HK1158955A1 - Combination therapy for treating protein deficiency disorders - Google Patents
Combination therapy for treating protein deficiency disordersInfo
- Publication number
- HK1158955A1 HK1158955A1 HK11113493.2A HK11113493A HK1158955A1 HK 1158955 A1 HK1158955 A1 HK 1158955A1 HK 11113493 A HK11113493 A HK 11113493A HK 1158955 A1 HK1158955 A1 HK 1158955A1
- Authority
- HK
- Hong Kong
- Prior art keywords
- combination therapy
- protein deficiency
- deficiency disorders
- treating protein
- treating
- Prior art date
Links
Classifications
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K38/00—Medicinal preparations containing peptides
- A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
- A61K38/43—Enzymes; Proenzymes; Derivatives thereof
- A61K38/46—Hydrolases (3)
- A61K38/47—Hydrolases (3) acting on glycosyl compounds (3.2), e.g. cellulases, lactases
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
- A61K31/445—Non condensed piperidines, e.g. piperocaine
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/46—8-Azabicyclo [3.2.1] octane; Derivatives thereof, e.g. atropine, cocaine
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
- A61P3/02—Nutrients, e.g. vitamins, minerals
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P3/00—Drugs for disorders of the metabolism
- A61P3/08—Drugs for disorders of the metabolism for glucose homeostasis
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/14—Vasoprotectives; Antihaemorrhoidals; Drugs for varicose therapy; Capillary stabilisers
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/0012—Galenical forms characterised by the site of application
- A61K9/0019—Injectable compositions; Intramuscular, intravenous, arterial, subcutaneous administration; Compositions to be administered through the skin in an invasive manner
Landscapes
- Health & Medical Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Animal Behavior & Ethology (AREA)
- Pharmacology & Pharmacy (AREA)
- General Health & Medical Sciences (AREA)
- Veterinary Medicine (AREA)
- Chemical & Material Sciences (AREA)
- Public Health (AREA)
- Medicinal Chemistry (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Engineering & Computer Science (AREA)
- Epidemiology (AREA)
- General Chemical & Material Sciences (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Chemical Kinetics & Catalysis (AREA)
- Organic Chemistry (AREA)
- Diabetes (AREA)
- Emergency Medicine (AREA)
- Hematology (AREA)
- Obesity (AREA)
- Gastroenterology & Hepatology (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
- Immunology (AREA)
- Heart & Thoracic Surgery (AREA)
- Cardiology (AREA)
- Nutrition Science (AREA)
- Vascular Medicine (AREA)
- Endocrinology (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Enzymes And Modification Thereof (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicinal Preparation (AREA)
Applications Claiming Priority (1)
Application Number | Priority Date | Filing Date | Title |
---|---|---|---|
US44413603P | 2003-01-31 | 2003-01-31 |
Publications (1)
Publication Number | Publication Date |
---|---|
HK1158955A1 true HK1158955A1 (en) | 2012-07-27 |
Family
ID=32850826
Family Applications (4)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
HK11113493.2A HK1158955A1 (en) | 2003-01-31 | 2011-12-14 | Combination therapy for treating protein deficiency disorders |
HK12109528.8A HK1168778A1 (en) | 2003-01-31 | 2012-09-27 | Combination therapy for treating protein deficiency disorders |
HK12109801.6A HK1169033A1 (en) | 2003-01-31 | 2012-10-05 | Combination therapy for treating protein deficiency disorders |
HK15107877.6A HK1207291A1 (en) | 2003-01-31 | 2015-08-14 | Combination therapy for treating protein deficiency disorders |
Family Applications After (3)
Application Number | Title | Priority Date | Filing Date |
---|---|---|---|
HK12109528.8A HK1168778A1 (en) | 2003-01-31 | 2012-09-27 | Combination therapy for treating protein deficiency disorders |
HK12109801.6A HK1169033A1 (en) | 2003-01-31 | 2012-10-05 | Combination therapy for treating protein deficiency disorders |
HK15107877.6A HK1207291A1 (en) | 2003-01-31 | 2015-08-14 | Combination therapy for treating protein deficiency disorders |
Country Status (16)
Country | Link |
---|---|
US (4) | US20040180419A1 (fr) |
EP (6) | EP1589993B1 (fr) |
JP (5) | JP5589165B2 (fr) |
CN (4) | CN1756558B (fr) |
BR (1) | BRPI0407001A (fr) |
CA (3) | CA2814774C (fr) |
CY (5) | CY1116215T1 (fr) |
DK (5) | DK1589993T3 (fr) |
ES (6) | ES2541952T3 (fr) |
HK (4) | HK1158955A1 (fr) |
HU (2) | HUE033381T2 (fr) |
IL (6) | IL169562A (fr) |
MX (2) | MX344587B (fr) |
PT (5) | PT2444102E (fr) |
SI (5) | SI2857036T1 (fr) |
WO (1) | WO2004069190A2 (fr) |
Families Citing this family (55)
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US20040204379A1 (en) * | 2000-06-19 | 2004-10-14 | Cheng Seng H. | Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases |
US20020095135A1 (en) * | 2000-06-19 | 2002-07-18 | David Meeker | Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases |
US7138262B1 (en) | 2000-08-18 | 2006-11-21 | Shire Human Genetic Therapies, Inc. | High mannose proteins and methods of making high mannose proteins |
CA2814774C (fr) | 2003-01-31 | 2016-03-22 | Mount Sinai School Of Medicine Of New York University | Therapie combinee destinee au traitement de troubles associes a une carence proteique |
FR2861991B1 (fr) | 2003-11-07 | 2008-01-18 | Centre Nat Rech Scient | Utilisation d'inhibiteurs de glucosidase pour une therapie de la mucoviscidose |
US20050256168A1 (en) * | 2004-04-28 | 2005-11-17 | Block Timothy M | Compositions for oral administration for the treatment of interferon-responsive disorders |
EP3782655A1 (fr) * | 2005-05-17 | 2021-02-24 | Amicus Therapeutics, Inc. | Procédé pour le traitement de la maladie de pompe au moyen de 1-désoxynojirimycine et de ses dérivés |
AU2006254796B2 (en) | 2005-06-08 | 2012-08-16 | Amicus Therapeutics, Inc. | Treatment of CNS disorders associated with mutations in genes encoding lysosomal enzymes |
PT1986612E (pt) | 2006-02-07 | 2012-11-06 | Shire Human Genetic Therapies | Composição estável de glucocerebrosidase |
ES2709445T3 (es) | 2006-05-16 | 2019-04-16 | Amicus Therapeutics Inc | Opciones de tratamiento para la enfermedad de Fabry |
US7829579B2 (en) * | 2006-06-23 | 2010-11-09 | Amicus Therapeutics, Inc. | Method for the treatment of neurological disorders by enhancing the activity of β-glucocerebrosidase |
CA2657238A1 (fr) * | 2006-07-27 | 2008-01-31 | University Of Florida Research Foundation, Inc. | Compositions et methodes destinees a traiter et/ou a prevenir des maladies ophtalmologiques |
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WO2008134628A2 (fr) * | 2007-04-26 | 2008-11-06 | Amicus Therapeutics, Inc. | Schémas posologiques pour le traitement de maladies de stockage lysosomal en utilisant des chaperons pharmacologiques |
CA2712593A1 (fr) * | 2008-02-01 | 2009-08-13 | The Scripps Research Institute | Methodes de traitement d'un etat pathologique caracterise par un dysfonctionnement de l'homeostasie des proteines |
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PT3626257T (pt) | 2010-06-25 | 2021-11-12 | Shire Human Genetic Therapies | Métodos e composições de arilsulfatase a para a administração no snc |
SG193379A1 (en) * | 2011-03-11 | 2013-10-30 | Amicus Therapeutics Inc | Dosing regimens for the treatment of fabry disease |
JP6320931B2 (ja) * | 2011-12-22 | 2018-05-09 | セントジーン アイピー ゲーエムベーハー | リソソーム酵素を再構成する能力を有する化合物ならびにアンブロキソールおよび/またはアンブロキソールの誘導体の組み合わせ |
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KR20140135222A (ko) | 2012-03-07 | 2014-11-25 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 폼페병의 치료를 위한 고농도 알파-글루코시다제 조성물 |
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TW201806597A (zh) | 2016-07-19 | 2018-03-01 | 美商阿米庫斯醫療股份有限公司 | 治療ert初治的和已經歷ert的患者中之法布瑞氏症 |
CN114617999A (zh) | 2017-03-27 | 2022-06-14 | 里珍纳龙药品有限公司 | 灭菌方法 |
JP7066157B2 (ja) | 2017-06-14 | 2022-05-13 | 学校法人 明治薬科大学 | ファブリー病治療用医薬の組合せ物及びその利用 |
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CA2814774C (fr) * | 2003-01-31 | 2016-03-22 | Mount Sinai School Of Medicine Of New York University | Therapie combinee destinee au traitement de troubles associes a une carence proteique |
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EP3782655A1 (fr) * | 2005-05-17 | 2021-02-24 | Amicus Therapeutics, Inc. | Procédé pour le traitement de la maladie de pompe au moyen de 1-désoxynojirimycine et de ses dérivés |
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-
2004
- 2004-02-02 CA CA2814774A patent/CA2814774C/fr not_active Expired - Fee Related
- 2004-02-02 CA CA2514642A patent/CA2514642C/fr not_active Expired - Fee Related
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