JP2020527329A5 - - Google Patents

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Publication number
JP2020527329A5
JP2020527329A5 JP2019567349A JP2019567349A JP2020527329A5 JP 2020527329 A5 JP2020527329 A5 JP 2020527329A5 JP 2019567349 A JP2019567349 A JP 2019567349A JP 2019567349 A JP2019567349 A JP 2019567349A JP 2020527329 A5 JP2020527329 A5 JP 2020527329A5
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JP
Japan
Prior art keywords
b4galt1
nucleic acid
seq
sequence
pharmaceutical composition
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2019567349A
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English (en)
Japanese (ja)
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JP2020527329A (ja
JP7661009B2 (ja
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Priority claimed from PCT/US2018/035806 external-priority patent/WO2018226560A1/en
Publication of JP2020527329A publication Critical patent/JP2020527329A/ja
Publication of JP2020527329A5 publication Critical patent/JP2020527329A5/ja
Priority to JP2023078115A priority Critical patent/JP2023113657A/ja
Application granted granted Critical
Publication of JP7661009B2 publication Critical patent/JP7661009B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2019567349A 2017-06-05 2018-06-04 B4galt1バリアント及びその使用 Active JP7661009B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023078115A JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762515140P 2017-06-05 2017-06-05
US62/515,140 2017-06-05
US201762550161P 2017-08-25 2017-08-25
US62/550,161 2017-08-25
US201862659344P 2018-04-18 2018-04-18
US62/659,344 2018-04-18
PCT/US2018/035806 WO2018226560A1 (en) 2017-06-05 2018-06-04 B4galt1 variants and uses thereof

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023078115A Division JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Publications (3)

Publication Number Publication Date
JP2020527329A JP2020527329A (ja) 2020-09-10
JP2020527329A5 true JP2020527329A5 (enExample) 2021-07-26
JP7661009B2 JP7661009B2 (ja) 2025-04-14

Family

ID=62705750

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2019567349A Active JP7661009B2 (ja) 2017-06-05 2018-06-04 B4galt1バリアント及びその使用
JP2023078115A Pending JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023078115A Pending JP2023113657A (ja) 2017-06-05 2023-05-10 B4galt1バリアント及びその使用

Country Status (14)

Country Link
US (3) US10738284B2 (enExample)
EP (1) EP3635102B1 (enExample)
JP (2) JP7661009B2 (enExample)
KR (1) KR102624979B1 (enExample)
CN (1) CN110997906B (enExample)
AU (1) AU2018282072B2 (enExample)
CA (1) CA3065938A1 (enExample)
DK (1) DK3635102T3 (enExample)
ES (1) ES3049196T3 (enExample)
FI (1) FI3635102T3 (enExample)
IL (1) IL271073B2 (enExample)
MX (1) MX2019014661A (enExample)
SG (1) SG11201911597YA (enExample)
WO (1) WO2018226560A1 (enExample)

Families Citing this family (7)

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DK3635102T3 (da) 2017-06-05 2025-10-27 Regeneron Pharma B4galt1-varianter og anvendelser deraf
WO2021178474A1 (en) * 2020-03-04 2021-09-10 Regeneron Pharmaceuticals, Inc. A rodent model of b4galt1-mediated functions
CA3249744A1 (en) 2022-06-01 2023-12-07 E-Therapeutics Plc EXPRESSION AND/OR FUNCTION INHIBITORS
WO2024121373A1 (en) * 2022-12-09 2024-06-13 Proqr Therapeutics Ii B.V. Antisense oligonucleotides for the treatment of cardiovascular disease
CN115960926A (zh) * 2022-12-30 2023-04-14 南方科技大学 一种mRNA及含有mRNA的药物
WO2025021989A1 (en) * 2023-07-27 2025-01-30 E-Therapeutics Plc Inhibitors of expression and/or function
CN121059826A (zh) * 2025-08-27 2025-12-05 武汉糖智药业有限公司 一种抗体药物偶联物及其制备方法和应用

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