DK3684423T3 - Adeno-associerede virusvariantcapsider og fremgangsmåder til anvendelse deraf - Google Patents

Adeno-associerede virusvariantcapsider og fremgangsmåder til anvendelse deraf Download PDF

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Publication number
DK3684423T3
DK3684423T3 DK18859241.4T DK18859241T DK3684423T3 DK 3684423 T3 DK3684423 T3 DK 3684423T3 DK 18859241 T DK18859241 T DK 18859241T DK 3684423 T3 DK3684423 T3 DK 3684423T3
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adeno
methods
same
associated virus
virus variant
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DK18859241.4T
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David H Kirn
Melissa Kotterman
David Schaffer
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4D Molecular Therapeutics Inc
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    • A61K38/17—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • A61K38/1703—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
    • A61K38/1709—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
    • A61K38/1719—Muscle proteins, e.g. myosin or actin
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    • C12Y116/03—Oxidoreductases oxidizing metal ions (1.16) with oxygen as acceptor (1.16.3)
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    • C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/0102—Alpha-glucosidase (3.2.1.20)
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    • C12N2750/14171—Demonstrated in vivo effect
DK18859241.4T 2017-09-20 2018-09-19 Adeno-associerede virusvariantcapsider og fremgangsmåder til anvendelse deraf DK3684423T3 (da)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201762560901P 2017-09-20 2017-09-20
PCT/US2018/051812 WO2019060454A2 (en) 2017-09-20 2018-09-19 CAPSID VARIANT ADENO-ASSOCIATED VIRUSES AND METHODS OF USE

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DK3684423T3 true DK3684423T3 (da) 2023-06-12

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US (4) US11118192B2 (da)
EP (2) EP3684423B1 (da)
JP (1) JP6825167B2 (da)
KR (2) KR20200052333A (da)
CN (1) CN111836649A (da)
AU (1) AU2018337833B2 (da)
BR (1) BR112020005436B1 (da)
CA (1) CA3076348A1 (da)
CL (1) CL2020000728A1 (da)
CO (1) CO2020004738A2 (da)
CR (1) CR20200165A (da)
DK (1) DK3684423T3 (da)
ES (1) ES2948902T3 (da)
FI (1) FI3684423T3 (da)
IL (1) IL273261A (da)
MX (1) MX2020003176A (da)
NZ (1) NZ763018A (da)
PE (1) PE20201264A1 (da)
PH (1) PH12020550094A1 (da)
PT (1) PT3684423T (da)
RU (1) RU2770922C2 (da)
SG (1) SG11202002276VA (da)
UA (1) UA127455C2 (da)
WO (1) WO2019060454A2 (da)
ZA (1) ZA202001679B (da)

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