CN111433368A - 具有启动子和增强子组合的载体用于治疗苯丙酮尿症 - Google Patents

具有启动子和增强子组合的载体用于治疗苯丙酮尿症 Download PDF

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CN111433368A
CN111433368A CN201880077904.0A CN201880077904A CN111433368A CN 111433368 A CN111433368 A CN 111433368A CN 201880077904 A CN201880077904 A CN 201880077904A CN 111433368 A CN111433368 A CN 111433368A
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pah
sequence
seq
vector
promoter
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T·拉胡森
C·D·保扎
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American Gene Technologies International Inc
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American Gene Technologies International Inc
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CN201880077904.0A 2017-10-02 2018-10-02 具有启动子和增强子组合的载体用于治疗苯丙酮尿症 Pending CN111433368A (zh)

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US201762566979P 2017-10-02 2017-10-02
US62/566,979 2017-10-02
PCT/US2018/053919 WO2019070674A2 (en) 2017-10-02 2018-10-02 VECTORS COMPRISING PROMOTER AND ACTIVATOR COMBINATIONS FOR THE TREATMENT OF PHENYLCETONURIA

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US (1) US20200318081A1 (enExample)
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KR (1) KR20200057766A (enExample)
CN (1) CN111433368A (enExample)
AU (1) AU2018345745A1 (enExample)
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IL297238B2 (en) 2016-01-15 2024-08-01 American Gene Tech Int Inc Methods and preparations for gamma-delta T-cell activation
US10137144B2 (en) 2016-01-15 2018-11-27 American Gene Technologies International Inc. Methods and compositions for the activation of gamma-delta T-cells
JP7153332B2 (ja) 2016-02-08 2022-10-14 アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド Ｈｉｖワクチン接種および免疫療法
ES2911448T3 (es) 2016-03-09 2022-05-19 American Gene Tech Int Inc Vectores combinados y métodos para el tratamiento del cáncer
WO2017213697A1 (en) 2016-06-08 2017-12-14 American Gene Technologies International Inc. Non-integrating viral delivery system and methods related thereto
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WO2018017882A1 (en) 2016-07-21 2018-01-25 American Gene Technologies International Inc. Viral vectors for treating parkinson's disease
US11820999B2 (en) 2017-04-03 2023-11-21 American Gene Technologies International Inc. Compositions and methods for treating phenylketonuria
US12559769B2 (en) 2017-06-16 2026-02-24 American Gene Technologies International Inc. Methods and compositions for the activation of tumor cytotoxicity via human gamma-delta t-cells
BR112021024124A2 (pt) * 2019-05-31 2022-01-11 American Gene Tech Int Inc Expressão otimizada de fenilalanina hidroxilase
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