RU2608643C2 - Способы и композиции для лечения гемофилии в - Google Patents
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| US20160045575A1 (en) * | 2012-12-07 | 2016-02-18 | Tom E. HOWARD | FACTOR VIII MUTATION REPAIR AND TOLERANCE INDUCTION AND RELATED cDNAs, COMPOSITIONS, METHODS AND SYSTEMS |
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| EP3725885A1 (en) | 2013-06-17 | 2020-10-21 | The Broad Institute, Inc. | Functional genomics using crispr-cas systems, compositions methods, screens and applications thereof |
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| WO2012051343A1 (en) | 2012-04-19 |
| BR112013008881A2 (pt) | 2016-06-28 |
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| CA2814143A1 (en) | 2012-04-19 |
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| US20120128635A1 (en) | 2012-05-24 |
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| AU2011316575A1 (en) | 2013-05-02 |
| RU2013120986A (ru) | 2014-11-20 |
| US9629930B2 (en) | 2017-04-25 |
| JP2013544077A (ja) | 2013-12-12 |
| KR101930711B1 (ko) | 2018-12-19 |
| US9175280B2 (en) | 2015-11-03 |
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