JP2012509258A - 核酸送達系のための分岐カチオン性脂質 - Google Patents

核酸送達系のための分岐カチオン性脂質 Download PDF

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JP2012509258A
JP2012509258A JP2011536348A JP2011536348A JP2012509258A JP 2012509258 A JP2012509258 A JP 2012509258A JP 2011536348 A JP2011536348 A JP 2011536348A JP 2011536348 A JP2011536348 A JP 2011536348A JP 2012509258 A JP2012509258 A JP 2012509258A
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ザオ,ホン
ヤン,ウェイリ
シー,リャンジュン
ウー,デシュン
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エンゾン ファーマシューティカルズ,インコーポレーテッド
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JP2011536348A 2008-11-17 2009-07-31 核酸送達系のための分岐カチオン性脂質 Withdrawn JP2012509258A (ja)

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US11530708P 2008-11-17 2008-11-17
US61/115,307 2008-11-17
PCT/US2009/052462 WO2010056403A1 (en) 2008-11-17 2009-07-31 Branched cationic lipids for nucleic acids delivery system

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US (1) US20110305769A1 (https=)
EP (1) EP2350296A4 (https=)
JP (1) JP2012509258A (https=)
CN (1) CN102216462A (https=)
CA (1) CA2742689A1 (https=)
TW (1) TW201019969A (https=)
WO (1) WO2010056403A1 (https=)

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JP2012509272A (ja) * 2008-11-17 2012-04-19 エンゾン ファーマシューティカルズ,インコーポレーテッド 核酸送達系のための放出性カチオン脂質
JP2015520195A (ja) * 2012-06-08 2015-07-16 シャイアー ヒューマン ジェネティック セラピーズ インコーポレイテッド 非肺標的細胞へのmRNAの経肺送達
JP2015530382A (ja) * 2012-08-28 2015-10-15 メディカル リサーチ カウンシル ナノ粒子製剤
JP2019535808A (ja) * 2016-10-17 2019-12-12 南京▲緑▼叶制▲薬▼有限公司 bcl−2を抑制するアンチセンスオリゴヌクレオチドの脂質ナノ粒子及びその調製方法

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EA034103B1 (ru) 2013-10-22 2019-12-27 Транслейт Био, Инк. СПОСОБ ЛЕЧЕНИЯ ФЕНИЛКЕТОНУРИИ С ПРИМЕНЕНИЕМ мРНК
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JP6457696B2 (ja) 2015-07-23 2019-01-23 アンスティテュ・キュリInstitut Curie 癌を処置するためのDbait分子とPARPインヒビターとの組合せの使用
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KR102778110B1 (ko) * 2017-04-20 2025-03-10 신테나 아게 트리시클로-dna 뉴클레오시드를 포함하는 변형 올리고머 화합물 및 그의 용도
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