比亚大学 | 包含无有机溶剂和去污剂的转染活性囊泡的组合物和系统以及与之相关的方法 |
| EP4330404A1 (en) * | 2021-04-28 | 2024-03-06 | Genevant Sciences Gmbh | Mrna delivery constructs and methods of using the same |
| KR20230083893A (ko) * | 2021-12-03 | 2023-06-12 | 고려대학교 산학협력단 | 번역 효율이 향상된 5'-utr, 이를 포함하는 합성 핵산 분자 및 이를 포함하는 백신 또는 치료제 조성물 |
| CN121335707A (zh) * | 2023-03-06 | 2026-01-13 | 通用药品有限责任公司 | 密码子优化及其使用方法 |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8853377B2 (en) * | 2010-11-30 | 2014-10-07 | Shire Human Genetic Therapies, Inc. | mRNA for use in treatment of human genetic diseases |
| DK2817287T3 (da) * | 2012-02-24 | 2019-01-02 | Arbutus Biopharma Corp | Trialkyl kationisk lipid og metoder til anvendelse deraf |
| WO2015011633A1 (en) * | 2013-07-23 | 2015-01-29 | Protiva Biotherapeutics, Inc. | Compositions and methods for delivering messenger rna |
| AU2014296278C1 (en) * | 2013-07-30 | 2023-02-02 | Genevant Sciences Gmbh | Block copolymers and their conjugates or complexes with oligonucleotides |
| EP3022354B1 (en) * | 2013-08-23 | 2017-04-26 | Dow Global Technologies LLC | Textiles attached with low density polyurethane foams made using a combination of frothing and blowing methods |
| CN114642735A (zh) * | 2015-01-21 | 2022-06-21 | 菲泽尔克斯公司 | 用于将治疗剂和诊断剂递送到细胞中的方法、组合物和系统 |
| CN109312313A (zh) * | 2016-06-13 | 2019-02-05 | 川斯勒佰尔公司 | 用于治疗鸟氨酸转氨甲酰酶缺乏症的信使rna疗法 |
| FI3568483T3 (fi) * | 2017-01-10 | 2025-11-21 | Childrens Medical Res Institute | Polynukleotideja ja vektoreita siirtogeenien ilmentämiseen |
| SG11202002186VA (en) * | 2017-10-19 | 2020-05-28 | Curevac Ag | Novel artificial nucleic acid molecules |
| EP3714048B1 (en) * | 2017-11-22 | 2025-04-09 | ModernaTX, Inc. | Polynucleotides encoding ornithine transcarbamylase for the treatment of urea cycle disorders |
-
2020
- 2020-10-22 WO PCT/US2020/056890 patent/WO2021081225A1/en not_active Ceased
- 2020-10-22 CN CN202080089266.1A patent/CN116096428A/zh active Pending
- 2020-10-22 EP EP20878326.6A patent/EP4048317A4/en active Pending
- 2020-10-22 KR KR1020227017024A patent/KR20240130161A/ko active Pending
- 2020-10-22 CA CA3158626A patent/CA3158626A1/en active Pending
- 2020-10-22 AU AU2020371697A patent/AU2020371697A1/en active Pending
- 2020-10-22 US US17/771,421 patent/US20230001021A1/en active Pending
- 2020-10-22 IL IL292420A patent/IL292420A/en unknown
- 2020-10-22 JP JP2022523854A patent/JP7826197B2/ja active Active
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