KR20230090337A - Crispr 유형 v 시스템을 위한 dna-함유 폴리뉴클레오티드 및 가이드, 및 그의 제조 및 사용 방법 - Google Patents

Crispr 유형 v 시스템을 위한 dna-함유 폴리뉴클레오티드 및 가이드, 및 그의 제조 및 사용 방법 Download PDF

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KR20230090337A
KR20230090337A KR1020237016342A KR20237016342A KR20230090337A KR 20230090337 A KR20230090337 A KR 20230090337A KR 1020237016342 A KR1020237016342 A KR 1020237016342A KR 20237016342 A KR20237016342 A KR 20237016342A KR 20230090337 A KR20230090337 A KR 20230090337A
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폴 대니얼 도노후에
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카리부 바이오사이언시스 인코포레이티드
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KR1020237016342A 2020-10-19 2021-10-18 Crispr 유형 v 시스템을 위한 dna-함유 폴리뉴클레오티드 및 가이드, 및 그의 제조 및 사용 방법 Pending KR20230090337A (ko)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202063093459P 2020-10-19 2020-10-19
US63/093,459 2020-10-19
US202063127648P 2020-12-18 2020-12-18
US63/127,648 2020-12-18
US202163229870P 2021-08-05 2021-08-05
US63/229,870 2021-08-05
PCT/US2021/055394 WO2022086846A2 (en) 2020-10-19 2021-10-18 Dna-containing polynucleotides and guides for crispr type v systems, and methods of making and using the same

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KR20230090337A true KR20230090337A (ko) 2023-06-21

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US (1) US20250027078A1 (https=)
EP (1) EP4229198A2 (https=)
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KR (1) KR20230090337A (https=)
AU (1) AU2021364314C1 (https=)
CA (1) CA3198905A1 (https=)
IL (1) IL302220A (https=)
MX (1) MX2023004505A (https=)
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WO2024046307A1 (zh) * 2022-08-29 2024-03-07 北京迅识科技有限公司 一种突变的v型crispr酶及其应用
AU2023353989A1 (en) 2022-09-30 2025-02-27 Caribou Biosciences, Inc. Anti-ror1 chimeric antigen receptors (cars), cells expressing the cars and related methods
WO2024102434A1 (en) 2022-11-10 2024-05-16 Senda Biosciences, Inc. Rna compositions comprising lipid nanoparticles or lipid reconstructed natural messenger packs
EP4584283A1 (en) 2022-11-14 2025-07-16 Caribou Biosciences, Inc. Anti-cll-1 chimeric antigen receptors, engineered cells and related methods
AU2024236558A1 (en) 2023-03-15 2025-10-09 Renagade Therapeutics Management Inc. Delivery of gene editing systems and methods of use thereof
EP4704886A1 (en) * 2023-05-01 2026-03-11 Caribou Biosciences, Inc. Treatment of autoimmune diseases with bcma-targeting engineered immune cells
WO2025006880A1 (en) 2023-06-29 2025-01-02 Caribou Biosciences, Inc. Diagnostic and therapeutic methods for use with ror1 antagonists
WO2025024679A1 (en) * 2023-07-26 2025-01-30 Caribou Biosciences, Inc. In vitro validation methods for car-t cell therapies
AU2024335327A1 (en) 2023-09-01 2026-03-26 Renagade Therapeutics Management Inc. Gene editing systems, compositions, and methods for treatment of vexas syndrome
WO2025117745A1 (en) 2023-12-01 2025-06-05 Caribou Biosciences, Inc. Methods and compositions for improving precision of endonuclease-mediated genome editing
WO2025174765A1 (en) 2024-02-12 2025-08-21 Renagade Therapeutics Management Inc. Lipid nanoparticles comprising coding rna molecules for use in gene editing and as vaccines and therapeutic agents
WO2025231432A1 (en) * 2024-05-03 2025-11-06 Caribou Biosciences, Inc. In vivo gene editing with crispr systems
WO2026024468A1 (en) 2024-07-26 2026-01-29 Caribou Biosciences, Inc. Modular linked chimeric antigen receptors
CN119881333B (zh) * 2025-01-27 2025-11-28 上海市肿瘤研究所 一种dna纳米花级联crispr系统的蛋白标志物检测平台及其构建方法和应用

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US9650617B2 (en) * 2015-01-28 2017-05-16 Pioneer Hi-Bred International. Inc. CRISPR hybrid DNA/RNA polynucleotides and methods of use
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EP4229198A2 (en) 2023-08-23
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AU2021364314A1 (en) 2023-03-16
WO2022086846A3 (en) 2022-07-21
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AU2021364314C1 (en) 2025-02-20
IL302220A (en) 2023-06-01
WO2022086846A9 (en) 2023-06-15
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