CA2715407C - Method to predict response to pharmacological chaperone treatment of diseases - Google Patents
Method to predict response to pharmacological chaperone treatment of diseases Download PDFInfo
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- CA2715407C CA2715407C CA2715407A CA2715407A CA2715407C CA 2715407 C CA2715407 C CA 2715407C CA 2715407 A CA2715407 A CA 2715407A CA 2715407 A CA2715407 A CA 2715407A CA 2715407 C CA2715407 C CA 2715407C
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| JP2011517556A (ja) * | 2008-03-12 | 2011-06-16 | アミカス セラピューティックス インコーポレイテッド | ポンペ病のための治療選択肢を診断し評価するための検定 |
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| KR102618519B1 (ko) | 2016-03-30 | 2023-12-28 | 아미쿠스 세라퓨틱스, 인코포레이티드 | 재조합 산 알파-글루코시다제를 포함하는 제형 |
| KR20240017126A (ko) | 2016-07-19 | 2024-02-06 | 아미쿠스 세라퓨틱스, 인코포레이티드 | Ert-치료경험이 없는 환자 및 있는 환자에서 파브리병의 치료 |
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