CA2905952A1 - Adeno-associated virus vectors and methods of use thereof - Google Patents
Adeno-associated virus vectors and methods of use thereof Download PDFInfo
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- CA2905952A1 CA2905952A1 CA2905952A CA2905952A CA2905952A1 CA 2905952 A1 CA2905952 A1 CA 2905952A1 CA 2905952 A CA2905952 A CA 2905952A CA 2905952 A CA2905952 A CA 2905952A CA 2905952 A1 CA2905952 A1 CA 2905952A1
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- C12N2750/00011—Details
- C12N2750/14011—Parvoviridae
- C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
- C12N2750/14141—Use of virus, viral particle or viral elements as a vector
- C12N2750/14145—Special targeting system for viral vectors
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N2810/00—Vectors comprising a targeting moiety
- C12N2810/50—Vectors comprising as targeting moiety peptide derived from defined protein
- C12N2810/60—Vectors comprising as targeting moiety peptide derived from defined protein from viruses
- C12N2810/6027—Vectors comprising as targeting moiety peptide derived from defined protein from viruses ssDNA viruses
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12Y—ENZYMES
- C12Y302/00—Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
- C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
- C12Y302/01031—Beta-glucuronidase (3.2.1.31)
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- Health & Medical Sciences (AREA)
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- Engineering & Computer Science (AREA)
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- Genetics & Genomics (AREA)
- Bioinformatics & Cheminformatics (AREA)
- Organic Chemistry (AREA)
- Biomedical Technology (AREA)
- Zoology (AREA)
- Wood Science & Technology (AREA)
- General Health & Medical Sciences (AREA)
- General Engineering & Computer Science (AREA)
- Biotechnology (AREA)
- Medicinal Chemistry (AREA)
- Biochemistry (AREA)
- Microbiology (AREA)
- Molecular Biology (AREA)
- Virology (AREA)
- Public Health (AREA)
- Veterinary Medicine (AREA)
- Animal Behavior & Ethology (AREA)
- Pharmacology & Pharmacy (AREA)
- Neurosurgery (AREA)
- Neurology (AREA)
- Immunology (AREA)
- Biophysics (AREA)
- Plant Pathology (AREA)
- Physics & Mathematics (AREA)
- General Chemical & Material Sciences (AREA)
- Chemical Kinetics & Catalysis (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
- Epidemiology (AREA)
- Gastroenterology & Hepatology (AREA)
- Hospice & Palliative Care (AREA)
- Psychiatry (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Medicines Containing Material From Animals Or Micro-Organisms (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Peptides Or Proteins (AREA)
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201361780423P | 2013-03-13 | 2013-03-13 | |
| US61/780,423 | 2013-03-13 | ||
| PCT/US2014/025794 WO2014160092A1 (en) | 2013-03-13 | 2014-03-13 | Adeno-associated virus vectors and methods of use thereof |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| CA2905952A1 true CA2905952A1 (en) | 2014-10-02 |
Family
ID=51625331
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| CA2905952A Abandoned CA2905952A1 (en) | 2013-03-13 | 2014-03-13 | Adeno-associated virus vectors and methods of use thereof |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20150374803A1 (enExample) |
| EP (1) | EP2970946A4 (enExample) |
| JP (1) | JP2016514152A (enExample) |
| AU (1) | AU2014244167A1 (enExample) |
| CA (1) | CA2905952A1 (enExample) |
| WO (1) | WO2014160092A1 (enExample) |
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| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6582692B1 (en) * | 1999-11-17 | 2003-06-24 | Avigen, Inc. | Recombinant adeno-associated virus virions for the treatment of lysosomal disorders |
| EP2298926A1 (en) * | 2003-09-30 | 2011-03-23 | The Trustees of The University of Pennsylvania | Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof |
| EP3514232A1 (en) * | 2010-04-23 | 2019-07-24 | University of Massachusetts | Cns targeting aav vectors and methods of use thereof |
| CA2799470A1 (en) * | 2010-05-14 | 2011-11-17 | The Children's Hospital Of Philadelphia | Humanized ttc and methods of use thereof |
| CN107828820B (zh) * | 2010-10-27 | 2022-06-07 | 学校法人自治医科大学 | 用于向神经系统细胞导入基因的腺相关病毒粒子 |
| EP4234571A3 (en) * | 2011-02-10 | 2023-09-27 | The University of North Carolina at Chapel Hill | Viral vectors with modified transduction profiles and methods of making and using the same |
| JP6224459B2 (ja) * | 2011-02-17 | 2017-11-01 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 組織特異性を改変し、ａａｖ９媒介遺伝子導入を改善するための組成物および方法 |
-
2014
- 2014-03-13 EP EP14776247.0A patent/EP2970946A4/en not_active Withdrawn
- 2014-03-13 WO PCT/US2014/025794 patent/WO2014160092A1/en not_active Ceased
- 2014-03-13 JP JP2016501968A patent/JP2016514152A/ja active Pending
- 2014-03-13 AU AU2014244167A patent/AU2014244167A1/en not_active Abandoned
- 2014-03-13 CA CA2905952A patent/CA2905952A1/en not_active Abandoned
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2015
- 2015-09-10 US US14/850,292 patent/US20150374803A1/en not_active Abandoned
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| EP2970946A1 (en) | 2016-01-20 |
| US20150374803A1 (en) | 2015-12-31 |
| AU2014244167A1 (en) | 2015-10-08 |
| JP2016514152A (ja) | 2016-05-19 |
| EP2970946A4 (en) | 2016-09-07 |
| WO2014160092A1 (en) | 2014-10-02 |
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Effective date: 20190313 |