DK2946785T3 - PROCEDURE FOR PREVENTING RESPONSE TO DISEASES OF PHARMACOLOGICAL CHAPERONE TREATMENT - Google Patents
PROCEDURE FOR PREVENTING RESPONSE TO DISEASES OF PHARMACOLOGICAL CHAPERONE TREATMENT Download PDFInfo
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- DK2946785T3 DK2946785T3 DK15162630.6T DK15162630T DK2946785T3 DK 2946785 T3 DK2946785 T3 DK 2946785T3 DK 15162630 T DK15162630 T DK 15162630T DK 2946785 T3 DK2946785 T3 DK 2946785T3
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| KR20190087673A (ko) * | 2016-03-22 | 2019-07-24 | 아미쿠스 세라퓨틱스, 인코포레이티드 | Ｇｌａ 유전자에 ｇ9331ａ 돌연변이를 갖는 환자에서 파브리 질병의 치료 방법 |
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| JP7046003B2 (ja) * | 2016-03-30 | 2022-04-01 | アミカス セラピューティックス インコーポレイテッド | 高ｍ６ｐ組換えタンパク質の選択方法 |
| AU2017298376A1 (en) | 2016-07-19 | 2019-03-07 | Amicus Therapeutics, Inc. | Treatment of Fabry disease in ERT-naive and ERT-experienced patients |
| JP6546135B2 (ja) | 2016-08-24 | 2019-07-17 | 株式会社ノリタケカンパニーリミテド | 積層造形焼成体、積層造形焼成体の製造方法および積層造形焼成体製造用キット |
| CN110022904B (zh) * | 2016-10-20 | 2024-04-19 | 桑格摩生物治疗股份有限公司 | 用于治疗法布里病的方法和组合物 |
| EA039750B1 (ru) * | 2017-03-30 | 2022-03-10 | Амикус Терапьютикс, Инк. | Способ отбора рекомбинантных белков с высоким содержанием m6p |
| ES2950808T3 (es) | 2017-05-15 | 2023-10-13 | Amicus Therapeutics Inc | Alfa-glucosidasa ácida humana recombinante |
| PT4324522T (pt) | 2017-05-30 | 2026-03-13 | Amicus Therapeutics Inc | Métodos de tratamento de pacientes com fabry tendo insuficiência renal |
| KR20220116305A (ko) | 2017-05-30 | 2022-08-22 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 신장 손상을 갖는 파브리 환자를 치료하는 방법 |
| WO2019017938A1 (en) | 2017-07-19 | 2019-01-24 | Amicus Therapeutics, Inc. | TREATMENT OF FABRY'S DISEASE IN PATIENTS WITHOUT SUBSTITUTED ENZYMATIC THERAPY (TES) AND PATIENTS SUBJECT TO TES |
| PT3675853T (pt) | 2017-08-28 | 2022-11-28 | Amicus Therapeutics Inc | Métodos para melhorar e/ou estabilizar a função cardíaca em pacientes com doença de fabry |
| PT3749308T (pt) | 2018-02-06 | 2024-01-25 | Amicus Therapeutics Inc | Tratamento de pacientes com doença de fabry clássica com migalastato |
| EP3749307B1 (en) | 2018-02-06 | 2025-12-10 | Amicus Therapeutics, Inc. | Use of migalastat for treating fabry disease in pregnant patients |
| US20220184185A1 (en) | 2018-07-25 | 2022-06-16 | Modernatx, Inc. | Mrna based enzyme replacement therapy combined with a pharmacological chaperone for the treatment of lysosomal storage disorders |
| EP4289476A3 (en) * | 2018-08-20 | 2024-02-21 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the gla gene |
| NL2021840B1 (en) | 2018-10-19 | 2020-05-13 | Univ Leiden | Pharmacological Chaperones For Enzyme Treatment Therapy |
| WO2020046132A1 (en) | 2018-08-31 | 2020-03-05 | Leiden University | Pharmacological chaperones for enzyme treatment therapy |
| TW202042812A (zh) | 2019-01-22 | 2020-12-01 | 美商阿米庫斯醫療股份有限公司 | 減少法布瑞氏症患者中之腦血管事件之方法 |
| BR112021024886A2 (pt) | 2019-06-11 | 2022-01-25 | Amicus Therapeutics Inc | Métodos de tratar a doença de fabry em pacientes com insuficiência renal |
| WO2021026447A1 (en) * | 2019-08-07 | 2021-02-11 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the gla gene |
| KR20220058587A (ko) | 2019-09-06 | 2022-05-09 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 생물학적 제제의 포획 및 정제 방법 |
| PL4103178T3 (pl) | 2020-02-10 | 2026-05-11 | Amicus Therapeutics, Inc. | Sposoby leczenia choroby fabry'ego |
| SI4114390T1 (sl) * | 2020-03-06 | 2025-03-31 | Amicus Therapeutics, Inc. | Postopki zdravljenja Fabryjeve bolezni pri bolnikih z mutacijo gena GLA |
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| WO2023288210A1 (en) | 2021-07-12 | 2023-01-19 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in pediatric patients |
| AU2023265155A1 (en) | 2022-05-05 | 2024-12-12 | Amicus Therapeutics, Inc. | Methods for treating pompe disease |
| EP4626464A1 (en) | 2022-12-02 | 2025-10-08 | Amicus Therapeutics, Inc. | Fexamethods for treating infantile-onset pompe disease in pediatric patients |
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| US20240197706A1 (en) | 2022-12-13 | 2024-06-20 | Amicus Therapeutics, Inc. | Methods of improving the pharmacokinetics of migalastat |
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