CN109477109B - 靶向人lmna的寡核苷酸类似物 - Google Patents

靶向人lmna的寡核苷酸类似物 Download PDF

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CN109477109B
CN109477109B CN201780040785.7A CN201780040785A CN109477109B CN 109477109 B CN109477109 B CN 109477109B CN 201780040785 A CN201780040785 A CN 201780040785A CN 109477109 B CN109477109 B CN 109477109B
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antisense
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oligomers
oligomer
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CN109477109A (zh
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M.R.埃尔多斯
F.S.科林斯
K.曹
R.科尔
R.K.贝斯特维克
L.B.戈登
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Progeria Research Foundation
University of Maryland Baltimore
Sarepta Therapeutics Inc
US Department of Health and Human Services
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Progeria Research Foundation
University of Maryland Baltimore
Sarepta Therapeutics Inc
US Department of Health and Human Services
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    • C12N2310/30—Chemical structure
    • C12N2310/31—Chemical structure of the backbone
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    • C12N2310/31—Chemical structure of the backbone
    • C12N2310/318—Chemical structure of the backbone where the PO2 is completely replaced, e.g. MMI or formacetal
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CN201780040785.7A 2016-04-29 2017-04-28 靶向人lmna的寡核苷酸类似物 Active CN109477109B (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662330027P 2016-04-29 2016-04-29
US62/330027 2016-04-29
PCT/US2017/030174 WO2017190041A1 (en) 2016-04-29 2017-04-28 Oligonucleotide analogues targeting human lmna

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CN109477109A CN109477109A (zh) 2019-03-15
CN109477109B true CN109477109B (zh) 2022-09-23

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US (2) US10822608B2 (enExample)
EP (1) EP3449000A1 (enExample)
JP (2) JP7042255B2 (enExample)
KR (1) KR102329187B1 (enExample)
CN (1) CN109477109B (enExample)
AU (2) AU2017258642B2 (enExample)
CA (1) CA3022303A1 (enExample)
CO (1) CO2018012873A2 (enExample)
EA (1) EA201892467A1 (enExample)
MA (1) MA45616A (enExample)
MX (1) MX2018013157A (enExample)
NZ (1) NZ747685A (enExample)
SG (1) SG11201809468XA (enExample)
WO (1) WO2017190041A1 (enExample)

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