ES2920850T3 - Procedimientos y composiciones para el tratamiento de enfermedades oculares genéticas - Google Patents
Procedimientos y composiciones para el tratamiento de enfermedades oculares genéticas Download PDFInfo
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| JP7046828B2 (ja) | 2016-04-15 | 2022-04-04 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 滲出型加齢性黄斑変性の治療のための組成物 |
| EP3827812B1 (en) | 2016-07-29 | 2025-10-29 | The Regents of the University of California | Adeno-associated virus virions with variant capsid and methods of use thereof |
| WO2018045347A1 (en) * | 2016-09-02 | 2018-03-08 | Spark Therapeutics, Inc. | Methods and vectors for treating cns disorders |
| WO2019006182A1 (en) * | 2017-06-30 | 2019-01-03 | The Regents Of The University Of California | VIRIONS OF ADENO-ASSOCIATED VIRUSES OF CAPSID VARIANTS AND METHODS OF USE THEREOF |
| JP7221275B2 (ja) | 2017-08-03 | 2023-02-13 | ボイジャー セラピューティクス インコーポレイテッド | Ａａｖを送達するための組成物および方法 |
| JP2020534788A (ja) | 2017-08-28 | 2020-12-03 | ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニア | アデノ随伴ウイルスカプシド変異体及びその使用方法 |
| NZ763617A (en) * | 2017-10-16 | 2026-01-30 | Vigeneron Gmbh | Aav vectors |
| SG11202003778QA (en) * | 2017-11-13 | 2020-05-28 | Univ California | Compositions and methods for enhancing visual function |
| MA50877A (fr) | 2017-11-21 | 2020-09-30 | Bayer Healthcare Llc | Matériaux et méthodes pour le traitement de la rétinite pigmentaire autosomique dominante |
| CN112105630A (zh) * | 2018-02-15 | 2020-12-18 | T·比约尔克隆德 | 经修饰的病毒衣壳 |
| US12558434B2 (en) | 2018-02-20 | 2026-02-24 | The Trustees Of The University Of Pennsylvania | Compositions for treatment of wet age-related macular degeneration |
| US12421525B2 (en) | 2018-02-28 | 2025-09-23 | University of Pittsburgh—of the Commonwealth System of Higher Education | Conjugates comprising AAVs and CAS9 polypeptides |
| SG11202011296VA (en) | 2018-05-15 | 2020-12-30 | Voyager Therapeutics Inc | Compositions and methods for the treatment of parkinson's disease |
| TW202015742A (zh) | 2018-05-15 | 2020-05-01 | 美商航海家醫療公司 | 投遞腺相關病毒（ａａｖ）之組成物和方法 |
| US12060567B2 (en) | 2018-06-13 | 2024-08-13 | Voyager Therapeutics, Inc. | Engineered untranslated regions (UTR) for AAV production |
| AU2019310459A1 (en) | 2018-07-24 | 2021-02-18 | Voyager Therapeutics, Inc. | Systems and methods for producing gene therapy formulations |
| US12281321B2 (en) | 2018-09-28 | 2025-04-22 | Voyager Therapeutics, Inc. | Frataxin expression constructs having engineered promoters and methods of use thereof |
| WO2020072849A1 (en) | 2018-10-04 | 2020-04-09 | Voyager Therapeutics, Inc. | Methods for measuring the titer and potency of viral vector particles |
| WO2020072844A1 (en) | 2018-10-05 | 2020-04-09 | Voyager Therapeutics, Inc. | Engineered nucleic acid constructs encoding aav production proteins |
| WO2020077165A1 (en) | 2018-10-12 | 2020-04-16 | Voyager Therapeutics, Inc. | Compositions and methods for delivery of aav |
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| JP2022522995A (ja) | 2019-01-18 | 2022-04-21 | ボイジャー セラピューティクス インコーポレイテッド | Ａａｖ粒子を生成するための方法及びシステム |
| EP4667578A3 (en) * | 2019-04-03 | 2026-04-01 | REGENXBIO Inc. | Gene therapy for eye pathologies |
| KR20210148333A (ko) * | 2019-04-08 | 2021-12-07 | 더 칠드런스 호스피탈 오브 필라델피아 | Tpp1을 발현하는 aav의 투여를 통한 눈의 리소좀 축적 질환 치료 |
| EP3962536A1 (en) | 2019-04-29 | 2022-03-09 | Voyager Therapeutics, Inc. | Systems and methods for producing baculoviral infected insect cells (biics) in bioreactors |
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| CN114729009A (zh) * | 2019-10-31 | 2022-07-08 | 伯尔尼大学 | 用于眼部基因递送的aav载体变体 |
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| US20090215879A1 (en) * | 2008-02-26 | 2009-08-27 | University Of North Carolina At Chapel Hill | Methods and compositions for adeno-associated virus (aav) with hi loop mutations |
| KR101154374B1 (ko) * | 2009-02-18 | 2012-07-09 | 재단법인 아산사회복지재단 | 표적화된 유전자 전달을 위한 아데노-부속 바이러스 혈청형5 벡터를 포함하는 조성물 |
| US20110052666A1 (en) * | 2009-09-03 | 2011-03-03 | Medtronic, Inc. | Compositions, Methods, and Systems for SIRNA Delivery |
| HRP20171334T1 (hr) * | 2011-04-22 | 2017-11-17 | The Regents Of The University Of California | Virioni adeno-povezanog virusa s kapsid varijantom i postupci njihove upotrebe |
| WO2013159036A1 (en) * | 2012-04-19 | 2013-10-24 | Oregon Health & Science University | Adeno associated virus plasmids and vectors |
| US9567376B2 (en) * | 2013-02-08 | 2017-02-14 | The Trustees Of The University Of Pennsylvania | Enhanced AAV-mediated gene transfer for retinal therapies |
-
2016
- 2016-02-22 CA CA2977355A patent/CA2977355A1/en active Pending
- 2016-02-22 SG SG11201706755SA patent/SG11201706755SA/en unknown
- 2016-02-22 EP EP16753229.0A patent/EP3261440B1/en active Active
- 2016-02-22 US US15/551,869 patent/US10472650B2/en active Active
- 2016-02-22 KR KR1020177026037A patent/KR102655319B1/ko active Active
- 2016-02-22 AU AU2016219789A patent/AU2016219789B2/en active Active
- 2016-02-22 CN CN201680022560.4A patent/CN108347932B/zh active Active
- 2016-02-22 ES ES16753229T patent/ES2920850T3/es active Active
- 2016-02-22 WO PCT/US2016/018970 patent/WO2016134375A1/en not_active Ceased
- 2016-02-22 JP JP2017543944A patent/JP6873907B2/ja active Active
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2017
- 2017-08-18 ZA ZA2017/05628A patent/ZA201705628B/en unknown
- 2017-08-20 SA SA517382162A patent/SA517382162B1/ar unknown
Also Published As
| Publication number | Publication date |
|---|---|
| EP3261440A1 (en) | 2018-01-03 |
| JP2018506980A (ja) | 2018-03-15 |
| EP3261440A4 (en) | 2018-10-31 |
| CN108347932B (zh) | 2022-09-13 |
| BR112017017867A2 (pt) | 2018-04-10 |
| US10472650B2 (en) | 2019-11-12 |
| EP3261440B1 (en) | 2022-04-06 |
| KR102655319B1 (ko) | 2024-04-04 |
| CA2977355A1 (en) | 2016-08-25 |
| US20180142259A1 (en) | 2018-05-24 |
| JP6873907B2 (ja) | 2021-05-19 |
| KR20180012734A (ko) | 2018-02-06 |
| SA517382162B1 (ar) | 2021-11-02 |
| AU2016219789A1 (en) | 2017-09-28 |
| NZ735344A (en) | 2024-09-27 |
| AU2016219789B2 (en) | 2021-03-25 |
| ZA201705628B (en) | 2024-08-28 |
| WO2016134375A1 (en) | 2016-08-25 |
| CN108347932A (zh) | 2018-07-31 |
| SG11201706755SA (en) | 2017-09-28 |
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