AU2018320849A1 - Recombinant adeno-associated vectors - Google Patents
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- AU2018320849A1 AU2018320849A1 AU2018320849A AU2018320849A AU2018320849A1 AU 2018320849 A1 AU2018320849 A1 AU 2018320849A1 AU 2018320849 A AU2018320849 A AU 2018320849A AU 2018320849 A AU2018320849 A AU 2018320849A AU 2018320849 A1 AU2018320849 A1 AU 2018320849A1
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| JP2023526439A (ja) | 2020-05-20 | 2023-06-21 | セルテゴ セラピューティクス インコーポレイテッド | 精神障害の処置のための環重水素化ガボキサドールおよびその使用 |
| JP2023540756A (ja) * | 2020-09-04 | 2023-09-26 | オハイオ・ステイト・イノベーション・ファウンデーション | 向上した形質導入効率及び脳内における広範な分布を有する組換えアデノ随伴ウイルスベクターの新規の操作されたキャプシド血清型 |
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| CN116096895A (zh) * | 2019-11-19 | 2023-05-09 | 阿斯克肋匹奥生物制药公司 | 用于治疗庞贝氏病和溶酶体紊乱的包含肝特异性启动子的治疗性腺相关病毒 |
| US11891616B2 (en) * | 2019-12-05 | 2024-02-06 | Board Of Regents Of The University Of Texas System | Transgene cassettes designed to express a human MECP2 gene |
| CA3116391A1 (en) * | 2020-09-14 | 2022-03-14 | President And Fellows Of Harvard College | Recombinant adeno associated virus encoding clarin-1 and uses thereof |
| WO2022169984A1 (en) * | 2021-02-03 | 2022-08-11 | The University Of North Carolina At Chapel Hill | Protein m analogs and fusion proteins and their use for inhibiting antibody function |
| EP4334332A4 (en) * | 2021-05-04 | 2025-11-12 | California Inst Of Techn | VAA RECOMMENDANTS FOR ADMINISTRATION TO THE CENTRAL NERVOUS SYSTEM AND CEREBRAL VASCULATURE |
| CN114259502A (zh) * | 2021-12-24 | 2022-04-01 | 南京鼓楼医院 | 一种基于脂肪组织的中枢靶向递送siRNA的方法及应用 |
| CN115554418B (zh) * | 2022-11-22 | 2023-04-14 | 四川至善唯新生物科技有限公司 | 一种重组腺相关病毒载体的药物组合物及其用途 |
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