CA3040483A1 - Aav capsid designs - Google Patents

Aav capsid designs Download PDF

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Publication number
CA3040483A1
CA3040483A1 CA3040483A CA3040483A CA3040483A1 CA 3040483 A1 CA3040483 A1 CA 3040483A1 CA 3040483 A CA3040483 A CA 3040483A CA 3040483 A CA3040483 A CA 3040483A CA 3040483 A1 CA3040483 A1 CA 3040483A1
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CA
Canada
Prior art keywords
hsa
mir
aav
promoter
nucleic acid
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Pending
Application number
CA3040483A
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English (en)
French (fr)
Inventor
Guangping Gao
Guangchao XU
Phillip TAI
Yuquan Wei
Li Luo
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University of Massachusetts Amherst
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University of Massachusetts Amherst
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Publication of CA3040483A1 publication Critical patent/CA3040483A1/en
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CA3040483A 2016-10-13 2017-10-13 Aav capsid designs Pending CA3040483A1 (en)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662408022P 2016-10-13 2016-10-13
US62/408,022 2016-10-13
US201662417756P 2016-11-04 2016-11-04
US62/417,756 2016-11-04
US201762486642P 2017-04-18 2017-04-18
US62/486,642 2017-04-18
PCT/US2017/056614 WO2018071831A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Publications (1)

Publication Number Publication Date
CA3040483A1 true CA3040483A1 (en) 2018-04-19

Family

ID=61906092

Family Applications (1)

Application Number Title Priority Date Filing Date
CA3040483A Pending CA3040483A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Country Status (8)

Country Link
US (2) US11578340B2 (enExample)
EP (1) EP3526333A4 (enExample)
JP (2) JP7577291B6 (enExample)
KR (2) KR20240173209A (enExample)
CN (1) CN110506119A (enExample)
AU (2) AU2017341849B2 (enExample)
CA (1) CA3040483A1 (enExample)
WO (1) WO2018071831A1 (enExample)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN115976106A (zh) * 2022-12-14 2023-04-18 中国人民解放军海军军医大学第一附属医院 一种携带人spink1基因的重组腺相关病毒载体及其防治胰腺炎的应用

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RU2020140209A (ru) 2014-10-21 2021-01-25 Юниверсити Оф Массачусетс Варианты рекомбинантных aav и их применения
GB201508026D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Capsid
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
CA3040483A1 (en) 2016-10-13 2018-04-19 University Of Massachusetts Aav capsid designs
WO2018119330A2 (en) * 2016-12-22 2018-06-28 Oregon Health & Science University Adeno associated viral vectors
EP3575398A4 (en) * 2017-01-30 2020-11-11 Nippon Medical School Foundation ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT
WO2018191450A2 (en) 2017-04-14 2018-10-18 National Taiwan University Hospital Gene therapy for aadc deficiency
CA3095660A1 (en) * 2018-02-15 2019-08-22 Tomas Bjorklund Modified viral capsids
AU2019227910B2 (en) 2018-02-28 2025-07-17 The Regents Of The University Of California A modular system for gene and protein delivery based on AAV
JP7438981B2 (ja) 2018-05-11 2024-02-27 マサチューセッツ アイ アンド イヤー インファーマリー アデノ随伴ウイルスの肝臓特異的向性
SG11202103102WA (en) 2018-09-26 2021-04-29 California Inst Of Techn Adeno-associated virus compositions for targeted gene therapy
US20220073905A1 (en) * 2018-12-28 2022-03-10 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods and materials for single cell transcriptome-based development of aav vectors and promoters
US11981967B2 (en) 2019-04-26 2024-05-14 Sangamo Therapeutics, Inc. Engineering AAV
WO2020223276A1 (en) * 2019-04-29 2020-11-05 Voyager Therapeutics, Inc. Compositions and methods for the treatment of tauopathy
WO2021000024A1 (en) * 2019-07-04 2021-01-07 Children's Medical Research Institute Methods and aav vectors for in vivo transduction
US12570998B2 (en) 2019-09-09 2026-03-10 Massachusetts Eye & Ear Infirmary Methods and compositions for modulating the interaction between adeno-associated virus (AAV) and the AAV receptor (AAVR) for altered bio-distribution of AAV
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