BR112014017587A8 - métodos e formulações para o tratamento de deficiências de ácido siálico - Google Patents

métodos e formulações para o tratamento de deficiências de ácido siálico

Info

Publication number
BR112014017587A8
BR112014017587A8 BR112014017587A BR112014017587A BR112014017587A8 BR 112014017587 A8 BR112014017587 A8 BR 112014017587A8 BR 112014017587 A BR112014017587 A BR 112014017587A BR 112014017587 A BR112014017587 A BR 112014017587A BR 112014017587 A8 BR112014017587 A8 BR 112014017587A8
Authority
BR
Brazil
Prior art keywords
methods
sialic acid
formulations
treatment
acid deficiencies
Prior art date
Application number
BR112014017587A
Other languages
English (en)
Portuguese (pt)
Other versions
BR112014017587A2 (pt
Inventor
D Kakkis Emil
Original Assignee
Ultragenyx Pharmaceutical Inc
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ultragenyx Pharmaceutical Inc filed Critical Ultragenyx Pharmaceutical Inc
Publication of BR112014017587A2 publication Critical patent/BR112014017587A2/pt
Publication of BR112014017587A8 publication Critical patent/BR112014017587A8/pt

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/20Pills, tablets, discs, rods
    • A61K9/2004Excipients; Inactive ingredients
    • A61K9/2022Organic macromolecular compounds
    • A61K9/205Polysaccharides, e.g. alginate, gums; Cyclodextrin
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/70Carbohydrates; Sugars; Derivatives thereof
    • A61K31/7012Compounds having a free or esterified carboxyl group attached, directly or through a carbon chain, to a carbon atom of the saccharide radical, e.g. glucuronic acid, neuraminic acid
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/0002Galenical forms characterised by the drug release technique; Application systems commanded by energy
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/20Pills, tablets, discs, rods
    • A61K9/2004Excipients; Inactive ingredients
    • A61K9/2022Organic macromolecular compounds
    • A61K9/205Polysaccharides, e.g. alginate, gums; Cyclodextrin
    • A61K9/2054Cellulose; Cellulose derivatives, e.g. hydroxypropyl methylcellulose
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00Drugs for disorders of the muscular or neuromuscular system

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Epidemiology (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Molecular Biology (AREA)
  • Neurology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Organic Chemistry (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicinal Preparation (AREA)
BR112014017587A 2012-01-18 2013-01-18 métodos e formulações para o tratamento de deficiências de ácido siálico BR112014017587A8 (pt)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261588069P 2012-01-18 2012-01-18
US201261709549P 2012-10-04 2012-10-04
PCT/US2013/022167 WO2013109906A2 (en) 2012-01-18 2013-01-18 Methods and formulations for treating sialic acid deficiencies

Publications (2)

Publication Number Publication Date
BR112014017587A2 BR112014017587A2 (pt) 2017-06-13
BR112014017587A8 true BR112014017587A8 (pt) 2017-07-04

Family

ID=48799814

Family Applications (1)

Application Number Title Priority Date Filing Date
BR112014017587A BR112014017587A8 (pt) 2012-01-18 2013-01-18 métodos e formulações para o tratamento de deficiências de ácido siálico

Country Status (9)

Country Link
EP (1) EP2804600A4 (enrdf_load_stackoverflow)
JP (2) JP2015504094A (enrdf_load_stackoverflow)
KR (1) KR20150000872A (enrdf_load_stackoverflow)
CN (1) CN104271125A (enrdf_load_stackoverflow)
AU (1) AU2013209610B2 (enrdf_load_stackoverflow)
BR (1) BR112014017587A8 (enrdf_load_stackoverflow)
CA (1) CA2862836A1 (enrdf_load_stackoverflow)
IL (1) IL233225A0 (enrdf_load_stackoverflow)
WO (1) WO2013109906A2 (enrdf_load_stackoverflow)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9241896B2 (en) 2008-12-19 2016-01-26 Ultragenyx Pharmaceutical Inc. Methods and formulations for treating sialic acid deficiencies
CN108606956A (zh) 2010-07-13 2018-10-02 奥特吉尼克斯制药公司 用于治疗唾液酸缺乏的方法和制剂
CN103974965B (zh) 2011-10-24 2019-09-24 奥特吉尼克斯制药公司 唾液酸类似物
AR106025A1 (es) 2015-09-14 2017-12-06 Ultragenyx Pharmaceutical Inc Formas cristalinas de ácido siálico o una sal o solvato de este
EP3486326A1 (en) 2017-11-21 2019-05-22 Jennewein Biotechnologie GmbH Method for the purification of n-acetylneuraminic acid from a fermentation broth
CN117969774B (zh) * 2024-04-02 2024-06-11 小仙炖霸州食品有限公司 一种自动化燕窝检测与分级系统

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL268475B (en) * 2007-05-31 2022-08-01 Government Of The Us Secretary Of The Department Of Health And Human Services National Institutes Of N-acetyl mannosamine as a therapeutic agent
US20100159001A1 (en) * 2008-12-19 2010-06-24 Cardinal John R Extended-Release Pharmaceutical Formulations
WO2010131712A1 (ja) * 2009-05-15 2010-11-18 財団法人ヒューマンサイエンス振興財団 Gneタンパク質の機能低下に起因する疾患の治療用医薬剤、食品組成物、食品添加物
CN108606956A (zh) * 2010-07-13 2018-10-02 奥特吉尼克斯制药公司 用于治疗唾液酸缺乏的方法和制剂
CN103974965B (zh) * 2011-10-24 2019-09-24 奥特吉尼克斯制药公司 唾液酸类似物

Also Published As

Publication number Publication date
JP2015504094A (ja) 2015-02-05
CA2862836A1 (en) 2013-07-25
AU2013209610B2 (en) 2017-11-30
WO2013109906A2 (en) 2013-07-25
IL233225A0 (en) 2014-08-31
AU2013209610A1 (en) 2014-07-10
EP2804600A2 (en) 2014-11-26
EP2804600A4 (en) 2015-09-02
KR20150000872A (ko) 2015-01-05
JP2017186381A (ja) 2017-10-12
BR112014017587A2 (pt) 2017-06-13
CN104271125A (zh) 2015-01-07

Similar Documents

Publication Publication Date Title
BR112013000776A2 (pt) método e formulação para tratamento de deficiência de ácido siálico
DOP2014000233A (es) Compuestos de microarn y métodos de modulación de la actividad de mir-21
MX391043B (es) Formulaciones de anticuerpo y metodos.
BR112015021999A2 (pt) inibidores de indoleamina 2,3-dioxigenase (ido)
CR20130480A (es) Nuevos inmunoconjugados
CR20120413A (es) Derivados de fumarato de ácido graso y sus usos
CL2013001947A1 (es) Composicion farmaceutica que comprende pioglitazona; uso de pioglitazona para tratar alzheimer; composicion que comprende pioglitazona.
BR112014030743A2 (pt) inibidores de neprilisina
GT201400101A (es) Procedimiento de preparación de 5-fluoro-1h-pirazolopiridinas sustituidas
MX2022011225A (es) Formulaciones farmaceuticas de un inhibidor de hidroxilasa de hif.
CR20140554A (es) Compuestos de acido dimetil-benzoico
BR112014014939A2 (pt) composição de tratamento de sementes
CR20140435A (es) Nuevos derivados de tienopirimidina, procesos para su preparacion y sus usos terapeuticos
BR112014017587A2 (pt) métodos e formulações para o tratamento de deficiências de ácido siálico
EP2696874A4 (en) COMPOSITIONS AND METHOD FOR THE TREATMENT OF NOSES
BR112015002275A2 (pt) processos e intermediários para a preparação de inibidores da integrase
GT201400242A (es) "nuevos compuestos de pirazol"
GT201400288A (es) "compuestos de fenoxietil piperidina"
BR112014026326A2 (pt) composição para tratamento de distúrbios metabólicos
MX2016006975A (es) Compuestos, composicion farmaceutica y metodos para su uso en el tratamiento de enfermedades inflamatorias.
DOP2016000120A (es) Nuevos inhibidores de dgat2
ECSP13012366A (es) Procedimiento de preparación de la sal de l-arginina de perindoprilo
BR112017028448A2 (pt) análogos de cisteamina resistentes a ado e usos dos mesmos
CO6801728A2 (es) Formulación de lipomosas adecuada para tratar o prevenir la tuberculosis
BR112015024859A2 (pt) processo e intermediários para a preparação de pregabalina

Legal Events

Date Code Title Description
B07D Technical examination (opinion) related to article 229 of industrial property law [chapter 7.4 patent gazette]
B06F Objections, documents and/or translations needed after an examination request according [chapter 6.6 patent gazette]
B07E Notification of approval relating to section 229 industrial property law [chapter 7.5 patent gazette]

Free format text: NOTIFICACAO DE ANUENCIA RELACIONADA COM O ART 229 DA LPI

B06U Preliminary requirement: requests with searches performed by other patent offices: procedure suspended [chapter 6.21 patent gazette]
B08F Application dismissed because of non-payment of annual fees [chapter 8.6 patent gazette]

Free format text: REFERENTE A 7A ANUIDADE.

B11B Dismissal acc. art. 36, par 1 of ipl - no reply within 90 days to fullfil the necessary requirements
B350 Update of information on the portal [chapter 15.35 patent gazette]