JP2021500072A5 - - Google Patents

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JP2021500072A5
JP2021500072A5 JP2020542542A JP2020542542A JP2021500072A5 JP 2021500072 A5 JP2021500072 A5 JP 2021500072A5 JP 2020542542 A JP2020542542 A JP 2020542542A JP 2020542542 A JP2020542542 A JP 2020542542A JP 2021500072 A5 JP2021500072 A5 JP 2021500072A5
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nucleic acid
grna
dna endonuclease
dna
acid encoding
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JP2020542542A
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JP2021500072A (ja
JP7482028B2 (ja
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Priority claimed from PCT/US2018/056390 external-priority patent/WO2019079527A1/en
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Priority to JP2023188673A priority Critical patent/JP2024009014A/ja
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JP2020542542A 2017-10-17 2018-10-17 血友病ａに対する遺伝子編集用組成物及び方法 Active JP7482028B2 (ja)

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JP2023188673A JP2024009014A (ja) 2017-10-17 2023-11-02 血友病ａに対する遺伝子編集用組成物及び方法

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US201762573633P 2017-10-17 2017-10-17
US62/573,633 2017-10-17
PCT/US2018/056390 WO2019079527A1 (en) 2017-10-17 2018-10-17 COMPOSITIONS AND METHODS FOR GENETIC EDITION FOR HEMOPHILIA A

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JP2021500072A JP2021500072A (ja) 2021-01-07
JP2021500072A5 true JP2021500072A5 (https=) 2021-11-25
JP7482028B2 JP7482028B2 (ja) 2024-05-13

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JP2020542542A Active JP7482028B2 (ja) 2017-10-17 2018-10-17 血友病ａに対する遺伝子編集用組成物及び方法
JP2023188673A Pending JP2024009014A (ja) 2017-10-17 2023-11-02 血友病ａに対する遺伝子編集用組成物及び方法

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US (3) US20190247517A1 (https=)
EP (1) EP3697907A1 (https=)
JP (2) JP7482028B2 (https=)
KR (1) KR102728416B1 (https=)
CN (1) CN111684070A (https=)
AU (1) AU2018353012B2 (https=)
BR (1) BR112020007502A2 (https=)
CA (1) CA3079172A1 (https=)
IL (1) IL273999A (https=)
MA (1) MA50833A (https=)
MX (1) MX2020004043A (https=)
SG (1) SG11202003464VA (https=)
WO (1) WO2019079527A1 (https=)

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CN119546757A (zh) 2022-05-25 2025-02-28 宏基因组学公司 肝酶表达的补充
WO2024254519A2 (en) * 2023-06-08 2024-12-12 Mammoth Biosciences, Inc. Compositions and methods for the modification of human genes expressed by liver cells
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