SA518391456B1 - مجموعات التعبير الوراثي للعامل viii، بنيات خاصة بالكبد وطرق استخدامها - Google Patents

مجموعات التعبير الوراثي للعامل viii، بنيات خاصة بالكبد وطرق استخدامها Download PDF

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SA518391456B1
SA518391456B1 SA518391456A SA518391456A SA518391456B1 SA 518391456 B1 SA518391456 B1 SA 518391456B1 SA 518391456 A SA518391456 A SA 518391456A SA 518391456 A SA518391456 A SA 518391456A SA 518391456 B1 SA518391456 B1 SA 518391456B1
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sequence
gene
jjh
intron
expression construct
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SA518391456A
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إي ريلي بريجيت
كيه لي جاري
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سانجامو ثيرابيوتكس، انك.
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Publication of SA518391456B1 publication Critical patent/SA518391456B1/ar

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    • C12N2750/14011—Parvoviridae
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
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    • C12N2830/00—Vector systems having a special element relevant for transcription
    • C12N2830/60—Vector systems having a special element relevant for transcription from viruses

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SA518391456A 2015-10-28 2018-04-28 مجموعات التعبير الوراثي للعامل viii، بنيات خاصة بالكبد وطرق استخدامها SA518391456B1 (ar)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201562247469P 2015-10-28 2015-10-28
US201662307897P 2016-03-14 2016-03-14
US201662315438P 2016-03-30 2016-03-30
US201662326229P 2016-04-22 2016-04-22
US201662355106P 2016-06-27 2016-06-27
PCT/US2016/042099 WO2017074526A1 (en) 2015-10-28 2016-07-13 Liver-specific constructs, factor viii expression cassettes and methods of use thereof

Publications (1)

Publication Number Publication Date
SA518391456B1 true SA518391456B1 (ar) 2022-12-18

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US (4) US10143760B2 (https=)
EP (1) EP3368664A4 (https=)
JP (2) JP6909212B2 (https=)
KR (2) KR102766526B1 (https=)
CN (2) CN115141836B (https=)
AU (1) AU2016343887B2 (https=)
CA (1) CA3002524A1 (https=)
CO (1) CO2018005215A2 (https=)
IL (1) IL258826B2 (https=)
MX (1) MX2018005272A (https=)
MY (1) MY189674A (https=)
PE (1) PE20181206A1 (https=)
PH (1) PH12018500927B1 (https=)
SA (1) SA518391456B1 (https=)
SG (1) SG11201803547RA (https=)
WO (1) WO2017074526A1 (https=)
ZA (1) ZA201802723B (https=)

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