RU2608643C2 - Способы и композиции для лечения гемофилии в - Google Patents
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| RU2758722C2 (ru) * | 2017-05-24 | 2021-11-01 | Эпипланта Биотек Элтэдэ. | Трансгенное растение и способ его получения |
| US12559748B2 (en) | 2017-02-06 | 2026-02-24 | Novartis Ag | Compositions and methods for the treatment of hemoglobinopathies |
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| US20100256062A1 (en) | 2004-12-06 | 2010-10-07 | Howard Tommy E | Allelic Variants of Human Factor VIII |
| CA2807942C (en) | 2010-08-10 | 2021-07-27 | Ecole Polytechnique Federale De Lausanne | Erythrocyte-binding therapeutics |
| US9850296B2 (en) | 2010-08-10 | 2017-12-26 | Ecole Polytechnique Federale De Lausanne (Epfl) | Erythrocyte-binding therapeutics |
| US9517257B2 (en) | 2010-08-10 | 2016-12-13 | Ecole Polytechnique Federale De Lausanne (Epfl) | Erythrocyte-binding therapeutics |
| CA2848417C (en) | 2011-09-21 | 2023-05-02 | Sangamo Biosciences, Inc. | Methods and compositions for regulation of transgene expression |
| WO2013123503A1 (en) * | 2012-02-17 | 2013-08-22 | The Children's Hospital Of Philadelphia | Aav vector compositions and methods for gene transfer to cells, organs and tissues |
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| WO2014093622A2 (en) | 2012-12-12 | 2014-06-19 | The Broad Institute, Inc. | Delivery, engineering and optimization of systems, methods and compositions for sequence manipulation and therapeutic applications |
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| EP2627665A1 (en) | 2013-08-21 |
| KR20140042764A (ko) | 2014-04-07 |
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| ES2562421T3 (es) | 2016-03-04 |
| CA2814143A1 (en) | 2012-04-19 |
| HK1185623A1 (zh) | 2014-02-21 |
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| US9629930B2 (en) | 2017-04-25 |
| US20160022838A1 (en) | 2016-01-28 |
| CA2814143C (en) | 2020-09-08 |
| EP2627665A4 (en) | 2014-02-26 |
| AU2011316575A1 (en) | 2013-05-02 |
| BR112013008881B1 (pt) | 2021-12-07 |
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