JP2021512906A5 - - Google Patents

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Publication number
JP2021512906A5
JP2021512906A5 JP2020542621A JP2020542621A JP2021512906A5 JP 2021512906 A5 JP2021512906 A5 JP 2021512906A5 JP 2020542621 A JP2020542621 A JP 2020542621A JP 2020542621 A JP2020542621 A JP 2020542621A JP 2021512906 A5 JP2021512906 A5 JP 2021512906A5
Authority
JP
Japan
Prior art keywords
salt
patient
use according
migalastat
pregnancy
Prior art date
Application number
JP2020542621A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021512906A (ja
JP7555818B2 (ja
JPWO2019157047A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/016841 external-priority patent/WO2019157047A1/en
Publication of JP2021512906A publication Critical patent/JP2021512906A/ja
Publication of JP2021512906A5 publication Critical patent/JP2021512906A5/ja
Publication of JPWO2019157047A5 publication Critical patent/JPWO2019157047A5/ja
Priority to JP2024112288A priority Critical patent/JP2024161361A/ja
Application granted granted Critical
Publication of JP7555818B2 publication Critical patent/JP7555818B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2020542621A 2018-02-06 2019-02-06 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用 Active JP7555818B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024112288A JP2024161361A (ja) 2018-02-06 2024-07-12 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862626955P 2018-02-06 2018-02-06
US62/626,955 2018-02-06
PCT/US2019/016841 WO2019157047A1 (en) 2018-02-06 2019-02-06 Use of migalastat for treating fabry disease in pregnant patients

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024112288A Division JP2024161361A (ja) 2018-02-06 2024-07-12 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用

Publications (4)

Publication Number Publication Date
JP2021512906A JP2021512906A (ja) 2021-05-20
JP2021512906A5 true JP2021512906A5 (https=) 2022-02-15
JPWO2019157047A5 JPWO2019157047A5 (https=) 2022-02-15
JP7555818B2 JP7555818B2 (ja) 2024-09-25

Family

ID=65494618

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020542621A Active JP7555818B2 (ja) 2018-02-06 2019-02-06 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用
JP2024112288A Pending JP2024161361A (ja) 2018-02-06 2024-07-12 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024112288A Pending JP2024161361A (ja) 2018-02-06 2024-07-12 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用

Country Status (8)

Country Link
US (2) US11357784B2 (https=)
EP (2) EP4717319A2 (https=)
JP (2) JP7555818B2 (https=)
KR (1) KR20200128676A (https=)
CN (1) CN111971044A (https=)
AU (2) AU2019217868A1 (https=)
CA (1) CA3090496C (https=)
WO (1) WO2019157047A1 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2573498T3 (es) 2006-05-16 2016-06-08 Amicus Therapeutics, Inc. Opciones de tratamiento para la enfermedad de Fabry
SI3470077T1 (sl) 2008-02-12 2020-12-31 Amicus Therapeutics, Inc. Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
CA3224537C (en) 2017-05-30 2025-09-09 Amicus Therapeutics, Inc. USE OF MIGALASTAT IN THE TREATMENT OF PATIENTS WITH FABRY DISEASE AND RENAL FAILURE
CA3090496C (en) 2018-02-06 2024-03-26 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
EP4282472A3 (en) * 2018-08-20 2024-02-21 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
EP3851105B1 (en) 2019-08-07 2026-03-04 Amicus Therapeutics, Inc. Migalastat for use in treating fabry disease in patients having a mutation in the gla gene
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same

Family Cites Families (25)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
SG155257A1 (en) * 2004-09-24 2009-09-30 Beth Israel Hospital Methods of diagnosing and treating complications of pregnancy
PL2027137T3 (pl) 2005-06-08 2015-08-31 Amicus Therapeutics Inc Oczyszczanie imino- i aminocukrów
ES2573498T3 (es) 2006-05-16 2016-06-08 Amicus Therapeutics, Inc. Opciones de tratamiento para la enfermedad de Fabry
AU2008232614A1 (en) 2007-03-30 2008-10-09 Amicus Therapeutics, Inc. Method for the treatment of Fabry disease using pharmacological chaperones
US9999618B2 (en) 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
EP2150254A4 (en) 2007-04-26 2010-11-10 Amicus Therapeutics Inc DOSAGES FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES WITH PHARMACOLOGICAL CHAPTERONES
SI3470077T1 (sl) 2008-02-12 2020-12-31 Amicus Therapeutics, Inc. Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
US8321148B2 (en) 2008-10-24 2012-11-27 Amicus Therapeutics, Inc. Multiple compartment dosing model
US9206457B2 (en) 2009-05-26 2015-12-08 Amicus Therapeutics, Inc. Utilization of pharmacological chaperones to improve manufacturing and purification of biologics
JP5739898B2 (ja) 2009-11-17 2015-06-24 ベイラー リサーチ インスティテュートBaylor Research Institute 心疾患マーカーとしての尿中トリアオシルセラミド(gb3)
CN103974619B (zh) 2011-03-11 2017-02-15 阿米库斯治疗学公司 治疗法布里病的给药方案
US10155027B2 (en) 2012-07-17 2018-12-18 Amicus Therapeutics, Inc. Alpha-galactosidase A and 1-deoxygalactonojirimycin co-formulation for the treatment of fabry disease
HK1209625A1 (en) 2012-07-17 2016-04-08 Amicus Therapeutics, Inc. Alpha-galactosidase a and 1-deoxygalactonojirimycin co-formulation
KR102004114B1 (ko) 2016-03-22 2019-07-26 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 g9331a 돌연변이를 갖는 환자에서 파브리 질병의 치료 방법
AR109103A1 (es) 2016-07-19 2018-10-31 Amicus Therapeutics Inc Tratamiento de la enfermedad de fabry en pacientes no tratados y tratados previamente con ert
TW201829770A (zh) 2017-01-10 2018-08-16 美商阿米庫斯醫療股份有限公司 用於治療fabry氏病之重組α-半乳糖苷酶A
CA3224537C (en) 2017-05-30 2025-09-09 Amicus Therapeutics, Inc. USE OF MIGALASTAT IN THE TREATMENT OF PATIENTS WITH FABRY DISEASE AND RENAL FAILURE
IL272893B2 (en) 2017-08-28 2024-07-01 Amicus Therapeutics Inc Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease
SMT202400027T1 (it) 2018-02-06 2024-03-13 Amicus Therapeutics Inc Trattamento di pazienti con malattia di fabry classica con migalastat
CA3090496C (en) 2018-02-06 2024-03-26 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
EP4282472A3 (en) 2018-08-20 2024-02-21 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
AR120055A1 (es) 2019-06-11 2022-02-02 Amicus Therapeutics Inc Métodos para tratar la enfermedad de fabry en pacientes que tienen insuficiencia renal
EP3851105B1 (en) 2019-08-07 2026-03-04 Amicus Therapeutics, Inc. Migalastat for use in treating fabry disease in patients having a mutation in the gla gene
FI4103178T3 (fi) 2020-02-10 2026-03-23 Amicus Therapeutics Inc Menetelmiä fabryn taudin hoitamiseksi

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