CN108350454B - 等位基因选择性基因编辑及其用途 - Google Patents

等位基因选择性基因编辑及其用途 Download PDF

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CN108350454B
CN108350454B CN201680067107.5A CN201680067107A CN108350454B CN 108350454 B CN108350454 B CN 108350454B CN 201680067107 A CN201680067107 A CN 201680067107A CN 108350454 B CN108350454 B CN 108350454B
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targeting
nucleotides
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targeting compound
molecules
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CN108350454A (zh
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帕德马纳巴·契吾库拉
R·威尔基-格兰瑟姆
立川洁
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Arcturus Therapeutics Inc
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CN201680067107.5A 2015-09-21 2016-09-21 等位基因选择性基因编辑及其用途 Active CN108350454B (zh)

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Application Number Priority Date Filing Date Title
US201562221407P 2015-09-21 2015-09-21
US62/221,407 2015-09-21
US201662330827P 2016-05-02 2016-05-02
US62/330,827 2016-05-02
PCT/US2016/052889 WO2017053431A2 (en) 2015-09-21 2016-09-21 Allele selective gene editing and uses thereof

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CN108350454B true CN108350454B (zh) 2022-05-10

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WO2017053431A2 (en) 2017-03-30
CN108350454A (zh) 2018-07-31
ES2959815T3 (es) 2024-02-28
EP3353298A2 (en) 2018-08-01
EP3353298B1 (en) 2023-09-13
EP3353298A4 (en) 2019-09-25
WO2017053431A3 (en) 2017-06-01
JP6799058B2 (ja) 2020-12-09
US10369232B2 (en) 2019-08-06
US20170080107A1 (en) 2017-03-23
CA3002647A1 (en) 2017-03-30

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