JP2018519811A - 修飾ｃｒｉｓｐｒ ｒｎａ及び修飾単一ｃｒｉｓｐｒ ｒｎａならびにその使用 - Google Patents

修飾ｃｒｉｓｐｒ ｒｎａ及び修飾単一ｃｒｉｓｐｒ ｒｎａならびにその使用 Download PDF

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JP2018519811A
JP2018519811A JP2017563986A JP2017563986A JP2018519811A JP 2018519811 A JP2018519811 A JP 2018519811A JP 2017563986 A JP2017563986 A JP 2017563986A JP 2017563986 A JP2017563986 A JP 2017563986A JP 2018519811 A JP2018519811 A JP 2018519811A
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compound
modified
crrna
scrrna
sugar moiety
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JP2018519811A5 (enExample
Inventor
ラフダー，メグダッド
プラカシュ，タジャ・ピー
スウェイジ，エリック・イー
ベネット，フランク・シー
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Ionis Pharmaceuticals Inc
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Ionis Pharmaceuticals Inc
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  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Saccharide Compounds (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Measuring Or Testing Involving Enzymes Or Micro-Organisms (AREA)
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JP2017563986A 2015-06-29 2016-06-29 修飾ｃｒｉｓｐｒ ｒｎａ及び修飾単一ｃｒｉｓｐｒ ｒｎａならびにその使用 Pending JP2018519811A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201562186363P 2015-06-29 2015-06-29
US62/186,363 2015-06-29
US201562233281P 2015-09-25 2015-09-25
US62/233,281 2015-09-25
US201562256649P 2015-11-17 2015-11-17
US62/256,649 2015-11-17
PCT/US2016/040191 WO2017004261A1 (en) 2015-06-29 2016-06-29 Modified crispr rna and modified single crispr rna and uses thereof

Publications (2)

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JP2018519811A true JP2018519811A (ja) 2018-07-26
JP2018519811A5 JP2018519811A5 (enExample) 2019-08-08

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JP2017563986A Pending JP2018519811A (ja) 2015-06-29 2016-06-29 修飾ｃｒｉｓｐｒ ｒｎａ及び修飾単一ｃｒｉｓｐｒ ｒｎａならびにその使用

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US (2) US11414657B2 (enExample)
EP (2) EP3313989B1 (enExample)
JP (1) JP2018519811A (enExample)
AU (1) AU2016285724A1 (enExample)
CA (1) CA2990699A1 (enExample)
WO (1) WO2017004261A1 (enExample)

Cited By (1)

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JP2023526057A (ja) * 2020-05-12 2023-06-20 ユニバーシティー オブ マサチューセッツ Ｃｒｉｓｐｒゲノム編集のための修飾されたガイドｒｎａ

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