KR20200057766A - 페닐케톤뇨증을 치료하기 위한 프로모터 및 인핸서 조합을 포함하는 벡터 - Google Patents

페닐케톤뇨증을 치료하기 위한 프로모터 및 인핸서 조합을 포함하는 벡터 Download PDF

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KR20200057766A
KR20200057766A KR1020207012276A KR20207012276A KR20200057766A KR 20200057766 A KR20200057766 A KR 20200057766A KR 1020207012276 A KR1020207012276 A KR 1020207012276A KR 20207012276 A KR20207012276 A KR 20207012276A KR 20200057766 A KR20200057766 A KR 20200057766A
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sequence
pah
seq
promoter
vector
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타일러 라후젠
찰스 데이비드 파우자
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아메리칸 진 테크놀로지스 인터내셔널 인코포레이티드
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KR1020207012276A 2017-10-02 2018-10-02 페닐케톤뇨증을 치료하기 위한 프로모터 및 인핸서 조합을 포함하는 벡터 Ceased KR20200057766A (ko)

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US201762566979P 2017-10-02 2017-10-02
US62/566,979 2017-10-02
PCT/US2018/053919 WO2019070674A2 (en) 2017-10-02 2018-10-02 VECTORS COMPRISING PROMOTER AND ACTIVATOR COMBINATIONS FOR THE TREATMENT OF PHENYLCETONURIA

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US (1) US20200318081A1 (enExample)
EP (1) EP3692157A4 (enExample)
JP (2) JP2020535828A (enExample)
KR (1) KR20200057766A (enExample)
CN (1) CN111433368A (enExample)
AU (1) AU2018345745A1 (enExample)
BR (1) BR112020006672A2 (enExample)
CA (1) CA3077355A1 (enExample)
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WO2010045659A1 (en) 2008-10-17 2010-04-22 American Gene Technologies International Inc. Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
WO2017007994A1 (en) 2015-07-08 2017-01-12 American Gene Technologies International Inc. Hiv pre-immunization and immunotherapy
AU2017207906B2 (en) 2016-01-15 2021-03-11 American Gene Technologies International Inc. Methods and compositions for the activation of gamma-delta T-cells
US10137144B2 (en) 2016-01-15 2018-11-27 American Gene Technologies International Inc. Methods and compositions for the activation of gamma-delta T-cells
US10888613B2 (en) 2016-02-08 2021-01-12 American Gene Technologies International Inc. Method of producing cells resistant to HIV infection
EP3426777B1 (en) 2016-03-09 2022-02-16 American Gene Technologies International Inc. Combination vectors and methods for treating cancer
JP7173548B2 (ja) 2016-06-08 2022-11-16 アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド 非組み込みウイルス送達系およびその関連方法
EP3481418A4 (en) 2016-07-08 2020-03-11 American Gene Technologies International Inc. PRE-IMMUNIZATION AND IMMUNOTHERAPY OF HIV
WO2018017882A1 (en) 2016-07-21 2018-01-25 American Gene Technologies International Inc. Viral vectors for treating parkinson's disease
JP2020512815A (ja) 2017-04-03 2020-04-30 アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド フェニルケトン尿症を処置するための組成物および方法
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