JP2022513718A5 - - Google Patents

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Publication number
JP2022513718A5
JP2022513718A5 JP2021531945A JP2021531945A JP2022513718A5 JP 2022513718 A5 JP2022513718 A5 JP 2022513718A5 JP 2021531945 A JP2021531945 A JP 2021531945A JP 2021531945 A JP2021531945 A JP 2021531945A JP 2022513718 A5 JP2022513718 A5 JP 2022513718A5
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JP
Japan
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sequence
mrna
human
uridine
nucleotides
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JP2021531945A
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English (en)
Japanese (ja)
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JP2022513718A (ja
JP7445657B2 (ja
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Priority claimed from PCT/US2019/064786 external-priority patent/WO2020118115A1/en
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Publication of JP2022513718A5 publication Critical patent/JP2022513718A5/ja
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JP2021531945A 2018-12-06 2019-12-05 オルニチントランスカルバミラーゼ欠損症を処置するための組成物および方法 Active JP7445657B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862776302P 2018-12-06 2018-12-06
US62/776,302 2018-12-06
PCT/US2019/064786 WO2020118115A1 (en) 2018-12-06 2019-12-05 Compositions and methods for treating ornithine transcarbamylase deficiency

Publications (3)

Publication Number Publication Date
JP2022513718A JP2022513718A (ja) 2022-02-09
JP2022513718A5 true JP2022513718A5 (enExample) 2022-12-12
JP7445657B2 JP7445657B2 (ja) 2024-03-07

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JP2021531945A Active JP7445657B2 (ja) 2018-12-06 2019-12-05 オルニチントランスカルバミラーゼ欠損症を処置するための組成物および方法

Country Status (9)

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US (3) US11685906B2 (enExample)
EP (2) EP3891274B1 (enExample)
JP (1) JP7445657B2 (enExample)
AU (2) AU2019394996B2 (enExample)
CA (1) CA3122080A1 (enExample)
ES (1) ES2960692T3 (enExample)
HU (1) HUE064076T2 (enExample)
PL (1) PL3891274T3 (enExample)
WO (1) WO2020118115A1 (enExample)

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WO2023028469A2 (en) * 2021-08-23 2023-03-02 The Board Of Trustees Of The Leland Stanford Junior University Targeted integration at beta-globin locus in human hematopoietic stem and progenitor cells

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