JP2020535828A - フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター - Google Patents

フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター Download PDF

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JP2020535828A
JP2020535828A JP2020518812A JP2020518812A JP2020535828A JP 2020535828 A JP2020535828 A JP 2020535828A JP 2020518812 A JP2020518812 A JP 2020518812A JP 2020518812 A JP2020518812 A JP 2020518812A JP 2020535828 A JP2020535828 A JP 2020535828A
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pah
sequence
seq
promoter
vector
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JP2020535828A5 (enExample
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テイラー ラフーゼン，
テイラー ラフーゼン，
チャールズ デイビッド パウザ，
チャールズ デイビッド パウザ，
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アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド
アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド
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Publication of JP2020535828A publication Critical patent/JP2020535828A/ja
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JP2020518812A 2017-10-02 2018-10-02 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター Pending JP2020535828A (ja)

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JP2023101880A JP2023115125A (ja) 2017-10-02 2023-06-21 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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US201762566979P 2017-10-02 2017-10-02
US62/566,979 2017-10-02
PCT/US2018/053919 WO2019070674A2 (en) 2017-10-02 2018-10-02 VECTORS COMPRISING PROMOTER AND ACTIVATOR COMBINATIONS FOR THE TREATMENT OF PHENYLCETONURIA

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JP2023101880A Pending JP2023115125A (ja) 2017-10-02 2023-06-21 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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US20100183558A1 (en) 2008-10-17 2010-07-22 Zhennan Lai Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
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