CA3040483A1 - Aav capsid designs - Google Patents

Aav capsid designs Download PDF

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Publication number
CA3040483A1
CA3040483A1 CA3040483A CA3040483A CA3040483A1 CA 3040483 A1 CA3040483 A1 CA 3040483A1 CA 3040483 A CA3040483 A CA 3040483A CA 3040483 A CA3040483 A CA 3040483A CA 3040483 A1 CA3040483 A1 CA 3040483A1
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CA
Canada
Prior art keywords
hsa
mir
aav
promoter
nucleic acid
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Pending
Application number
CA3040483A
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English (en)
French (fr)
Inventor
Guangping Gao
Guangchao XU
Phillip TAI
Yuquan Wei
Li Luo
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University of Massachusetts Amherst
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University of Massachusetts Amherst
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Publication of CA3040483A1 publication Critical patent/CA3040483A1/en
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    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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CA3040483A 2016-10-13 2017-10-13 Aav capsid designs Pending CA3040483A1 (en)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662408022P 2016-10-13 2016-10-13
US62/408,022 2016-10-13
US201662417756P 2016-11-04 2016-11-04
US62/417,756 2016-11-04
US201762486642P 2017-04-18 2017-04-18
US62/486,642 2017-04-18
PCT/US2017/056614 WO2018071831A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Publications (1)

Publication Number Publication Date
CA3040483A1 true CA3040483A1 (en) 2018-04-19

Family

ID=61906092

Family Applications (1)

Application Number Title Priority Date Filing Date
CA3040483A Pending CA3040483A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Country Status (8)

Country Link
US (2) US11578340B2 (enExample)
EP (1) EP3526333A4 (enExample)
JP (2) JP7577291B6 (enExample)
KR (2) KR20240173209A (enExample)
CN (1) CN110506119A (enExample)
AU (2) AU2017341849B2 (enExample)
CA (1) CA3040483A1 (enExample)
WO (1) WO2018071831A1 (enExample)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN115976106A (zh) * 2022-12-14 2023-04-18 中国人民解放军海军军医大学第一附属医院 一种携带人spink1基因的重组腺相关病毒载体及其防治胰腺炎的应用

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* Cited by examiner, † Cited by third party
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US8734809B2 (en) 2009-05-28 2014-05-27 University Of Massachusetts AAV's and uses thereof
RU2020140209A (ru) 2014-10-21 2021-01-25 Юниверсити Оф Массачусетс Варианты рекомбинантных aav и их применения
GB201508026D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Capsid
AU2017341849B2 (en) 2016-10-13 2024-03-21 University Of Massachusetts AAV capsid designs
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
US20180182497A1 (en) * 2016-12-22 2018-06-28 DxRx, Inc. Creating engagement with an inner circle social network in substance abuse treatment
EP3575398A4 (en) * 2017-01-30 2020-11-11 Nippon Medical School Foundation ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT
US10898585B2 (en) 2017-04-14 2021-01-26 Ptc Therapeutics .Inc. Gene therapy for AADC deficiency
CA3095660A1 (en) * 2018-02-15 2019-08-22 Tomas Bjorklund Modified viral capsids
KR20200128112A (ko) 2018-02-28 2020-11-11 유니버시티 오브 피츠버그-오브 더 커먼웰쓰 시스템 오브 하이어 에듀케이션 Aav에 기반한 유전자 및 단백질 전달을 위한 모듈식 시스템
CN112368391A (zh) * 2018-05-11 2021-02-12 马萨诸塞眼科耳科诊所 腺相关病毒的肝脏特异性嗜性
KR20210084459A (ko) 2018-09-26 2021-07-07 캘리포니아 인스티튜트 오브 테크놀로지 표적화된 유전자 요법을 위한 아데노-연관 바이러스 조성물
US20220073905A1 (en) * 2018-12-28 2022-03-10 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods and materials for single cell transcriptome-based development of aav vectors and promoters
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