LT3102673T - Beta talasemijos gydymo būdai ir kompozicijos - Google Patents

Beta talasemijos gydymo būdai ir kompozicijos

Info

Publication number
LT3102673T
LT3102673T LTEP15742584.4T LT15742584T LT3102673T LT 3102673 T LT3102673 T LT 3102673T LT 15742584 T LT15742584 T LT 15742584T LT 3102673 T LT3102673 T LT 3102673T
Authority
LT
Lithuania
Prior art keywords
compositions
treatment
methods
beta thalessemia
thalessemia
Prior art date
Application number
LTEP15742584.4T
Other languages
English (en)
Lithuanian (lt)
Inventor
Pei-Qi Liu
Andreas Reik
Lei Zhang
Original Assignee
Sangamo Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Sangamo Therapeutics, Inc. filed Critical Sangamo Therapeutics, Inc.
Publication of LT3102673T publication Critical patent/LT3102673T/lt

Links

Classifications

    • C—CHEMISTRY; METALLURGY
    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C07K14/795—Porphyrin- or corrin-ring-containing peptides
    • C07K14/805—Haemoglobins; Myoglobins
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K35/00—Medicinal preparations containing materials or reaction products thereof with undetermined constitution
    • A61K35/12—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells
    • A61K35/28—Bone marrow; Haematopoietic stem cells; Mesenchymal stem cells of any origin, e.g. adipose-derived stem cells
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P7/00—Drugs for disorders of the blood or the extracellular fluid
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K35/00—Medicinal preparations containing materials or reaction products thereof with undetermined constitution
    • A61K35/12—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells
    • A61K2035/124—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells the cells being hematopoietic, bone marrow derived or blood cells
    • C—CHEMISTRY; METALLURGY
    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K2319/00—Fusion polypeptide
    • C07K2319/80—Fusion polypeptide containing a DNA binding domain, e.g. Lacl or Tet-repressor
    • C07K2319/81—Fusion polypeptide containing a DNA binding domain, e.g. Lacl or Tet-repressor containing a Zn-finger domain for DNA binding

Landscapes

  • Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Organic Chemistry (AREA)
  • Medicinal Chemistry (AREA)
  • General Health & Medical Sciences (AREA)
  • Immunology (AREA)
  • Developmental Biology & Embryology (AREA)
  • Cell Biology (AREA)
  • Engineering & Computer Science (AREA)
  • Hematology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Animal Behavior & Ethology (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Genetics & Genomics (AREA)
  • Zoology (AREA)
  • Biotechnology (AREA)
  • Molecular Biology (AREA)
  • Biochemistry (AREA)
  • Biomedical Technology (AREA)
  • Virology (AREA)
  • Biophysics (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Epidemiology (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Diabetes (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Wood Science & Technology (AREA)
  • Microbiology (AREA)
  • General Engineering & Computer Science (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Separation Of Suspended Particles By Flocculating Agents (AREA)
LTEP15742584.4T 2014-02-03 2015-02-02 Beta talasemijos gydymo būdai ir kompozicijos LT3102673T (lt)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201461935219P 2014-02-03 2014-02-03
PCT/US2015/014103 WO2015117081A2 (fr) 2014-02-03 2015-02-02 Méthodes et compositions pour le traitement de la bêta-thalassémie

Publications (1)

Publication Number Publication Date
LT3102673T true LT3102673T (lt) 2020-08-25

Family

ID=53754265

Family Applications (1)

Application Number Title Priority Date Filing Date
LTEP15742584.4T LT3102673T (lt) 2014-02-03 2015-02-02 Beta talasemijos gydymo būdai ir kompozicijos

Country Status (12)

Country Link
US (1) US10072066B2 (fr)
EP (1) EP3102673B1 (fr)
DK (1) DK3102673T3 (fr)
ES (1) ES2796087T3 (fr)
HR (1) HRP20201038T1 (fr)
HU (1) HUE051232T2 (fr)
LT (1) LT3102673T (fr)
PL (1) PL3102673T3 (fr)
PT (1) PT3102673T (fr)
RS (1) RS60514B1 (fr)
SI (1) SI3102673T1 (fr)
WO (1) WO2015117081A2 (fr)

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CN104471067B (zh) 2012-05-07 2020-08-14 桑格摩生物治疗股份有限公司 用于核酸酶介导的转基因靶向整合的方法和组合物
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EP3102673A2 (fr) 2016-12-14
DK3102673T3 (da) 2020-07-06
PT3102673T (pt) 2020-05-21
WO2015117081A2 (fr) 2015-08-06
US20150218253A1 (en) 2015-08-06
SI3102673T1 (sl) 2020-11-30
EP3102673B1 (fr) 2020-04-15
EP3102673A4 (fr) 2017-11-01
US10072066B2 (en) 2018-09-11
WO2015117081A3 (fr) 2015-09-24
PL3102673T3 (pl) 2020-11-02
HUE051232T2 (hu) 2021-03-01
ES2796087T3 (es) 2020-11-25
RS60514B1 (sr) 2020-08-31

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