JP2021101713A5 - - Google Patents

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Publication number
JP2021101713A5
JP2021101713A5 JP2021042924A JP2021042924A JP2021101713A5 JP 2021101713 A5 JP2021101713 A5 JP 2021101713A5 JP 2021042924 A JP2021042924 A JP 2021042924A JP 2021042924 A JP2021042924 A JP 2021042924A JP 2021101713 A5 JP2021101713 A5 JP 2021101713A5
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JP
Japan
Prior art keywords
mbnl
modified
polypeptide
viral vector
type
Prior art date
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Application number
JP2021042924A
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English (en)
Japanese (ja)
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JP2021101713A (ja
JP7739017B2 (ja
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Priority claimed from PCT/EP2014/057553 external-priority patent/WO2015158365A1/en
Application filed filed Critical
Publication of JP2021101713A publication Critical patent/JP2021101713A/ja
Publication of JP2021101713A5 publication Critical patent/JP2021101713A5/ja
Priority to JP2023072627A priority Critical patent/JP7752148B2/ja
Application granted granted Critical
Publication of JP7739017B2 publication Critical patent/JP7739017B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2021042924A 2014-04-14 2021-03-16 筋強直性ジストロフィーの処置 Active JP7739017B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023072627A JP7752148B2 (ja) 2014-04-14 2023-04-26 筋強直性ジストロフィーの処置

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EPPCT/EP2014/057553 2014-04-14
PCT/EP2014/057553 WO2015158365A1 (en) 2014-04-14 2014-04-14 Treatment of myotonic dystrophy
JP2016562263A JP6953131B2 (ja) 2014-04-14 2015-04-14 筋強直性ジストロフィーの処置

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
JP2016562263A Division JP6953131B2 (ja) 2014-04-14 2015-04-14 筋強直性ジストロフィーの処置

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023072627A Division JP7752148B2 (ja) 2014-04-14 2023-04-26 筋強直性ジストロフィーの処置

Publications (3)

Publication Number Publication Date
JP2021101713A JP2021101713A (ja) 2021-07-15
JP2021101713A5 true JP2021101713A5 (https=) 2021-08-26
JP7739017B2 JP7739017B2 (ja) 2025-09-16

Family

ID=50588655

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2016562263A Active JP6953131B2 (ja) 2014-04-14 2015-04-14 筋強直性ジストロフィーの処置
JP2021042924A Active JP7739017B2 (ja) 2014-04-14 2021-03-16 筋強直性ジストロフィーの処置
JP2023072627A Active JP7752148B2 (ja) 2014-04-14 2023-04-26 筋強直性ジストロフィーの処置

Family Applications Before (1)

Application Number Title Priority Date Filing Date
JP2016562263A Active JP6953131B2 (ja) 2014-04-14 2015-04-14 筋強直性ジストロフィーの処置

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023072627A Active JP7752148B2 (ja) 2014-04-14 2023-04-26 筋強直性ジストロフィーの処置

Country Status (6)

Country Link
US (1) US10799556B2 (https=)
EP (1) EP3145529B1 (https=)
JP (3) JP6953131B2 (https=)
CA (1) CA2944606C (https=)
ES (1) ES2970841T3 (https=)
WO (2) WO2015158365A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2015158365A1 (en) * 2014-04-14 2015-10-22 Association Institut De Myologie Treatment of myotonic dystrophy
CA3150413A1 (en) * 2019-09-12 2021-03-18 Denis Furling NUCLEIC ACID SEQUENCE FOR THE REGULATION OF TRANSGENE EXPRESSION
WO2024249893A1 (en) * 2023-05-31 2024-12-05 The Trustees Of Columbia University In The City Of New York Generation of mature neurons differentiated from pluripotent stem cells

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2019143A1 (en) * 2007-07-23 2009-01-28 Genethon CNS gene delivery using peripheral administration of AAV vectors
WO2010044894A1 (en) * 2008-10-15 2010-04-22 4S3 Bioscience Inc. Methods and compositions for treatment of myotonic dystrophy
WO2015158365A1 (en) * 2014-04-14 2015-10-22 Association Institut De Myologie Treatment of myotonic dystrophy

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