AU2013209610B2 - Methods and formulations for treating sialic acid deficiencies - Google Patents
Methods and formulations for treating sialic acid deficiencies Download PDFInfo
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- AU2013209610B2 AU2013209610B2 AU2013209610A AU2013209610A AU2013209610B2 AU 2013209610 B2 AU2013209610 B2 AU 2013209610B2 AU 2013209610 A AU2013209610 A AU 2013209610A AU 2013209610 A AU2013209610 A AU 2013209610A AU 2013209610 B2 AU2013209610 B2 AU 2013209610B2
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- Prior art keywords
- sialic acid
- extended release
- release formulation
- neuac
- acceptable salt
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- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/70—Carbohydrates; Sugars; Derivatives thereof
- A61K31/7012—Compounds having a free or esterified carboxyl group attached, directly or through a carbon chain, to a carbon atom of the saccharide radical, e.g. glucuronic acid, neuraminic acid
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- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/0002—Galenical forms characterised by the drug release technique; Application systems commanded by energy
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- A—HUMAN NECESSITIES
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- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/20—Pills, tablets, discs, rods
- A61K9/2004—Excipients; Inactive ingredients
- A61K9/2022—Organic macromolecular compounds
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- A—HUMAN NECESSITIES
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- A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
- A61K9/00—Medicinal preparations characterised by special physical form
- A61K9/20—Pills, tablets, discs, rods
- A61K9/2004—Excipients; Inactive ingredients
- A61K9/2022—Organic macromolecular compounds
- A61K9/205—Polysaccharides, e.g. alginate, gums; Cyclodextrin
- A61K9/2054—Cellulose; Cellulose derivatives, e.g. hydroxypropyl methylcellulose
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P21/00—Drugs for disorders of the muscular or neuromuscular system
Landscapes
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- Chemical & Material Sciences (AREA)
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- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
- Organic Chemistry (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicinal Preparation (AREA)
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201261588069P | 2012-01-18 | 2012-01-18 | |
| US61/588,069 | 2012-01-18 | ||
| US201261709549P | 2012-10-04 | 2012-10-04 | |
| US61/709,549 | 2012-10-04 | ||
| PCT/US2013/022167 WO2013109906A2 (en) | 2012-01-18 | 2013-01-18 | Methods and formulations for treating sialic acid deficiencies |
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| AU2013209610A1 AU2013209610A1 (en) | 2014-07-10 |
| AU2013209610B2 true AU2013209610B2 (en) | 2017-11-30 |
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| AU2013209610A Expired - Fee Related AU2013209610B2 (en) | 2012-01-18 | 2013-01-18 | Methods and formulations for treating sialic acid deficiencies |
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| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9241896B2 (en) | 2008-12-19 | 2016-01-26 | Ultragenyx Pharmaceutical Inc. | Methods and formulations for treating sialic acid deficiencies |
| CN108606956A (zh) | 2010-07-13 | 2018-10-02 | 奥特吉尼克斯制药公司 | 用于治疗唾液酸缺乏的方法和制剂 |
| CN103974965B (zh) | 2011-10-24 | 2019-09-24 | 奥特吉尼克斯制药公司 | 唾液酸类似物 |
| AR106025A1 (es) | 2015-09-14 | 2017-12-06 | Ultragenyx Pharmaceutical Inc | Formas cristalinas de ácido siálico o una sal o solvato de este |
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- 2013-01-18 AU AU2013209610A patent/AU2013209610B2/en not_active Expired - Fee Related
- 2013-01-18 CA CA2862836A patent/CA2862836A1/en not_active Abandoned
- 2013-01-18 BR BR112014017587A patent/BR112014017587A8/pt not_active Application Discontinuation
- 2013-01-18 CN CN201380015020.XA patent/CN104271125A/zh active Pending
- 2013-01-18 WO PCT/US2013/022167 patent/WO2013109906A2/en active Application Filing
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Also Published As
| Publication number | Publication date |
|---|---|
| JP2015504094A (ja) | 2015-02-05 |
| CA2862836A1 (en) | 2013-07-25 |
| WO2013109906A2 (en) | 2013-07-25 |
| IL233225A0 (en) | 2014-08-31 |
| AU2013209610A1 (en) | 2014-07-10 |
| EP2804600A2 (en) | 2014-11-26 |
| EP2804600A4 (en) | 2015-09-02 |
| KR20150000872A (ko) | 2015-01-05 |
| JP2017186381A (ja) | 2017-10-12 |
| BR112014017587A8 (pt) | 2017-07-04 |
| BR112014017587A2 (pt) | 2017-06-13 |
| CN104271125A (zh) | 2015-01-07 |
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