JP2015522280A5 - - Google Patents

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Publication number
JP2015522280A5
JP2015522280A5 JP2015520166A JP2015520166A JP2015522280A5 JP 2015522280 A5 JP2015522280 A5 JP 2015522280A5 JP 2015520166 A JP2015520166 A JP 2015520166A JP 2015520166 A JP2015520166 A JP 2015520166A JP 2015522280 A5 JP2015522280 A5 JP 2015522280A5
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JP
Japan
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JP2015520166A
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Japanese (ja)
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JP6366581B2 (ja
JP2015522280A (ja
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Priority claimed from PCT/US2013/031644 external-priority patent/WO2014007858A1/en
Publication of JP2015522280A publication Critical patent/JP2015522280A/ja
Publication of JP2015522280A5 publication Critical patent/JP2015522280A5/ja
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JP2015520166A 2012-07-06 2013-03-14 改変されたアデノ随伴ウイルスベクター組成物 Active JP6366581B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261668839P 2012-07-06 2012-07-06
US61/668,839 2012-07-06
PCT/US2013/031644 WO2014007858A1 (en) 2012-07-06 2013-03-14 Modified adeno-associated virus vector compositions

Publications (3)

Publication Number Publication Date
JP2015522280A JP2015522280A (ja) 2015-08-06
JP2015522280A5 true JP2015522280A5 (enExample) 2016-01-21
JP6366581B2 JP6366581B2 (ja) 2018-08-08

Family

ID=49882407

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2015520166A Active JP6366581B2 (ja) 2012-07-06 2013-03-14 改変されたアデノ随伴ウイルスベクター組成物

Country Status (12)

Country Link
US (2) US9540659B2 (enExample)
EP (1) EP2870237B1 (enExample)
JP (1) JP6366581B2 (enExample)
CN (1) CN104619832B (enExample)
AU (1) AU2013287261B2 (enExample)
BR (1) BR112015000161A2 (enExample)
CA (1) CA2878401C (enExample)
ES (1) ES2703177T3 (enExample)
HK (1) HK1210214A1 (enExample)
IN (1) IN2015KN00074A (enExample)
RU (1) RU2679843C2 (enExample)
WO (1) WO2014007858A1 (enExample)

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CN112553229A (zh) 2014-11-05 2021-03-26 沃雅戈治疗公司 用于治疗帕金森病的aadc多核苷酸
MX2017006217A (es) 2014-11-14 2018-05-02 Voyager Therapeutics Inc Polinucleotidos moduladores.
RU2020108189A (ru) 2014-11-14 2020-03-11 Вояджер Терапьютикс, Инк. Композиции и способы лечения бокового амиотрофического склероза (als)
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US20190000940A1 (en) * 2015-07-31 2019-01-03 Voyager Therapeutics, Inc. Compositions and methods for the treatment of aadc deficiency
WO2017161273A1 (en) * 2016-03-18 2017-09-21 The Children's Hospital Of Philadelphia Therapeutic for treatment of diseases including the central nervous system
US11299751B2 (en) 2016-04-29 2022-04-12 Voyager Therapeutics, Inc. Compositions for the treatment of disease
EP3448874A4 (en) 2016-04-29 2020-04-22 Voyager Therapeutics, Inc. COMPOSITIONS FOR TREATING A DISEASE
AU2017267665C1 (en) 2016-05-18 2023-10-05 Voyager Therapeutics, Inc. Modulatory polynucleotides
BR112018073472A2 (pt) 2016-05-18 2019-08-27 Voyager Therapeutics, Inc. composições e métodos de tratamento da doença de huntington
WO2018044933A1 (en) 2016-08-30 2018-03-08 The Regents Of The University Of California Methods for biomedical targeting and delivery and devices and systems for practicing the same
CA3061652A1 (en) 2017-05-05 2018-11-08 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
CN111108198A (zh) 2017-05-05 2020-05-05 沃雅戈治疗公司 治疗亨廷顿病的组合物和方法
JOP20190269A1 (ar) 2017-06-15 2019-11-20 Voyager Therapeutics Inc بولي نوكليوتيدات aadc لعلاج مرض باركنسون
CN111132626B (zh) 2017-07-17 2024-01-30 沃雅戈治疗公司 轨迹阵列引导系统
AU2018338728B2 (en) 2017-09-29 2025-01-02 Centre National De La Recherche Scientifique (Cnrs) Rescue of central and peripheral neurological phenotype of Friedreich's Ataxia by intravenous delivery
US20200237799A1 (en) 2017-10-16 2020-07-30 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis (als)
CN111479924B (zh) 2017-10-16 2024-06-14 沃雅戈治疗公司 肌萎缩性侧索硬化症(als)的治疗
CN111712569A (zh) * 2017-12-11 2020-09-25 爱迪塔斯医药公司 用于基因编辑的Cpf1-相关方法和组合物
US20190256867A1 (en) 2018-02-01 2019-08-22 Homology Medicines, Inc. Adeno-associated virus compositions for restoring pah gene function and methods of use thereof
US10610606B2 (en) 2018-02-01 2020-04-07 Homology Medicines, Inc. Adeno-associated virus compositions for PAH gene transfer and methods of use thereof
CN112041437A (zh) 2018-02-19 2020-12-04 同源药物公司 用于恢复f8基因功能的腺相关病毒组合物和其使用方法
MX2020010464A (es) 2018-04-03 2021-01-29 Vectores de virus que evitan anticuerpos.
JP7425738B2 (ja) 2018-04-03 2024-01-31 ギンコ バイオワークス インコーポレイテッド 眼組織を標的とするウイルスベクター
US12091435B2 (en) 2018-04-03 2024-09-17 Ginkgo Bioworks, Inc. Antibody-evading virus vectors
AU2019268330A1 (en) 2018-05-15 2020-11-26 Voyager Therapeutics, Inc. Compositions and methods for the treatment of Parkinson's disease
US20210254103A1 (en) * 2018-07-02 2021-08-19 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
EP3856762A1 (en) 2018-09-28 2021-08-04 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
JP7698583B2 (ja) 2019-03-21 2025-06-25 ギンコ バイオワークス インコーポレイテッド 組換えアデノ随伴ウイルスベクター
MX2021013913A (es) * 2019-05-14 2022-03-17 Univ Duke Composiciones y metodos para el tratamiento de enfermedades mediadas por atpasa.
AR122285A1 (es) * 2019-07-18 2022-08-31 Lysogene Composiciones y métodos para el tratamiento de la enfermedad de sanfilippo y otros trastornos
IL292297A (en) 2019-10-17 2022-06-01 Stridebio Inc Adeno-associated viral vectors for treatment of niemann-pick disease type c
TW202140791A (zh) 2020-01-13 2021-11-01 美商霍蒙拉奇醫藥公司 治療苯酮尿症之方法
CN115768900A (zh) * 2020-05-11 2023-03-07 戈迪安生物技术公司 病毒递送媒剂选择
TW202208632A (zh) 2020-05-27 2022-03-01 美商同源醫藥公司 用於恢復pah基因功能的腺相關病毒組成物及其使用方法
CA3189878A1 (en) 2020-08-19 2022-02-24 Colin O'BANION Adeno-associated virus vectors for treatment of rett syndrome
KR20230142576A (ko) * 2021-02-05 2023-10-11 메이즈 테라퓨틱스, 인코퍼레이티드 스터퍼 폴리뉴클레오티드 서열을 포함하는 벡터
US20240218397A1 (en) * 2021-05-04 2024-07-04 Regenxbio Inc. Novel aav vectors and methods and uses thereof
CN119654414A (zh) * 2022-08-09 2025-03-18 谢菲尔德大学 病毒载体

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WO2009134681A2 (en) * 2008-04-30 2009-11-05 The Trustees Of The University Of Pennsylvania Aav7 viral vectors for targeted delivery of rpe cells
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