KR102766526B1 - 간-특이적 작제물인, 인자 viii 발현 카세트 및 이의 사용 방법 - Google Patents

간-특이적 작제물인, 인자 viii 발현 카세트 및 이의 사용 방법 Download PDF

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KR102766526B1
KR102766526B1 KR1020187014472A KR20187014472A KR102766526B1 KR 102766526 B1 KR102766526 B1 KR 102766526B1 KR 1020187014472 A KR1020187014472 A KR 1020187014472A KR 20187014472 A KR20187014472 A KR 20187014472A KR 102766526 B1 KR102766526 B1 KR 102766526B1
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vector
sequence
expression construct
polynucleotide expression
transgene
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KR20180069054A (ko
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브리짓 이. 라일리
게리 케이. 이
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상가모 테라퓨틱스, 인코포레이티드
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KR1020187014472A 2015-10-28 2016-07-13 간-특이적 작제물인, 인자 viii 발현 카세트 및 이의 사용 방법 Active KR102766526B1 (ko)

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Application Number Priority Date Filing Date Title
KR1020257003908A KR20250022906A (ko) 2015-10-28 2016-07-13 간-특이적 작제물인, 인자 viii 발현 카세트 및 이의 사용 방법

Applications Claiming Priority (11)

Application Number Priority Date Filing Date Title
US201562247469P 2015-10-28 2015-10-28
US62/247,469 2015-10-28
US201662307897P 2016-03-14 2016-03-14
US62/307,897 2016-03-14
US201662315438P 2016-03-30 2016-03-30
US62/315,438 2016-03-30
US201662326229P 2016-04-22 2016-04-22
US62/326,229 2016-04-22
US201662355106P 2016-06-27 2016-06-27
US62/355,106 2016-06-27
PCT/US2016/042099 WO2017074526A1 (en) 2015-10-28 2016-07-13 Liver-specific constructs, factor viii expression cassettes and methods of use thereof

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KR102766526B1 true KR102766526B1 (ko) 2025-02-13

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KR1020257003908A Pending KR20250022906A (ko) 2015-10-28 2016-07-13 간-특이적 작제물인, 인자 viii 발현 카세트 및 이의 사용 방법

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US (4) US10143760B2 (https=)
EP (1) EP3368664A4 (https=)
JP (2) JP6909212B2 (https=)
KR (2) KR102766526B1 (https=)
CN (2) CN115141836B (https=)
AU (1) AU2016343887B2 (https=)
CA (1) CA3002524A1 (https=)
CO (1) CO2018005215A2 (https=)
IL (1) IL258826B2 (https=)
MX (1) MX2018005272A (https=)
MY (1) MY189674A (https=)
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PH (1) PH12018500927B1 (https=)
SA (1) SA518391456B1 (https=)
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