AU2017341849B2 - AAV capsid designs - Google Patents

AAV capsid designs Download PDF

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Publication number
AU2017341849B2
AU2017341849B2 AU2017341849A AU2017341849A AU2017341849B2 AU 2017341849 B2 AU2017341849 B2 AU 2017341849B2 AU 2017341849 A AU2017341849 A AU 2017341849A AU 2017341849 A AU2017341849 A AU 2017341849A AU 2017341849 B2 AU2017341849 B2 AU 2017341849B2
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Australia
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hsa
mir
aav
raav
transgene
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AU2017341849A1 (en
Inventor
Guangping Gao
Li Luo
Phillip TAI
Yuquan Wei
Guangchao XU
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University of Massachusetts Amherst
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University of Massachusetts Amherst
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    • C07K14/005—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from viruses
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    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
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AU2017341849A 2016-10-13 2017-10-13 AAV capsid designs Active AU2017341849B2 (en)

Priority Applications (1)

Application Number Priority Date Filing Date Title
AU2024203491A AU2024203491B2 (en) 2016-10-13 2024-05-24 AAV capsid designs

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662408022P 2016-10-13 2016-10-13
US62/408,022 2016-10-13
US201662417756P 2016-11-04 2016-11-04
US62/417,756 2016-11-04
US201762486642P 2017-04-18 2017-04-18
US62/486,642 2017-04-18
PCT/US2017/056614 WO2018071831A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Related Child Applications (1)

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AU2024203491A Division AU2024203491B2 (en) 2016-10-13 2024-05-24 AAV capsid designs

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AU2017341849A1 AU2017341849A1 (en) 2019-05-02
AU2017341849B2 true AU2017341849B2 (en) 2024-03-21

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US (2) US11578340B2 (enExample)
EP (1) EP3526333A4 (enExample)
JP (2) JP7577291B6 (enExample)
KR (2) KR20190075964A (enExample)
CN (1) CN110506119A (enExample)
AU (1) AU2017341849B2 (enExample)
CA (1) CA3040483A1 (enExample)
WO (1) WO2018071831A1 (enExample)

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US8734809B2 (en) 2009-05-28 2014-05-27 University Of Massachusetts AAV's and uses thereof
WO2016065001A1 (en) 2014-10-21 2016-04-28 University Of Massachusetts Recombinant aav variants and uses thereof
GB201508026D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Capsid
KR20190075964A (ko) 2016-10-13 2019-07-01 유니버시티 오브 매사추세츠 Aav 캡시드 설계
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
US20230048025A1 (en) * 2016-12-22 2023-02-16 Oregon Health & Science University Adeno associated viral vectors
EP3575398A4 (en) * 2017-01-30 2020-11-11 Nippon Medical School Foundation ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT
CA3059891A1 (en) 2017-04-14 2018-10-18 National Taiwan University Gene therapy for aadc deficiency
AU2019220368B2 (en) * 2018-02-15 2024-06-13 Brave Bioscience Ab Modified viral capsids
US12421525B2 (en) 2018-02-28 2025-09-23 University of Pittsburgh—of the Commonwealth System of Higher Education Conjugates comprising AAVs and CAS9 polypeptides
IL278598B2 (en) * 2018-05-11 2025-11-01 Massachusetts Eye & Ear Infirmary Altering tissue tropism of adeno-associated viruses
US11149256B2 (en) 2018-09-26 2021-10-19 California Institute Of Technology Adeno-associated virus compositions for targeted gene therapy
US20220073905A1 (en) * 2018-12-28 2022-03-10 University Of Pittsburgh - Of The Commonwealth System Of Higher Education Methods and materials for single cell transcriptome-based development of aav vectors and promoters
CN114269926A (zh) 2019-04-26 2022-04-01 美商圣加莫治疗股份有限公司 Aav工程化
TW202106705A (zh) * 2019-04-29 2021-02-16 美商航海家醫療公司 用於tau蛋白病變之治療之組合物及方法
AU2020299026A1 (en) * 2019-07-04 2022-01-20 Children's Medical Research Institute Methods and AAV vectors for in vivo transduction
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