AU2018324477A1 - Adeno-associated virus capsid variants and methods of use thereof - Google Patents
Adeno-associated virus capsid variants and methods of use thereof Download PDFInfo
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- AU2018324477A1 AU2018324477A1 AU2018324477A AU2018324477A AU2018324477A1 AU 2018324477 A1 AU2018324477 A1 AU 2018324477A1 AU 2018324477 A AU2018324477 A AU 2018324477A AU 2018324477 A AU2018324477 A AU 2018324477A AU 2018324477 A1 AU2018324477 A1 AU 2018324477A1
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| EP3800191B1 (en) | 2014-03-17 | 2025-08-20 | Adverum Biotechnologies, Inc. | Compositions and methods for enhanced gene expression in cone cells |
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| AU2018338728B2 (en) | 2017-09-29 | 2025-01-02 | Centre National De La Recherche Scientifique (Cnrs) | Rescue of central and peripheral neurological phenotype of Friedreich's Ataxia by intravenous delivery |
| WO2019200016A1 (en) | 2018-04-10 | 2019-10-17 | President And Fellows Of Harvard College | Aav vectors encoding clarin-1 or gjb2 and uses thereof |
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