CA2862836A1 - Methods and formulations for treating sialic acid deficiencies - Google Patents
Methods and formulations for treating sialic acid deficiencies Download PDFInfo
- Publication number
- CA2862836A1 CA2862836A1 CA2862836A CA2862836A CA2862836A1 CA 2862836 A1 CA2862836 A1 CA 2862836A1 CA 2862836 A CA2862836 A CA 2862836A CA 2862836 A CA2862836 A CA 2862836A CA 2862836 A1 CA2862836 A1 CA 2862836A1
- Authority
- CA
- Canada
- Prior art keywords
- sialic acid
- extended release
- release formulation
- pharmaceutically acceptable
- acceptable salt
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Abandoned
Links
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- A—HUMAN NECESSITIES
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- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/70—Carbohydrates; Sugars; Derivatives thereof
- A61K31/7012—Compounds having a free or esterified carboxyl group attached, directly or through a carbon chain, to a carbon atom of the saccharide radical, e.g. glucuronic acid, neuraminic acid
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/0002—Galenical forms characterised by the drug release technique; Application systems commanded by energy
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/20—Pills, tablets, discs, rods
- A61K9/2004—Excipients; Inactive ingredients
- A61K9/2022—Organic macromolecular compounds
- A61K9/205—Polysaccharides, e.g. alginate, gums; Cyclodextrin
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/20—Pills, tablets, discs, rods
- A61K9/2004—Excipients; Inactive ingredients
- A61K9/2022—Organic macromolecular compounds
- A61K9/205—Polysaccharides, e.g. alginate, gums; Cyclodextrin
- A61K9/2054—Cellulose; Cellulose derivatives, e.g. hydroxypropyl methylcellulose
-
- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P21/00—Drugs for disorders of the muscular or neuromuscular system
Landscapes
- Health & Medical Sciences (AREA)
- Life Sciences & Earth Sciences (AREA)
- Chemical & Material Sciences (AREA)
- Medicinal Chemistry (AREA)
- Pharmacology & Pharmacy (AREA)
- Animal Behavior & Ethology (AREA)
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- Bioinformatics & Cheminformatics (AREA)
- Molecular Biology (AREA)
- Neurology (AREA)
- Orthopedic Medicine & Surgery (AREA)
- Physical Education & Sports Medicine (AREA)
- Chemical Kinetics & Catalysis (AREA)
- General Chemical & Material Sciences (AREA)
- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Organic Chemistry (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicinal Preparation (AREA)
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201261588069P | 2012-01-18 | 2012-01-18 | |
| US61/588,069 | 2012-01-18 | ||
| US201261709549P | 2012-10-04 | 2012-10-04 | |
| US61/709,549 | 2012-10-04 | ||
| PCT/US2013/022167 WO2013109906A2 (en) | 2012-01-18 | 2013-01-18 | Methods and formulations for treating sialic acid deficiencies |
Publications (1)
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| CA2862836A1 true CA2862836A1 (en) | 2013-07-25 |
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| CA2862836A Abandoned CA2862836A1 (en) | 2012-01-18 | 2013-01-18 | Methods and formulations for treating sialic acid deficiencies |
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|---|---|---|---|---|
| US9241896B2 (en) | 2008-12-19 | 2016-01-26 | Ultragenyx Pharmaceutical Inc. | Methods and formulations for treating sialic acid deficiencies |
| CN108606956A (zh) | 2010-07-13 | 2018-10-02 | 奥特吉尼克斯制药公司 | 用于治疗唾液酸缺乏的方法和制剂 |
| CN103974965B (zh) | 2011-10-24 | 2019-09-24 | 奥特吉尼克斯制药公司 | 唾液酸类似物 |
| AR106025A1 (es) | 2015-09-14 | 2017-12-06 | Ultragenyx Pharmaceutical Inc | Formas cristalinas de ácido siálico o una sal o solvato de este |
| EP3486326A1 (en) | 2017-11-21 | 2019-05-22 | Jennewein Biotechnologie GmbH | Method for the purification of n-acetylneuraminic acid from a fermentation broth |
| CN117969774B (zh) * | 2024-04-02 | 2024-06-11 | 小仙炖霸州食品有限公司 | 一种自动化燕窝检测与分级系统 |
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| IL268475B (en) * | 2007-05-31 | 2022-08-01 | Government Of The Us Secretary Of The Department Of Health And Human Services National Institutes Of | N-acetyl mannosamine as a therapeutic agent |
| US20100159001A1 (en) * | 2008-12-19 | 2010-06-24 | Cardinal John R | Extended-Release Pharmaceutical Formulations |
| WO2010131712A1 (ja) * | 2009-05-15 | 2010-11-18 | 財団法人ヒューマンサイエンス振興財団 | Ｇｎｅタンパク質の機能低下に起因する疾患の治療用医薬剤、食品組成物、食品添加物 |
| CN108606956A (zh) * | 2010-07-13 | 2018-10-02 | 奥特吉尼克斯制药公司 | 用于治疗唾液酸缺乏的方法和制剂 |
| CN103974965B (zh) * | 2011-10-24 | 2019-09-24 | 奥特吉尼克斯制药公司 | 唾液酸类似物 |
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2013
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- 2013-01-18 KR KR1020147022912A patent/KR20150000872A/ko not_active Withdrawn
- 2013-01-18 EP EP13739040.7A patent/EP2804600A4/en not_active Withdrawn
- 2013-01-18 AU AU2013209610A patent/AU2013209610B2/en not_active Expired - Fee Related
- 2013-01-18 CA CA2862836A patent/CA2862836A1/en not_active Abandoned
- 2013-01-18 BR BR112014017587A patent/BR112014017587A8/pt not_active Application Discontinuation
- 2013-01-18 CN CN201380015020.XA patent/CN104271125A/zh active Pending
- 2013-01-18 WO PCT/US2013/022167 patent/WO2013109906A2/en active Application Filing
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2014
- 2014-06-18 IL IL233225A patent/IL233225A0/en unknown
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2017
- 2017-07-21 JP JP2017141883A patent/JP2017186381A/ja active Pending
Also Published As
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| JP2015504094A (ja) | 2015-02-05 |
| AU2013209610B2 (en) | 2017-11-30 |
| WO2013109906A2 (en) | 2013-07-25 |
| IL233225A0 (en) | 2014-08-31 |
| AU2013209610A1 (en) | 2014-07-10 |
| EP2804600A2 (en) | 2014-11-26 |
| EP2804600A4 (en) | 2015-09-02 |
| KR20150000872A (ko) | 2015-01-05 |
| JP2017186381A (ja) | 2017-10-12 |
| BR112014017587A8 (pt) | 2017-07-04 |
| BR112014017587A2 (pt) | 2017-06-13 |
| CN104271125A (zh) | 2015-01-07 |
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