JP2021074010A5 - - Google Patents

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JP2021074010A5
JP2021074010A5 JP2021015452A JP2021015452A JP2021074010A5 JP 2021074010 A5 JP2021074010 A5 JP 2021074010A5 JP 2021015452 A JP2021015452 A JP 2021015452A JP 2021015452 A JP2021015452 A JP 2021015452A JP 2021074010 A5 JP2021074010 A5 JP 2021074010A5
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pharmaceutical composition
composition according
compound
thalassemia
anemia
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JP7037681B2 (ja
JP2021074010A (ja
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JP2021015452A 2015-04-03 2021-02-03 Tmprss6発現を調節するための化合物及び方法 Active JP7037681B2 (ja)

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JP2022033166A JP2022104917A (ja) 2015-04-03 2022-03-04 Tmprss6発現を調節するための化合物及び方法

Applications Claiming Priority (2)

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US201562142986P 2015-04-03 2015-04-03
US62/142,986 2015-04-03

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JP2017546624A Division JP6833705B2 (ja) 2015-04-03 2016-04-04 Tmprss6発現を調節するための化合物及び方法

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JP2021074010A JP2021074010A (ja) 2021-05-20
JP2021074010A5 true JP2021074010A5 (enExample) 2022-01-06
JP7037681B2 JP7037681B2 (ja) 2022-03-16

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JP2017546624A Active JP6833705B2 (ja) 2015-04-03 2016-04-04 Tmprss6発現を調節するための化合物及び方法
JP2021015452A Active JP7037681B2 (ja) 2015-04-03 2021-02-03 Tmprss6発現を調節するための化合物及び方法
JP2022033166A Withdrawn JP2022104917A (ja) 2015-04-03 2022-03-04 Tmprss6発現を調節するための化合物及び方法

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US (4) US10415038B2 (enExample)
EP (1) EP3277817A4 (enExample)
JP (3) JP6833705B2 (enExample)
KR (1) KR102539587B1 (enExample)
CN (1) CN107429250B (enExample)
AU (1) AU2016244106B2 (enExample)
CA (1) CA2978100C (enExample)
HK (1) HK1249140A1 (enExample)
IL (2) IL253509B2 (enExample)
MX (1) MX2017012426A (enExample)
RU (1) RU2017137410A (enExample)
WO (1) WO2016161429A1 (enExample)

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CN115247173B (zh) * 2021-11-11 2025-11-11 南京启真基因工程有限公司 构建tmprss6基因突变的缺铁性贫血猪核移植供体细胞的基因编辑系统及其应用
TWI868755B (zh) 2022-06-24 2025-01-01 丹麥商諾佛 儂迪克股份有限公司 抑制跨膜絲胺酸蛋白酶6(tmprss6)表現的組成物及方法
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WO2024060649A1 (zh) * 2022-09-29 2024-03-28 广州必贝特医药股份有限公司 用于抑制TMPRSS6基因表达的siRNA或其盐、药物及其应用
WO2024200512A1 (en) 2023-03-27 2024-10-03 Silence Therapeutics Gmbh Compounds and compositions for use in stem cell transplantation
TW202527968A (zh) * 2024-01-08 2025-07-16 大陸商上海舶望製藥有限公司 用於抑制跨膜絲氨酸蛋白酶6(tmprss6)表達的組合物和方法
WO2025206092A1 (ja) * 2024-03-27 2025-10-02 田辺三菱製薬株式会社 Myoregulin発現を調節するための化合物及び医薬組成物

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