JP2023529054A5 - - Google Patents
Info
- Publication number
- JP2023529054A5 JP2023529054A5 JP2022559694A JP2022559694A JP2023529054A5 JP 2023529054 A5 JP2023529054 A5 JP 2023529054A5 JP 2022559694 A JP2022559694 A JP 2022559694A JP 2022559694 A JP2022559694 A JP 2022559694A JP 2023529054 A5 JP2023529054 A5 JP 2023529054A5
- Authority
- JP
- Japan
- Prior art keywords
- composition according
- raav
- nucleic acid
- composition
- subject
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063003143P | 2020-03-31 | 2020-03-31 | |
| US63/003,143 | 2020-03-31 | ||
| PCT/US2021/024837 WO2021202494A1 (en) | 2020-03-31 | 2021-03-30 | Aav capsids variants and uses thereof |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023529054A JP2023529054A (ja) | 2023-07-07 |
| JP2023529054A5 true JP2023529054A5 (https=) | 2024-04-10 |
Family
ID=75870702
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022559694A Pending JP2023529054A (ja) | 2020-03-31 | 2021-03-30 | Ａａｖキャプシドバリアントおよびその使用 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20230138766A1 (https=) |
| EP (1) | EP4126911A1 (https=) |
| JP (1) | JP2023529054A (https=) |
| KR (1) | KR20230113689A (https=) |
| CN (1) | CN115698039A (https=) |
| AR (1) | AR122404A1 (https=) |
| AU (1) | AU2021248577A1 (https=) |
| BR (1) | BR112022019304A2 (https=) |
| CA (1) | CA3177182A1 (https=) |
| CO (1) | CO2022015313A2 (https=) |
| IL (1) | IL296765A (https=) |
| MX (1) | MX2022012279A (https=) |
| TW (1) | TW202204377A (https=) |
| WO (1) | WO2021202494A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US8734809B2 (en) | 2009-05-28 | 2014-05-27 | University Of Massachusetts | AAV's and uses thereof |
| EP4169576A1 (en) | 2018-03-23 | 2023-04-26 | University of Massachusetts | Gene therapeutics for treating bone disorders |
| KR20240095539A (ko) | 2021-10-08 | 2024-06-25 | 디노 테라퓨틱스, 인코포레이티드 | 캡시드 변이체 및 이의 사용 방법 |
| WO2024020376A1 (en) * | 2022-07-22 | 2024-01-25 | University Of Massachusetts | Aav-mediated delivery of osteoblast/osteoclast-regulating mirnas for osteoporosis therapy |
Family Cites Families (25)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5549910A (en) | 1989-03-31 | 1996-08-27 | The Regents Of The University Of California | Preparation of liposome and lipid complex compositions |
| US5252334A (en) | 1989-09-08 | 1993-10-12 | Cygnus Therapeutic Systems | Solid matrix system for transdermal drug delivery |
| JP3218637B2 (ja) | 1990-07-26 | 2001-10-15 | 大正製薬株式会社 | 安定なリポソーム水懸濁液 |
| JP2958076B2 (ja) | 1990-08-27 | 1999-10-06 | 株式会社ビタミン研究所 | 遺伝子導入用多重膜リポソーム及び遺伝子捕捉多重膜リポソーム製剤並びにその製法 |
| US5399363A (en) | 1991-01-25 | 1995-03-21 | Eastman Kodak Company | Surface modified anticancer nanoparticles |
| US5478745A (en) | 1992-12-04 | 1995-12-26 | University Of Pittsburgh | Recombinant viral vector system |
| US5543158A (en) | 1993-07-23 | 1996-08-06 | Massachusetts Institute Of Technology | Biodegradable injectable nanoparticles |
| US5741516A (en) | 1994-06-20 | 1998-04-21 | Inex Pharmaceuticals Corporation | Sphingosomes for enhanced drug delivery |
| US5795587A (en) | 1995-01-23 | 1998-08-18 | University Of Pittsburgh | Stable lipid-comprising drug delivery complexes and methods for their production |
| US5697899A (en) | 1995-02-07 | 1997-12-16 | Gensia | Feedback controlled drug delivery system |
| IE80468B1 (en) | 1995-04-04 | 1998-07-29 | Elan Corp Plc | Controlled release biodegradable nanoparticles containing insulin |
| US5738868A (en) | 1995-07-18 | 1998-04-14 | Lipogenics Ltd. | Liposome compositions and kits therefor |
| US6001650A (en) | 1995-08-03 | 1999-12-14 | Avigen, Inc. | High-efficiency wild-type-free AAV helper functions |
| US5656016A (en) | 1996-03-18 | 1997-08-12 | Abbott Laboratories | Sonophoretic drug delivery system |
| US5797898A (en) | 1996-07-02 | 1998-08-25 | Massachusetts Institute Of Technology | Microchip drug delivery devices |
| US5783208A (en) | 1996-07-19 | 1998-07-21 | Theratech, Inc. | Transdermal drug delivery matrix for coadministering estradiol and another steroid |
| US5779708A (en) | 1996-08-15 | 1998-07-14 | Cyberdent, Inc. | Intraosseous drug delivery device and method |
| EP0931158A1 (en) | 1996-09-06 | 1999-07-28 | The Trustees Of The University Of Pennsylvania | An inducible method for production of recombinant adeno-associated viruses utilizing t7 polymerase |
| US6177403B1 (en) | 1996-10-21 | 2001-01-23 | The Trustees Of The University Of Pennsylvania | Compositions, methods, and apparatus for delivery of a macromolecular assembly to an extravascular tissue of an animal |
| US6156303A (en) | 1997-06-11 | 2000-12-05 | University Of Washington | Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom |
| MX359371B (es) | 2001-11-13 | 2018-09-25 | Univ Pennsylvania | Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo. |
| WO2015164786A1 (en) | 2014-04-25 | 2015-10-29 | University Of Massachusetts | Recombinant aav vectors useful for reducing immunity against transgene products |
| LT3137497T (lt) * | 2014-05-02 | 2021-07-26 | Genzyme Corporation | Aav vektoriai, skirti tinklainės ir cns genų terapijai |
| US20200316221A1 (en) * | 2016-10-13 | 2020-10-08 | University Of Massachusetts | Aav capsid designs |
| AU2017341849B2 (en) * | 2016-10-13 | 2024-03-21 | University Of Massachusetts | AAV capsid designs |
-
2021
- 2021-03-30 WO PCT/US2021/024837 patent/WO2021202494A1/en not_active Ceased
- 2021-03-30 JP JP2022559694A patent/JP2023529054A/ja active Pending
- 2021-03-30 AU AU2021248577A patent/AU2021248577A1/en active Pending
- 2021-03-30 MX MX2022012279A patent/MX2022012279A/es unknown
- 2021-03-30 AR ARP210100790A patent/AR122404A1/es unknown
- 2021-03-30 TW TW110111670A patent/TW202204377A/zh unknown
- 2021-03-30 CA CA3177182A patent/CA3177182A1/en active Pending
- 2021-03-30 US US17/915,548 patent/US20230138766A1/en active Pending
- 2021-03-30 CN CN202180025786.0A patent/CN115698039A/zh active Pending
- 2021-03-30 BR BR112022019304A patent/BR112022019304A2/pt unknown
- 2021-03-30 EP EP21724401.1A patent/EP4126911A1/en active Pending
- 2021-03-30 IL IL296765A patent/IL296765A/en unknown
- 2021-03-30 KR KR1020227037874A patent/KR20230113689A/ko not_active Withdrawn
-
2022
- 2022-10-27 CO CONC2022/0015313A patent/CO2022015313A2/es unknown
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