JP2019531754A5 - - Google Patents

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JP2019531754A5
JP2019531754A5 JP2019522537A JP2019522537A JP2019531754A5 JP 2019531754 A5 JP2019531754 A5 JP 2019531754A5 JP 2019522537 A JP2019522537 A JP 2019522537A JP 2019522537 A JP2019522537 A JP 2019522537A JP 2019531754 A5 JP2019531754 A5 JP 2019531754A5
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JP
Japan
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cell
nuclease
cell according
endogenous
endogenous il2rg
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JP2019522537A
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Japanese (ja)
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JP2019531754A (ja
JP7108608B2 (ja
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Priority claimed from PCT/US2017/059197 external-priority patent/WO2018081775A1/en
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Priority to JP2022083035A priority Critical patent/JP2022105621A/ja
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Publication of JP7108608B2 publication Critical patent/JP7108608B2/ja
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JP2019522537A 2016-10-31 2017-10-31 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正 Expired - Fee Related JP7108608B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2022083035A JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662415056P 2016-10-31 2016-10-31
US62/415,056 2016-10-31
PCT/US2017/059197 WO2018081775A1 (en) 2016-10-31 2017-10-31 Gene correction of scid-related genes in hematopoietic stem and progenitor cells

Related Child Applications (1)

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JP2022083035A Division JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

Publications (3)

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JP2019531754A JP2019531754A (ja) 2019-11-07
JP2019531754A5 true JP2019531754A5 (enExample) 2020-09-24
JP7108608B2 JP7108608B2 (ja) 2022-07-28

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ID=62025525

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JP2019522537A Expired - Fee Related JP7108608B2 (ja) 2016-10-31 2017-10-31 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正
JP2022083035A Pending JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

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JP2022083035A Pending JP2022105621A (ja) 2016-10-31 2022-05-20 造血幹細胞および前駆細胞におけるｓｃｉｄ関連遺伝子の遺伝子修正

Country Status (6)

Country Link
US (1) US11020492B2 (enExample)
EP (1) EP3532106A4 (enExample)
JP (2) JP7108608B2 (enExample)
AU (1) AU2017347928A1 (enExample)
CA (1) CA3041668A1 (enExample)
WO (1) WO2018081775A1 (enExample)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11214789B2 (en) 2016-05-03 2022-01-04 Flodesign Sonics, Inc. Concentration and washing of particles with acoustics
KR102828669B1 (ko) * 2019-11-13 2025-07-02 더 리전트 오브 더 유니버시티 오브 캘리포니아 재조합 활성화 유전자 1 (rag1) 중증 복합 면역결핍증 (scid) 을 치료하기 위한 조혈 줄기 세포에서의 렌티바이러스 벡터
CN115279421A (zh) * 2020-01-10 2022-11-01 坚固生物科技公司 用于联合疗法的病毒载体

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