CA2814143C - Methods and compositions for treating hemophilia b - Google Patents
Methods and compositions for treating hemophilia b Download PDFInfo
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- CA2814143C CA2814143C CA2814143A CA2814143A CA2814143C CA 2814143 C CA2814143 C CA 2814143C CA 2814143 A CA2814143 A CA 2814143A CA 2814143 A CA2814143 A CA 2814143A CA 2814143 C CA2814143 C CA 2814143C
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- C12N9/6424—Serine endopeptidases (3.4.21)
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- C12Y—ENZYMES
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| CA3186126A1 (en) | 2011-09-21 | 2013-03-28 | Sangamo Biosciences, Inc. | Methods and compositions for regulation of transgene expression |
| RU2653444C2 (ru) * | 2012-02-17 | 2018-05-08 | Дзе Чилдрен'З Хоспитал Оф Филадельфия | Композиции вектора aav и способы переноса генов в клетки, органы и ткани |
| US10648001B2 (en) | 2012-07-11 | 2020-05-12 | Sangamo Therapeutics, Inc. | Method of treating mucopolysaccharidosis type I or II |
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| KR20250068794A (ko) * | 2013-12-12 | 2025-05-16 | 더 브로드 인스티튜트, 인코퍼레이티드 | 게놈 편집을 위한 ｃｒｉｓｐｒ-ｃａｓ 시스템 및 조성물의 전달, 용도 및 치료적 응용 |
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| US10953101B2 (en) | 2014-02-21 | 2021-03-23 | École Polytechnique Fédérale De Lausanne (Epfl) | Glycotargeting therapeutics |
| US10946079B2 (en) | 2014-02-21 | 2021-03-16 | Ecole Polytechnique Federale De Lausanne | Glycotargeting therapeutics |
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| EP2627665A4 (en) | 2014-02-26 |
| WO2012051343A1 (en) | 2012-04-19 |
| BR112013008881A2 (pt) | 2016-06-28 |
| BR112013008881B1 (pt) | 2021-12-07 |
| ES2562421T3 (es) | 2016-03-04 |
| ZA201302625B (en) | 2014-05-28 |
| HK1185623A1 (zh) | 2014-02-21 |
| AU2011316575B2 (en) | 2015-10-29 |
| US20160022838A1 (en) | 2016-01-28 |
| JP6018069B2 (ja) | 2016-11-02 |
| RU2608643C2 (ru) | 2017-01-23 |
| CN103270046B (zh) | 2016-05-11 |
| CN103270046A (zh) | 2013-08-28 |
| KR20140042764A (ko) | 2014-04-07 |
| EP2627665A1 (en) | 2013-08-21 |
| CA2814143A1 (en) | 2012-04-19 |
| US20120128635A1 (en) | 2012-05-24 |
| EP2627665B1 (en) | 2015-12-16 |
| AU2011316575A1 (en) | 2013-05-02 |
| RU2013120986A (ru) | 2014-11-20 |
| US9629930B2 (en) | 2017-04-25 |
| JP2013544077A (ja) | 2013-12-12 |
| KR101930711B1 (ko) | 2018-12-19 |
| US9175280B2 (en) | 2015-11-03 |
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