JP2018500311A5 - - Google Patents

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Publication number
JP2018500311A5
JP2018500311A5 JP2017531531A JP2017531531A JP2018500311A5 JP 2018500311 A5 JP2018500311 A5 JP 2018500311A5 JP 2017531531 A JP2017531531 A JP 2017531531A JP 2017531531 A JP2017531531 A JP 2017531531A JP 2018500311 A5 JP2018500311 A5 JP 2018500311A5
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JP
Japan
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vector
item
aav
promoter
vector according
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JP2017531531A
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Japanese (ja)
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JP6754361B2 (ja
JP2018500311A (ja
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Priority claimed from PCT/US2015/066206 external-priority patent/WO2016100575A1/en
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Publication of JP2018500311A5 publication Critical patent/JP2018500311A5/ja
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JP2017531531A 2014-12-16 2015-12-16 若年型バッテン病のための遺伝子療法 Expired - Fee Related JP6754361B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201462092501P 2014-12-16 2014-12-16
US62/092,501 2014-12-16
US201562146793P 2015-04-13 2015-04-13
US62/146,793 2015-04-13
PCT/US2015/066206 WO2016100575A1 (en) 2014-12-16 2015-12-16 Gene therapy for juvenile batten disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2020078099A Division JP2020122004A (ja) 2014-12-16 2020-04-27 若年型バッテン病のための遺伝子療法

Publications (3)

Publication Number Publication Date
JP2018500311A JP2018500311A (ja) 2018-01-11
JP2018500311A5 true JP2018500311A5 (enExample) 2019-01-31
JP6754361B2 JP6754361B2 (ja) 2020-09-09

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JP2017531531A Expired - Fee Related JP6754361B2 (ja) 2014-12-16 2015-12-16 若年型バッテン病のための遺伝子療法
JP2020078099A Pending JP2020122004A (ja) 2014-12-16 2020-04-27 若年型バッテン病のための遺伝子療法

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JP2020078099A Pending JP2020122004A (ja) 2014-12-16 2020-04-27 若年型バッテン病のための遺伝子療法

Country Status (7)

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US (2) US10876134B2 (enExample)
EP (1) EP3233131A1 (enExample)
JP (2) JP6754361B2 (enExample)
CN (1) CN107249646B (enExample)
AU (2) AU2015364636B9 (enExample)
CA (1) CA2967468A1 (enExample)
WO (1) WO2016100575A1 (enExample)

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